ニーマン・ピック病（NPD）の世界市場レポート 2025年

ニーマン・ピック病（NPD）の市場規模は今後数年で急成長が見込まれます。2029年には年間平均成長率（CAGR）11.0％で16億3,000万米ドルに成長します。予測期間中の成長は、個別化医療に対する需要の高まり、ライソゾーム貯蔵障害に対する関心の高まり、希少疾病用医薬品に対する規制当局の承認の高まり、標的治療に対する需要の高まり、高度診断ツールに対するニーズの高まりに起因しています。予測期間における主な動向としては、治療選択肢の発展、診断ツールの技術革新、診断における人工知能の統合、酵素補充療法（ERT）の革新、新薬の臨床試験開発などが挙げられます。

遺伝子治療の採用拡大が、今後数年間のニーマン・ピック病（NPD）市場の成長を牽引すると予想されます。遺伝子治療とは、個人の遺伝子を改変または操作して病気を治療または予防する医療技術です。遺伝子治療は、遺伝子工学の進歩により、正確で効果的な遺伝子改変が可能となり、遺伝性疾患の治療成績を向上させる。ニーマン・ピック病（NPD）の場合、遺伝子治療は、障害の原因となる酵素欠損を修正し、細胞機能を強化するために、根本的な遺伝子変異を標的とします。例えば、2024年1月、遺伝子・細胞治療に特化した米国を拠点とする組織である米国遺伝子・細胞治療学会は、2023年第4四半期に第Ⅲ相臨床試験中の遺伝子治療薬の数が前期比で10％増加し、2022年第3四半期以来の増加となったと報告しました。このように、遺伝子治療の採用拡大がニーマン・ピック病（NPD）市場の拡大に拍車をかけています。

ニーマン・ピック病（NPD）市場の主なプレーヤーは、治療効果と患者の転帰を改善するために、併用療法などの先進治療の開発に注力しています。併用療法は、2種類以上の治療薬や治療戦略を用いて病気を治療するもので、単剤治療の効果を高め、耐性を低下させる。例えば、米国を拠点とするバイオ医薬品会社Zevra Therapeutics Inc.は2024年9月、2歳以上の成人および小児患者におけるニーマン・ピック病C型（NPC）の神経症状の治療薬として、ミグルスタットと併用するMIPLYFFAの承認を米国食品医薬品局（FDA）から取得しました。ミプリファ（アリモクロモール）は熱ショック蛋白（HSP）の産生を促進することにより作用し、HSPは蓄積した有害脂質を除去し、神経細胞を損傷から保護します。一方、ミグルスタットはグルコシルセラミド合成酵素を阻害し、脂質の蓄積を抑えます。これらの療法を併用することで、NPC患者の神経機能低下の進行を遅らせることができます。

目次

第1章 エグゼクティブサマリー

第2章 市場の特徴

第3章 市場動向と戦略

第4章 市場- 金利、インフレ、地政学、貿易戦争と関税、そしてコロナ禍と回復が市場に与える影響を含むマクロ経済シナリオ

第5章 世界の成長分析と戦略分析フレームワーク

• 世界ニーマン・ピック病（NPD） PESTEL分析（政治、社会、技術、環境、法的要因、促進要因と抑制要因）
• 最終用途産業の分析
• 世界のニーマン・ピック病（NPD）市場：成長率分析
• 世界のニーマン・ピック病（NPD）市場の実績：規模と成長, 2019-2024
• 世界のニーマン・ピック病（NPD）市場の予測：規模と成長, 2024-2029, 2034F
• 世界ニーマン・ピック病（NPD）総アドレス可能市場（TAM）

第6章 市場セグメンテーション

• 世界のニーマン・ピック病（NPD）市場：タイプ別、実績と予測, 2019-2024, 2024-2029F, 2034F
• ニーマン・ピック病A型
• ニーマン・ピック病B型
• ニーマン・ピック病C型
• 世界のニーマン・ピック病（NPD）市場治療の種類別、実績と予測, 2019-2024, 2024-2029F, 2034F
• 薬物
• 理学療法
• その他の治療の種類
• 世界のニーマン・ピック病（NPD）市場：投与経路別、実績と予測, 2019-2024, 2024-2029F, 2034F
• オーラル
• 静脈内
• 皮下
• 世界のニーマン・ピック病（NPD）市場：流通チャネル別、実績と予測, 2019-2024, 2024-2029F, 2034F
• 病院薬局
• 小売薬局
• その他の流通チャネル
• 世界のニーマン・ピック病（NPD）市場：エンドユーザー別、実績と予測, 2019-2024, 2024-2029F, 2034F
• 病院
• クリニック
• 在宅ケア設定
• 世界のニーマン・ピック病（NPD）市場ニーマン・ピック病A型のサブセグメンテーション（型別）、実績と予測, 2019-2024, 2024-2029F, 2034F
• 乳児発症ニーマン・ピック病
• 神経変性ニーマン・ピック病
• 急性内臓ニーマン・ピック病
• 重度のリソソーム蓄積症
• 世界のニーマン・ピック病（NPD）市場ニーマン・ピック病B型のサブセグメンテーション（型別）、実績と予測, 2019-2024, 2024-2029F, 2034F
• 遅発性ニーマン・ピック病
• 非神経性ニーマン・ピック病
• 慢性内臓ニーマン・ピック病
• 軽度リソソーム蓄積症
• 世界のニーマン・ピック病（NPD）市場ニーマン・ピック病C型のサブセグメンテーション（型別）、実績と予測, 2019-2024, 2024-2029F, 2034F
• 早期発症型ニーマン・ピック病
• 若年性ニーマン・ピック病
• 成人発症ニーマン・ピック病
• 進行性神経変性ニーマン・ピック病

第7章 地域別・国別分析

• 世界のニーマン・ピック病（NPD）市場：地域別、実績と予測, 2019-2024, 2024-2029F, 2034F
• 世界のニーマン・ピック病（NPD）市場：国別、実績と予測, 2019-2024, 2024-2029F, 2034F

第8章 アジア太平洋市場

第9章 中国市場

第10章 インド市場

第11章 日本市場

第12章 オーストラリア市場

第13章 インドネシア市場

第14章 韓国市場

第15章 西欧市場

第16章 英国市場

第17章 ドイツ市場

第18章 フランス市場

第19章 イタリア市場

第20章 スペイン市場

第21章 東欧市場

第22章 ロシア市場

第23章 北米市場

第24章 米国市場

第25章 カナダ市場

第26章 南米市場

第27章 ブラジル市場

第28章 中東市場

第29章 アフリカ市場

第30章 競合情勢と企業プロファイル

• ニーマン・ピック病（NPD）市場：競合情勢
• ニーマン・ピック病（NPD）市場：企業プロファイル
  • Sanofi S.A. Overview, Products and Services, Strategy and Financial Analysis
  • Mayo Clinic Overview, Products and Services, Strategy and Financial Analysis
  • Cincinnati Children's Hospital Medical Center Overview, Products and Services, Strategy and Financial Analysis
  • Boston Children's Hospital Overview, Products and Services, Strategy and Financial Analysis
  • Mallinckrodt Pharmaceuticals plc Overview, Products and Services, Strategy and Financial Analysis

第31章 その他の大手企業と革新的企業

• Myriad Genetics
• CENTOGENE N.V.
• The Florey Institute of Neuroscience and Mental Health
• National Organization for Rare Disorders（NORD）
• Evox Therapeutics Limited
• Zevra Therapeutics Inc.
• IntraBio Inc.
• Dipharma SA
• Okklo Life Sciences
• Bloomsbury Genetic Therapies Ltd.
• Azafaros A.G
• Cyclo Therapeutics Inc.
• Mandos Health
• CarelonRx
• Rainbow Children's Hospital

第32章 世界の市場競合ベンチマーキングとダッシュボード

第33章 主要な合併と買収

第34章 最近の市場動向

第35章 市場の潜在力が高い国、セグメント、戦略

• ニーマン・ピック病（NPD）市場2029：新たな機会を提供する国
• ニーマン・ピック病（NPD）市場2029：新たな機会を提供するセグメント
• ニーマン・ピック病（NPD）市場2029：成長戦略
  • 市場動向に基づく戦略
  • 競合の戦略

第36章 付録

Niemann-Pick disease (NPD) is a rare inherited lysosomal storage disorder caused by mutations in the SMPD1 (Types A and B) or NPC1/NPC2 (Type C) genes, resulting in excessive lipid accumulation in cells. This buildup leads to progressive damage to the brain, liver, spleen, and other organs. The symptoms of NPD vary by type but may include neurodegeneration, hepatosplenomegaly (enlargement of the liver and spleen), respiratory complications, and developmental delays.

Note that the outlook for this market is being affected by rapid changes in trade relations and tariffs globally. The report will be updated prior to delivery to reflect the latest status, including revised forecasts and quantified impact analysis. The report's Recommendations and Conclusions sections will be updated to give strategies for entities dealing with the fast-moving international environment.

The main types of Niemann-Pick disease are Type A, Type B, and Type C. Niemann-Pick disease type A is a rare and severe genetic disorder caused by a deficiency of the enzyme acid sphingomyelinase (ASM), leading to the accumulation of sphingomyelin in various organs. Treatment for this type includes drugs, physical therapy, and other interventions, administered through various routes such as oral, intravenous, and subcutaneous. Distribution channels for these treatments include hospital pharmacies, retail pharmacies, and others, and they are used by various end users, including hospitals, clinics, and home care settings.

The niemann-pick disease (NPD) market research report is one of a series of new reports from The Business Research Company that provides niemann-pick disease (NPD) market statistics, including niemann-pick disease (NPD) industry global market size, regional shares, competitors with a niemann-pick disease (NPD) market share, detailed niemann-pick disease (NPD) market segments, market trends and opportunities, and any further data you may need to thrive in the niemann-pick disease (NPD) industry. This niemann-pick disease (NPD) market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future scenario of the industry.

The niemann-pick disease (NPD) market size has grown rapidly in recent years. It will grow from$0.97 billion in 2024 to $1.07 billion in 2025 at a compound annual growth rate (CAGR) of 11.3%. The growth during the historic period can be attributed to the rising number of genetic counselors, increased funding for rare disease research, growing investment from venture capital firms, the increasing use of biomarkers, and enhanced healthcare access.

The niemann-pick disease (NPD) market size is expected to see rapid growth in the next few years. It will grow to$1.63 billion in 2029 at a compound annual growth rate (CAGR) of 11.0%. The growth during the forecast period can be attributed to the growing demand for personalized medicine, increased interest in lysosomal storage disorders, rising regulatory approvals for orphan drugs, increasing demand for targeted therapies, and the growing need for advanced diagnostic tools. Key trends in the forecast period include advancements in treatment options, technological innovations in diagnostic tools, integration of artificial intelligence in diagnosis, innovation in enzyme replacement therapies (ERT), and the development of clinical trials for new drugs.

The increasing adoption of gene therapy is expected to drive the growth of the Niemann-Pick disease (NPD) market in the coming years. Gene therapy is a medical technique that modifies or manipulates an individual's genes to treat or prevent diseases. The rise in gene therapy is fueled by advancements in genetic engineering, which enable precise and effective gene modifications that improve treatment outcomes for genetic disorders. In the case of Niemann-Pick disease (NPD), gene therapy targets the underlying genetic mutations to correct enzyme deficiencies that cause the disorder and enhance cellular function. For example, in January 2024, the American Society of Gene and Cell Therapy, a U.S.-based organization focused on gene and cell therapy, reported that the number of gene therapies in Phase III trials increased by 10% in the fourth quarter of 2023 compared to the previous quarter, marking the first rise since the third quarter of 2022. Thus, the growing adoption of gene therapy is fueling the expansion of the Niemann-Pick disease (NPD) market.

Key players in the Niemann-Pick disease (NPD) market are focusing on developing advanced treatments, such as combination therapy, to improve treatment efficacy and patient outcomes. Combination therapy involves using two or more therapeutic agents or strategies to treat a disease, enhancing effectiveness and reducing resistance to single-agent treatments. For example, in September 2024, Zevra Therapeutics Inc., a U.S.-based biopharmaceutical company, received U.S. Food and Drug Administration (FDA) approval for MIPLYFFA, combined with miglustat, for treating the neurological symptoms of Niemann-Pick disease type C (NPC) in both adult and pediatric patients aged 2 years and older. MIPLYFFA (arimoclomol) works by boosting the production of heat shock proteins (HSPs), which help clear toxic lipid buildup and protect neurons from damage. Meanwhile, miglustat inhibits glucosylceramide synthase, reducing lipid accumulation. Together, these therapies help slow the progression of neurological decline in NPC patients.

In May 2022, Zevra Therapeutics Inc. (formerly KemPharm Inc.), a U.S.-based pharmaceutical company, acquired arimoclomol from Orphazyme A/S for $12.8 million. This acquisition allows Zevra to strengthen its rare disease pipeline by gaining access to arimoclomol, a promising heat shock protein amplifier developed for treating Niemann-Pick disease type C (NPC). Orphazyme A/S, a Denmark-based biopharmaceutical company, specializes in developing treatments for rare neurodegenerative diseases, including Niemann-Pick disease type C (NPC).

Major players in the niemann-pick disease (NPD) market are Sanofi S.A., Mayo Clinic, Cincinnati Children's Hospital Medical Center, Boston Children's Hospital, Mallinckrodt Pharmaceuticals plc, Myriad Genetics, CENTOGENE N.V., The Florey Institute of Neuroscience and Mental Health, National Organization for Rare Disorders (NORD), Evox Therapeutics Limited, Zevra Therapeutics Inc., IntraBio Inc., Dipharma SA, Okklo Life Sciences, Bloomsbury Genetic Therapies Ltd., Azafaros A.G, Cyclo Therapeutics Inc., Mandos Health, CarelonRx, Rainbow Children's Hospital, and Vtesse Inc.

North America was the largest region in the niemann-pick disease (NPD) market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in niemann-pick disease (NPD report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East and Africa.

The countries covered in the niemann-pick disease (NPD) market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

The niemann-pick disease (NPD) market consists of revenues earned by entities by providing services such as diagnostic testing, genetic counseling, patient support programs, clinical trial management, drug development, and regulatory consulting. The market value includes the value of related goods sold by the service provider or included within the service offering. The niemann-pick disease (NPD) market also includes sales of gene therapy products, enzyme replacement tools, diagnostic kits, biomarker testing tools, and supportive care products. Values in this market are 'factory gate' values, that is the value of goods sold by the manufacturers or creators of the goods, whether to other entities (including downstream manufacturers, wholesalers, distributors and retailers) or directly to end customers. The value of goods in this market includes related services sold by the creators of the goods.

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD, unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

Niemann-Pick Disease (NPD) Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on niemann-pick disease (npd) market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

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Where is the largest and fastest growing market for niemann-pick disease (npd) ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward? The niemann-pick disease (npd) market global report from the Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market's historic and forecast market growth by geography.

• The market characteristics section of the report defines and explains the market.
• The market size section gives the market size ($b) covering both the historic growth of the market, and forecasting its development.
• The forecasts are made after considering the major factors currently impacting the market. These include:

The forecasts are made after considering the major factors currently impacting the market. These include the Russia-Ukraine war, rising inflation, higher interest rates, and the legacy of the COVID-19 pandemic.

• Market segmentations break down the market into sub markets.
• The regional and country breakdowns section gives an analysis of the market in each geography and the size of the market by geography and compares their historic and forecast growth. It covers the growth trajectory of COVID-19 for all regions, key developed countries and major emerging markets.
• The competitive landscape chapter gives a description of the competitive nature of the market, market shares, and a description of the leading companies. Key financial deals which have shaped the market in recent years are identified.
• The trends and strategies section analyses the shape of the market as it emerges from the crisis and suggests how companies can grow as the market recovers.

Scope

• Markets Covered:1) By Type: Niemann-Pick Disease Type A; Niemann-Pick Disease Type B; Niemann-Pick Disease Type C
• 2) By Treatment Type: Drugs; Physical Therapy; Other Treatment Types
• 3) By Route Of Administration: Oral; Intravenous; Subcutaneous
• 4) By Distribution Channel: Hospital Pharmacies; Retail Pharmacies; Other Distribution Channels
• 5) By End-User: Hospitals; Clinics; Homecare Settings
• Subsegments:
• 1) By Niemann-Pick Disease Type A: Infantile-Onset Niemann-Pick Disease; Neurodegenerative Niemann-Pick Disease; Acute Visceral Niemann-Pick Disease; Severe Lysosomal Storage Disorder
• 2) By Niemann-Pick Disease Type B: Late-Onset Niemann-Pick Disease; Non-Neurological Niemann-Pick Disease; Chronic Visceral Niemann-Pick Disease; Mild Lysosomal Storage Disorder
• 3) By Niemann-Pick Disease Type C: Early-Onset Niemann-Pick Disease; Juvenile Niemann-Pick Disease; Adult-Onset Niemann-Pick Disease; Progressive Neurodegenerative Niemann-Pick Disease
• Companies Mentioned: Sanofi S.A.; Mayo Clinic; Cincinnati Children's Hospital Medical Center; Boston Children's Hospital; Mallinckrodt Pharmaceuticals plc
• Countries: Australia; Brazil; China; France; Germany; India; Indonesia; Japan; Russia; South Korea; UK; USA; Canada; Italy; Spain
• Regions: Asia-Pacific; Western Europe; Eastern Europe; North America; South America; Middle East; Africa
• Time series: Five years historic and ten years forecast.
• Data: Ratios of market size and growth to related markets, GDP proportions, expenditure per capita,
• Data segmentations: country and regional historic and forecast data, market share of competitors, market segments.
• Sourcing and Referencing: Data and analysis throughout the report is sourced using end notes.
• Delivery Format: PDF, Word and Excel Data Dashboard.

Table of Contents

1. Executive Summary

2. Niemann-Pick Disease (NPD) Market Characteristics

3. Niemann-Pick Disease (NPD) Market Trends And Strategies

4. Niemann-Pick Disease (NPD) Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market

5. Global Niemann-Pick Disease (NPD) Growth Analysis And Strategic Analysis Framework

• 5.1. Global Niemann-Pick Disease (NPD) PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)
• 5.2. Analysis Of End Use Industries
• 5.3. Global Niemann-Pick Disease (NPD) Market Growth Rate Analysis
• 5.4. Global Niemann-Pick Disease (NPD) Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)
• 5.5. Global Niemann-Pick Disease (NPD) Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)
• 5.6. Global Niemann-Pick Disease (NPD) Total Addressable Market (TAM)

6. Niemann-Pick Disease (NPD) Market Segmentation

• 6.1. Global Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Niemann-Pick Disease Type A
• Niemann-Pick Disease Type B
• Niemann-Pick Disease Type C
• 6.2. Global Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Drugs
• Physical Therapy
• Other Treatment Types
• 6.3. Global Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Oral
• Intravenous
• Subcutaneous
• 6.4. Global Niemann-Pick Disease (NPD) Market, Segmentation By Distribution Channel, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Hospital Pharmacies
• Retail Pharmacies
• Other Distribution Channels
• 6.5. Global Niemann-Pick Disease (NPD) Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Hospitals
• Clinics
• Homecare Settings
• 6.6. Global Niemann-Pick Disease (NPD) Market, Sub-Segmentation Of Niemann-Pick Disease Type A, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Infantile-Onset Niemann-Pick Disease
• Neurodegenerative Niemann-Pick Disease
• Acute Visceral Niemann-Pick Disease
• Severe Lysosomal Storage Disorder
• 6.7. Global Niemann-Pick Disease (NPD) Market, Sub-Segmentation Of Niemann-Pick Disease Type B, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Late-Onset Niemann-Pick Disease
• Non-Neurological Niemann-Pick Disease
• Chronic Visceral Niemann-Pick Disease
• Mild Lysosomal Storage Disorder
• 6.8. Global Niemann-Pick Disease (NPD) Market, Sub-Segmentation Of Niemann-Pick Disease Type C, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• Early-Onset Niemann-Pick Disease
• Juvenile Niemann-Pick Disease
• Adult-Onset Niemann-Pick Disease
• Progressive Neurodegenerative Niemann-Pick Disease

7. Niemann-Pick Disease (NPD) Market Regional And Country Analysis

• 7.1. Global Niemann-Pick Disease (NPD) Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 7.2. Global Niemann-Pick Disease (NPD) Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

8. Asia-Pacific Niemann-Pick Disease (NPD) Market

• 8.1. Asia-Pacific Niemann-Pick Disease (NPD) Market Overview
• Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies
• 8.2. Asia-Pacific Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 8.3. Asia-Pacific Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 8.4. Asia-Pacific Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

9. China Niemann-Pick Disease (NPD) Market

• 9.1. China Niemann-Pick Disease (NPD) Market Overview
• 9.2. China Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
• 9.3. China Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
• 9.4. China Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion

10. India Niemann-Pick Disease (NPD) Market

• 10.1. India Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 10.2. India Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 10.3. India Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

11. Japan Niemann-Pick Disease (NPD) Market

• 11.1. Japan Niemann-Pick Disease (NPD) Market Overview
• 11.2. Japan Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 11.3. Japan Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 11.4. Japan Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

12. Australia Niemann-Pick Disease (NPD) Market

• 12.1. Australia Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 12.2. Australia Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 12.3. Australia Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

13. Indonesia Niemann-Pick Disease (NPD) Market

• 13.1. Indonesia Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 13.2. Indonesia Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 13.3. Indonesia Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

14. South Korea Niemann-Pick Disease (NPD) Market

• 14.1. South Korea Niemann-Pick Disease (NPD) Market Overview
• 14.2. South Korea Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 14.3. South Korea Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 14.4. South Korea Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

15. Western Europe Niemann-Pick Disease (NPD) Market

• 15.1. Western Europe Niemann-Pick Disease (NPD) Market Overview
• 15.2. Western Europe Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 15.3. Western Europe Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 15.4. Western Europe Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

16. UK Niemann-Pick Disease (NPD) Market

• 16.1. UK Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 16.2. UK Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 16.3. UK Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

17. Germany Niemann-Pick Disease (NPD) Market

• 17.1. Germany Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 17.2. Germany Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 17.3. Germany Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

18. France Niemann-Pick Disease (NPD) Market

• 18.1. France Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 18.2. France Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 18.3. France Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

19. Italy Niemann-Pick Disease (NPD) Market

• 19.1. Italy Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 19.2. Italy Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 19.3. Italy Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

20. Spain Niemann-Pick Disease (NPD) Market

• 20.1. Spain Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 20.2. Spain Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 20.3. Spain Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

21. Eastern Europe Niemann-Pick Disease (NPD) Market

• 21.1. Eastern Europe Niemann-Pick Disease (NPD) Market Overview
• 21.2. Eastern Europe Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 21.3. Eastern Europe Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 21.4. Eastern Europe Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

22. Russia Niemann-Pick Disease (NPD) Market

• 22.1. Russia Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 22.2. Russia Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 22.3. Russia Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

23. North America Niemann-Pick Disease (NPD) Market

• 23.1. North America Niemann-Pick Disease (NPD) Market Overview
• 23.2. North America Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 23.3. North America Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 23.4. North America Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

24. USA Niemann-Pick Disease (NPD) Market

• 24.1. USA Niemann-Pick Disease (NPD) Market Overview
• 24.2. USA Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 24.3. USA Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 24.4. USA Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

25. Canada Niemann-Pick Disease (NPD) Market

• 25.1. Canada Niemann-Pick Disease (NPD) Market Overview
• 25.2. Canada Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 25.3. Canada Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 25.4. Canada Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

26. South America Niemann-Pick Disease (NPD) Market

• 26.1. South America Niemann-Pick Disease (NPD) Market Overview
• 26.2. South America Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 26.3. South America Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 26.4. South America Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

27. Brazil Niemann-Pick Disease (NPD) Market

• 27.1. Brazil Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 27.2. Brazil Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 27.3. Brazil Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

28. Middle East Niemann-Pick Disease (NPD) Market

• 28.1. Middle East Niemann-Pick Disease (NPD) Market Overview
• 28.2. Middle East Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 28.3. Middle East Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 28.4. Middle East Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

29. Africa Niemann-Pick Disease (NPD) Market

• 29.1. Africa Niemann-Pick Disease (NPD) Market Overview
• 29.2. Africa Niemann-Pick Disease (NPD) Market, Segmentation By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 29.3. Africa Niemann-Pick Disease (NPD) Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
• 29.4. Africa Niemann-Pick Disease (NPD) Market, Segmentation By Route Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion

30. Niemann-Pick Disease (NPD) Market Competitive Landscape And Company Profiles

• 30.1. Niemann-Pick Disease (NPD) Market Competitive Landscape
• 30.2. Niemann-Pick Disease (NPD) Market Company Profiles
  • 30.2.1. Sanofi S.A. Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.2. Mayo Clinic Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.3. Cincinnati Children's Hospital Medical Center Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.4. Boston Children's Hospital Overview, Products and Services, Strategy and Financial Analysis
  • 30.2.5. Mallinckrodt Pharmaceuticals plc Overview, Products and Services, Strategy and Financial Analysis

31. Niemann-Pick Disease (NPD) Market Other Major And Innovative Companies

• 31.1. Myriad Genetics
• 31.2. CENTOGENE N.V.
• 31.3. The Florey Institute of Neuroscience and Mental Health
• 31.4. National Organization for Rare Disorders (NORD)
• 31.5. Evox Therapeutics Limited
• 31.6. Zevra Therapeutics Inc.
• 31.7. IntraBio Inc.
• 31.8. Dipharma SA
• 31.9. Okklo Life Sciences
• 31.10. Bloomsbury Genetic Therapies Ltd.
• 31.11. Azafaros A.G
• 31.12. Cyclo Therapeutics Inc.
• 31.13. Mandos Health
• 31.14. CarelonRx
• 31.15. Rainbow Children's Hospital

32. Global Niemann-Pick Disease (NPD) Market Competitive Benchmarking And Dashboard

33. Key Mergers And Acquisitions In The Niemann-Pick Disease (NPD) Market

34. Recent Developments In The Niemann-Pick Disease (NPD) Market

35. Niemann-Pick Disease (NPD) Market High Potential Countries, Segments and Strategies

• 35.1 Niemann-Pick Disease (NPD) Market In 2029 - Countries Offering Most New Opportunities
• 35.2 Niemann-Pick Disease (NPD) Market In 2029 - Segments Offering Most New Opportunities
• 35.3 Niemann-Pick Disease (NPD) Market In 2029 - Growth Strategies
  • 35.3.1 Market Trend Based Strategies
  • 35.3.2 Competitor Strategies

36. Appendix

• 36.1. Abbreviations
• 36.2. Currencies
• 36.3. Historic And Forecast Inflation Rates
• 36.4. Research Inquiries
• 36.5. The Business Research Company
• 36.6. Copyright And Disclaimer
• 250617_r34909_Niemann_Pick_Disease_NPD_GMR_2025