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ライソゾーム病(リソソーム蓄積症)治療の世界市場、規模、シェア、動向、産業分析レポート:疾患タイプ別、治療タイプ別、エンドユーザー別、地域別 - 市場予測、2025年~2034年

Lysosomal Storage Disease Treatment Market Size, Share, Trends, & Industry Analysis Report By Disease Type, By Type of Therapy, By End User, and By Region - Market Forecast, 2025-2034


出版日
ページ情報
英文 129 Pages
納期
即日から翌営業日
カスタマイズ可能
価格
価格表記: USDを日本円(税抜)に換算
本日の銀行送金レート: 1USD=148.66円
ライソゾーム病(リソソーム蓄積症)治療の世界市場、規模、シェア、動向、産業分析レポート:疾患タイプ別、治療タイプ別、エンドユーザー別、地域別 - 市場予測、2025年~2034年
出版日: 2025年07月01日
発行: Polaris Market Research
ページ情報: 英文 129 Pages
納期: 即日から翌営業日
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  • 概要
  • 図表
  • 目次
概要

Polaris Market Research社の最新調査によると、ライソゾーム病(リソソーム蓄積症)治療の市場規模は2034年までに68億米ドルに達する見込みです。この調査レポートは、現在の市場力学を詳細に洞察し、将来の市場成長に関する分析を提供しています。

ライソゾーム病治療市場は、製薬企業や研究開発機関が希少な遺伝性疾患への対処を目的とした新たな治療法を開発する中で、着実な進展を見せています。認知度の向上、患者擁護の高まり、支持的な規制の枠組みが、医薬品の承認を加速し、革新的な治療法へのアクセスを改善するのに役立っています。

バイオテクノロジーと個別化医療への投資が増加し、市場の焦点は対症療法から長期的な疾病管理と潜在的な治療法の開発へと移っています。この進化は、ゴーシェ病、ファブリー病、ポンペ病などの疾患に対して、患者の転帰を改善し、より効果的で的を絞った治療法を提供することへの強い後押しを反映しています。

ライソゾーム病治療市場レポートハイライト

疾患タイプ別では、ゴーシェ病が2024年に市場を席巻します。これは、世界的に広く普及していることと、確立された治療エコシステムが存在することが背景にあります。

治療タイプ別では、酵素補充療法(ERT)分野が2024年の市場を独占しました。これは、さまざまなライソゾーム貯蔵障害の管理において採用が増加していることが背景にあります。

エンドユーザー別では、酵素補充療法や幹細胞を用いた治療など、専門的な介入を提供する病院分野が2024年の市場を独占しました。

北米は、希少遺伝性疾患の治療を進めるバイオテクノロジー企業や製薬企業の強い存在感により、2024年の世界のライソゾーム貯蔵症治療市場で36.98%の大半のシェアを占めました。

アジア太平洋地域は6.13%の市場シェアを占めましたが、これは医療インフラの継続的な改善と高度な診断能力へのアクセスによるものです。

世界の主要市場企業には、 Alexion Pharmaceuticals, Inc., Amicus Therapeutics, Inc., BioMarin Pharmaceutical Inc., Eli Lilly and Company, Johnson & Johnson (Actelion Pharmaceuticals Ltd.), Merck & Co., Inc., Novartis AG, Pfizer Inc., Sanofi (Genzyme Corporation), Sigilon Therapeutics, Inc., Takeda Pharmaceutical Company Limited (Shire Plc), Chiesi Farmaceutici S.p.A., Orphazyme A/S, Protalix BioTherapeutics, Inc., Ultragenyx Pharmaceutical Inc.などがあります。

目次

第1章 イントロダクション

第2章 エグゼクティブサマリー

第3章 調査手法

第4章 世界のライソゾーム病治療市場の洞察

  • 市場スナップショット
  • ライソゾーム病治療市場力学
    • 促進要因と機会
      • 希少遺伝性疾患の発生率の上昇
      • 酵素補充療法(ERT)の進歩
    • 抑制要因と課題
      • 高額な治療費と限られた償還
  • PESTEL分析
  • ライソゾーム病治療市場の動向
  • バリューチェーン分析

第5章 世界のライソゾーム病治療市場:疾患タイプ別

  • 主な調査結果
  • イントロダクション
  • ゴーシェ病
  • ファブリー病
  • ポンペ症候群
  • ムコ多糖症
  • その他

第6章 世界のライソゾーム病治療市場:治療タイプ別

  • 主な調査結果
  • イントロダクション
  • 酵素補充療法
  • 幹細胞療法
  • 基質還元療法
  • その他

第7章 世界のライソゾーム病治療市場:エンドユーザー別

  • 主な調査結果
  • イントロダクション
  • 病院
  • クリニック
  • その他

第8章 世界のライソゾーム病治療市場:地域別

  • 主な調査結果
  • イントロダクション
    • ライソゾーム病治療市場評価:地域別、2020-2034年
  • 北米
    • 北米:疾患タイプ別、2020~2034年
    • 北米:治療タイプ別、2020年~2034年
    • 北米:エンドユーザー別、2020~2034年
    • 米国
    • カナダ
  • 欧州
    • 欧州:疾患タイプ別、2020~2034年
    • 欧州:治療タイプ別、2020~2034年
    • 欧州:エンドユーザー別、2020~2034年
    • 英国
    • フランス
    • ドイツ
    • イタリア
    • スペイン
    • オランダ
    • ロシア
    • その他欧州
  • アジア太平洋地域
    • アジア太平洋地域:疾病タイプ別、2020~2034年
    • アジア太平洋地域:治療タイプ別、2020年~2034年
    • アジア太平洋地域:エンドユーザー別、2020~2034年
    • 中国
    • インド
    • マレーシア
    • 日本
    • インドネシア
    • 韓国
    • オーストラリア
    • その他アジア太平洋地域
  • 中東・アフリカ
    • 中東・アフリカ:疾病タイプ別、2020~2034年
    • 中東・アフリカ:治療タイプ別、2020~2034年
    • 中東・アフリカ:エンドユーザー別、2020~2034年
    • サウジアラビア
    • アラブ首長国連邦
    • イスラエル
    • 南アフリカ
    • その他中東・アフリカ
  • ラテンアメリカ
    • ラテンアメリカ:疾病タイプ別、2020-2034年
    • ラテンアメリカ:治療タイプ別、2020-2034年
    • ラテンアメリカ:エンドユーザー別、2020~2034年
    • メキシコ
    • ブラジル
    • アルゼンチン
    • その他ラテンアメリカ

第9章 競合情勢

  • 拡大と買収の分析
    • 拡大
    • 買収
  • 提携/協業/合意/公開

第10章 企業プロファイル

  • Alexion Pharmaceuticals, Inc.
  • Amicus Therapeutics, Inc.
  • BioMarin Pharmaceutical Inc.
  • Eli Lilly and Company
  • Johnson & Johnson(Actelion Pharmaceuticals Ltd.)
  • Merck & Co., Inc.
  • Novartis AG
  • Pfizer Inc.
  • Sanofi(Genzyme Corporation)
  • Sigilon Therapeutics, Inc.
  • Takeda Pharmaceutical Company Limited(Shire Plc)
  • Chiesi Farmaceutici S.p.A.
図表

List of Tables:

  • Table 1 Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 2 Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 3 Global Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 4 North America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 5 North America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 6 North America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 7 U.S.: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 8 U.S.: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 9 U.S.: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 10 Canada: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 11 Canada: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 12 Canada: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 13 Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 14 Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 15 Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 16 UK: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 17 UK: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 18 UK: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 19 France: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 20 France: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 21 France: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 22 Germany: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 23 Germany: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 24 Germany: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 25 Italy: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 26 Italy: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 27 Italy: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 28 Spain: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 29 Spain: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 30 Spain: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 31 Netherlands: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 32 Netherlands: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 33 Netherlands: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 34 Russia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 35 Russia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 36 Russia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 37 Rest of Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 38 Rest of Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 39 Rest of Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 40 Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 41 Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 42 Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 43 China: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 44 China: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 45 China: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 46 India: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 47 India: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 48 India: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 49 Malaysia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 50 Malaysia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 51 Malaysia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 52 Japan: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 53 Japan: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 54 Japan: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 55 Indonesia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 56 Indonesia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 57 Indonesia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 58 South Korea: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 59 South Korea: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 60 South Korea: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 61 Australia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 62 Australia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 63 Australia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 64 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 65 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 66 Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 67 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 68 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 69 Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 70 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 71 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 72 Saudi Arabia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 73 UAE: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 74 UAE: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 75 UAE: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 76 Israel: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 77 Israel: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 78 Israel: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 79 South Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 80 South Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 81 South Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 82 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 83 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 84 Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 85 Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 86 Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 87 Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 88 Mexico: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 89 Mexico: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 90 Mexico: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 91 Brazil: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 92 Brazil: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 93 Brazil: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 94 Argentina: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 95 Argentina: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 96 Argentina: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • Table 97 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • Table 98 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • Table 99 Rest of Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)

List of Figures:

  • Figure 1. Global Lysosomal Storage Disease Treatment Market, 2020-2034 (USD Billion)
  • Figure 2. Integrated Ecosystem
  • Figure 3. Research Methodology: Top-Down & Bottom-Up Price
  • Figure 4. Market by Geography
  • Figure 5. Porter's Five Forces
  • Figure 6. Market by Disease Type
  • Figure 7. Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2024 & 2034 (USD Billion)
  • Figure 8. Market by Type of Therapy
  • Figure 9. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2024 & 2034 (USD Billion)
  • Figure 10. Market by End User
  • Figure 11. Global Lysosomal Storage Disease Treatment Market, by End User, 2024 & 2034 (USD Billion)
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目次
Product Code: PM6066

The lysosomal storage disease treatment market size is expected to reach USD 6.80 Billion by 2034, according to a new study by Polaris Market Research. The report "Lysosomal Storage Disease Treatment Market Size, Share, Trends, & Industry Analysis Report By Disease Type (Gaucher's Diseases, Fabry Diseases, Pompe's Syndrome, Mucopolysaccharidosis, and Others), By Type of Therapy, By End User, and By Region - Market Forecast, 2025-2034" gives a detailed insight into current market dynamics and provides analysis on future market growth.

The lysosomal storage disease (LSD) treatment market is witnessing steady progress as pharmaceutical companies and research institutions develop new therapies aimed at addressing rare genetic disorders. Growing awareness, increasing patient advocacy, and supportive regulatory frameworks are helping accelerate drug approvals and improve access to innovative treatments.

Rising investments in biotechnology and personalized medicine are shifting the market focus beyond symptom control toward long-term disease management and the development of potential cures. This evolution reflects a strong push toward improving patient outcomes and delivering more effective, targeted therapies for conditions such as Gaucher disease, Fabry disease, and Pompe disease.

Lysosomal Storage Disease Treatment Market Report Highlights

Based on disease type, gaucher's disease segment dominated the market in 2024, driven by its wider global prevalence and the presence of an established therapeutic ecosystem.

In terms of type of therapy, the enzyme replacement therapy (ERT) segment dominated the market in 2024. This is driven by the increasing adoption in managing various lysosomal storage disorders.

In terms of end user, the hospital segment dominated the market in 2024, attributed to delivery of specialized interventions such as enzyme replacement therapies and stem cell-based procedures.

North America accounted for the majority share of 36.98 in the global lysosomal storage disease treatment market in 2024, due to the strong presence of biotech and pharmaceutical firms advancing treatments for rare genetic conditions.

Asia Pacific held 6.13% market share, owing to ongoing improvements in healthcare infrastructure and access to advanced diagnostic capabilities.

A few global key market players include Alexion Pharmaceuticals, Inc., Amicus Therapeutics, Inc., BioMarin Pharmaceutical Inc., Eli Lilly and Company, Johnson & Johnson (Actelion Pharmaceuticals Ltd.), Merck & Co., Inc., Novartis AG, Pfizer Inc., Sanofi (Genzyme Corporation), Sigilon Therapeutics, Inc., Takeda Pharmaceutical Company Limited (Shire Plc), Chiesi Farmaceutici S.p.A., Orphazyme A/S, Protalix BioTherapeutics, Inc., and Ultragenyx Pharmaceutical Inc.

Polaris Market Research has segmented the market report on the basis of disease type, type of therapy, end user, and region:

By Disease Type Outlook (Revenue, USD Billion, 2020-2034)

Gaucher's Diseases

Fabry Diseases

Pompe's Syndrome

Mucopolysaccharidosis

Others

By Type of Therapy Outlook (Revenue, USD Billion, 2020-2034)

Enzyme Replacement Therapy

Stem Cell Therapy

Substrate Reduction Therapy

Others

By End User Outlook (Revenue, USD Billion, 2020-2034)

Hospitals

Clinics

Others

By Regional Outlook (Revenue, USD Billion, 2020-2034)

North America

US

Canada

Europe

Germany

France

UK

Italy

Spain

Netherlands

Russia

Rest of Europe

Asia Pacific

China

Japan

India

Malaysia

South Korea

Indonesia

Australia

Vietnam

Rest of Asia Pacific

Middle East & Africa

Saudi Arabia

UAE

Israel

South Africa

Rest of Middle East & Africa

Latin America

Mexico

Brazil

Argentina

Rest of Latin America

Table of Contents

1. Introduction

  • 1.1. Report Description
    • 1.1.1. Objectives of the Study
    • 1.1.2. Market Scope
    • 1.1.3. Assumptions
  • 1.2. Stakeholders

2. Executive Summary

  • 2.1. Market Highlights

3. Research Methodology

  • 3.1. Overview
    • 3.1.1. Data Mining
  • 3.2. Data Sources
    • 3.2.1. Primary Sources
    • 3.2.2. Secondary Sources

4. Global Lysosomal Storage Disease Treatment Market Insights

  • 4.1. Lysosomal Storage Disease Treatment Market - Market Snapshot
  • 4.2. Lysosomal Storage Disease Treatment Market Dynamics
    • 4.2.1. Drivers and Opportunities
      • 4.2.1.1. Rising Incidence of Rare Genetic Disorders
      • 4.2.1.2. Advancements in Enzyme Replacement Therapy (ERT)
    • 4.2.2. Restraints and Challenges
      • 4.2.2.1. High Treatment Costs and Limited Reimbursement
  • 4.3. Porter's Five Forces Analysis
    • 4.3.1. Bargaining Power of Suppliers (Moderate)
    • 4.3.2. Threats of New Entrants: (Low)
    • 4.3.3. Bargaining Power of Buyers (Moderate)
    • 4.3.4. Threat of Substitute (Moderate)
    • 4.3.5. Rivalry among existing firms (High)
  • 4.4. PESTEL Analysis
  • 4.5. Lysosomal Storage Disease Treatment Market Trends
  • 4.6. Value Chain Analysis

5. Global Lysosomal Storage Disease Treatment Market, by Disease Type

  • 5.1. Key Findings
  • 5.2. Introduction
    • 5.2.1. Global Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
  • 5.3. Gaucher's Diseases
    • 5.3.1. Global Lysosomal Storage Disease Treatment Market, by Gaucher's Diseases, by Region, 2020-2034 (USD Billion)
  • 5.4. Fabry Diseases
    • 5.4.1. Global Lysosomal Storage Disease Treatment Market, by Fabry Diseases, by Region, 2020-2034 (USD Billion)
  • 5.5. Pompe's Syndrome
    • 5.5.1. Global Lysosomal Storage Disease Treatment Market, by Pompe's Syndrome, by Region, 2020-2034 (USD Billion)
  • 5.6. Mucopolysaccharidosis
    • 5.6.1. Global Lysosomal Storage Disease Treatment Market, by Mucopolysaccharidosis, by Region, 2020-2034 (USD Billion)
  • 5.7. Others
    • 5.7.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

6. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy

  • 6.1. Key Findings
  • 6.2. Introduction
    • 6.2.1. Global Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
  • 6.3. Enzyme Replacement Therapy
    • 6.3.1. Global Lysosomal Storage Disease Treatment Market, by Enzyme Replacement Therapy, by Region, 2020-2034 (USD Billion)
  • 6.4. Stem Cell Therapy
    • 6.4.1. Global Lysosomal Storage Disease Treatment Market, by Stem Cell Therapy, by Region, 2020-2034 (USD Billion)
  • 6.5. Substrate Reduction Therapy
    • 6.5.1. Global Lysosomal Storage Disease Treatment Market, by Substrate Reduction Therapy, by Region, 2020-2034 (USD Billion)
  • 6.6. Others
    • 6.6.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

7. Global Lysosomal Storage Disease Treatment Market, by End User

  • 7.1. Key Findings
  • 7.2. Introduction
    • 7.2.1. Global Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 7.3. Hospitals
    • 7.3.1. Global Lysosomal Storage Disease Treatment Market, by Hospitals, by Region, 2020-2034 (USD Billion)
  • 7.4. Clinics
    • 7.4.1. Global Lysosomal Storage Disease Treatment Market, by Clinics, by Region, 2020-2034 (USD Billion)
  • 7.5. Others
    • 7.5.1. Global Lysosomal Storage Disease Treatment Market, by Others, by Region, 2020-2034 (USD Billion)

8. Global Lysosomal Storage Disease Treatment Market, by Geography

  • 8.1. Key Findings
  • 8.2. Introduction
    • 8.2.1. Lysosomal Storage Disease Treatment Market Assessment, By Geography, 2020-2034 (USD Billion)
  • 8.3. Lysosomal Storage Disease Treatment Market - North America
    • 8.3.1. North America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.3.2. North America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.3.3. North America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.3.4. Lysosomal Storage Disease Treatment Market - U.S.
      • 8.3.4.1. U.S.: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.3.4.2. U.S.: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.3.4.3. U.S.: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.3.5. Lysosomal Storage Disease Treatment Market - Canada
      • 8.3.5.1. Canada: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.3.5.2. Canada: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.3.5.3. Canada: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.4. Lysosomal Storage Disease Treatment Market - Europe
    • 8.4.1. Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.4.2. Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.4.3. Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.4. Lysosomal Storage Disease Treatment Market - UK
      • 8.4.4.1. UK: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.4.2. UK: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.4.3. UK: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.5. Lysosomal Storage Disease Treatment Market - France
      • 8.4.5.1. France: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.5.2. France: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.5.3. France: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.6. Lysosomal Storage Disease Treatment Market - Germany
      • 8.4.6.1. Germany: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.6.2. Germany: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.6.3. Germany: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.7. Lysosomal Storage Disease Treatment Market - Italy
      • 8.4.7.1. Italy: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.7.2. Italy: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.7.3. Italy: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.8. Lysosomal Storage Disease Treatment Market - Spain
      • 8.4.8.1. Spain: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.8.2. Spain: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.8.3. Spain: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.9. Lysosomal Storage Disease Treatment Market - Netherlands
      • 8.4.9.1. Netherlands: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.9.2. Netherlands: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.9.3. Netherlands: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.10. Lysosomal Storage Disease Treatment Market - Russia
      • 8.4.10.1. Russia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.10.2. Russia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.10.3. Russia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.4.11. Lysosomal Storage Disease Treatment Market - Rest of Europe
      • 8.4.11.1. Rest of Europe: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.4.11.2. Rest of Europe: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.4.11.3. Rest of Europe: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.5. Lysosomal Storage Disease Treatment Market - Asia Pacific
    • 8.5.1. Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.5.2. Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.5.3. Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.4. Lysosomal Storage Disease Treatment Market - China
      • 8.5.4.1. China: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.4.2. China: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.4.3. China: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.5. Lysosomal Storage Disease Treatment Market - India
      • 8.5.5.1. India: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.5.2. India: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.5.3. India: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.6. Lysosomal Storage Disease Treatment Market - Malaysia
      • 8.5.6.1. Malaysia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.6.2. Malaysia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.6.3. Malaysia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.7. Lysosomal Storage Disease Treatment Market - Japan
      • 8.5.7.1. Japan: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.7.2. Japan: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.7.3. Japan: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.8. Lysosomal Storage Disease Treatment Market - Indonesia
      • 8.5.8.1. Indonesia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.8.2. Indonesia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.8.3. Indonesia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.9. Lysosomal Storage Disease Treatment Market - South Korea
      • 8.5.9.1. South Korea: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.9.2. South Korea: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.9.3. South Korea: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.10. Lysosomal Storage Disease Treatment Market - Australia
      • 8.5.10.1. Australia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.10.2. Australia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.10.3. Australia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.5.11. Lysosomal Storage Disease Treatment Market - Rest of Asia Pacific
      • 8.5.11.1. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.5.11.2. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.5.11.3. Rest of Asia Pacific: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.6. Lysosomal Storage Disease Treatment Market - Middle East & Africa
    • 8.6.1. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.6.2. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.6.3. Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.4. Lysosomal Storage Disease Treatment Market - Saudi Arabia
      • 8.6.4.1. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.4.2. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.4.3. Saudi Arabia: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.5. Lysosomal Storage Disease Treatment Market - UAE
      • 8.6.5.1. UAE: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.5.2. UAE: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.5.3. UAE: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.6. Lysosomal Storage Disease Treatment Market - Israel
      • 8.6.6.1. Israel: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.6.2. Israel: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.6.3. Israel: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.7. Lysosomal Storage Disease Treatment Market - South Africa
      • 8.6.7.1. South Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.7.2. South Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.7.3. South Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.6.8. Lysosomal Storage Disease Treatment Market - Rest of Middle East & Africa
      • 8.6.8.1. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.6.8.2. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.6.8.3. Rest of Middle East & Africa: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
  • 8.7. Lysosomal Storage Disease Treatment Market - Latin America
    • 8.7.1. Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
    • 8.7.2. Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
    • 8.7.3. Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.4. Lysosomal Storage Disease Treatment Market - Mexico
      • 8.7.4.1. Mexico: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.4.2. Mexico: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.4.3. Mexico: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.5. Lysosomal Storage Disease Treatment Market - Brazil
      • 8.7.5.1. Brazil: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.5.2. Brazil: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.5.3. Brazil: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.6. Lysosomal Storage Disease Treatment Market - Argentina
      • 8.7.6.1. Argentina: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.6.2. Argentina: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.6.3. Argentina: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)
    • 8.7.7. Lysosomal Storage Disease Treatment Market - Rest of Latin America
      • 8.7.7.1. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Disease Type, 2020-2034 (USD Billion)
      • 8.7.7.2. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by Type of Therapy, 2020-2034 (USD Billion)
      • 8.7.7.3. Rest of Latin America: Lysosomal Storage Disease Treatment Market, by End User, 2020-2034 (USD Billion)

9. Competitive Landscape

  • 9.1. Expansion and Acquisition Analysis
    • 9.1.1. Expansion
    • 9.1.2. Acquisitions
  • 9.2. Partnerships/Collaborations/Agreements/Exhibitions

10. Company Profiles

  • 10.1. Alexion Pharmaceuticals, Inc.
    • 10.1.1. Company Overview
    • 10.1.2. Financial Performance
    • 10.1.3. Disease Type Benchmarking
    • 10.1.4. Recent Development
  • 10.2. Amicus Therapeutics, Inc.
    • 10.2.1. Company Overview
    • 10.2.2. Financial Performance
    • 10.2.3. Disease Type Benchmarking
    • 10.2.4. Recent Development
  • 10.3. BioMarin Pharmaceutical Inc.
    • 10.3.1. Company Overview
    • 10.3.2. Financial Performance
    • 10.3.3. Disease Type Benchmarking
    • 10.3.4. Recent Development
  • 10.4. Eli Lilly and Company
    • 10.4.1. Company Overview
    • 10.4.2. Financial Performance
    • 10.4.3. Disease Type Benchmarking
    • 10.4.4. Recent Development
  • 10.5. Johnson & Johnson (Actelion Pharmaceuticals Ltd.)
    • 10.5.1. Company Overview
    • 10.5.2. Financial Performance
    • 10.5.3. Disease Type Benchmarking
    • 10.5.4. Recent Development
  • 10.6. Merck & Co., Inc.
    • 10.6.1. Company Overview
    • 10.6.2. Financial Performance
    • 10.6.3. Disease Type Benchmarking
    • 10.6.4. Recent Development
  • 10.7. Novartis AG
    • 10.7.1. Company Overview
    • 10.7.2. Financial Performance
    • 10.7.3. Disease Type Benchmarking
    • 10.7.4. Recent Development
  • 10.8. Pfizer Inc.
    • 10.8.1. Company Overview
    • 10.8.2. Financial Performance
    • 10.8.3. Disease Type Benchmarking
    • 10.8.4. Recent Development
  • 10.9. Sanofi (Genzyme Corporation)
    • 10.9.1. Company Overview
    • 10.9.2. Financial Performance
    • 10.9.3. Disease Type Benchmarking
    • 10.9.4. Recent Development
  • 10.10. Sigilon Therapeutics, Inc.
    • 10.10.1. Company Overview
    • 10.10.2. Financial Performance
    • 10.10.3. Disease Type Benchmarking
    • 10.10.4. Recent Development
  • 10.11. Takeda Pharmaceutical Company Limited (Shire Plc)
    • 10.11.1. Company Overview
    • 10.11.2. Financial Performance
    • 10.11.3. Disease Type Benchmarking
    • 10.11.4. Recent Development
  • 10.12. Chiesi Farmaceutici S.p.A.
    • 10.12.1. Company Overview
    • 10.12.2. Financial Performance
    • 10.12.3. Disease Type Benchmarking
    • 10.12.4. Recent Development