デフォルト表紙
市場調査レポート
商品コード
1602658

アルファ型マンノシドーシスの市場:治療タイプ、適応症、エンドユーザー別-2025-2030年の世界予測

Alpha Mannosidosis Market by Treatment Type (Bone Marrow Transplant, Enzyme Replacement Therapy), Indication (Type I, Type II, Type III), End-User - Global Forecast 2025-2030


出版日
発行
360iResearch
ページ情報
英文 184 Pages
納期
即日から翌営業日
カスタマイズ可能
適宜更新あり
価格
価格表記: USDを日本円(税抜)に換算
本日の銀行送金レート: 1USD=143.57円
アルファ型マンノシドーシスの市場:治療タイプ、適応症、エンドユーザー別-2025-2030年の世界予測
出版日: 2024年10月31日
発行: 360iResearch
ページ情報: 英文 184 Pages
納期: 即日から翌営業日
GIIご利用のメリット
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  • 概要
  • 図表
  • 目次
概要

アルファ型マンノシドーシス市場は、2023年に68億1,000万米ドルと評価され、2024年には74億9,000万米ドルに達すると予測され、CAGR 10.82%で成長し、2030年には139億8,000万米ドルに達すると予測されています。

アルファ型マンノシドーシスは、MAN2B1遺伝子の変異によって引き起こされるまれな遺伝子疾患で、リソソーム貯蔵の問題を引き起こします。この疾患は、知的障害から骨格異常まで様々な症状を引き起こします。市場には、これらの症状に対処する治療薬、酵素補充療法、支持療法が含まれます。市場成長の必要性は、新規治療への需要と早期診断の進歩によってもたらされます。調査用途は主に患者のQOL向上と寿命延長であり、最終用途は主に専門ヘルスケア施設と研究機関です。市場成長は、認知度の向上、希少疾患に対する資金援助、ゲノムおよび分子医学の進歩に影響されます。希少疾病用医薬品の指定や助成金のような規制上の優遇措置が増加していることから、機会は熟しています。さらに、バイオテクノロジー企業とヘルスケアプロバイダーとのパートナーシップは、治療法の開発とアクセシビリティを促進するために不可欠です。しかし、市場拡大には、高額な治療費、限られた患者数、新治療の市場投入までの期間を長期化させる厳しい規制経路などの制約があります。重要な課題は、包括的な世界登録の欠如が患者層の理解を妨げていることです。イノベーションは、遺伝子治療と精密医療に焦点を当てた、費用対効果が高く患者に優しい治療法の開発に向けられるのが最善です。さらに、臨床試験でビッグデータとAIを活用すれば、開発期間を短縮できる可能性があります。企業はまた、患者エンゲージメント・プラットフォームを革新し、アドヒアランスとアウトカムを向上させる可能性もあります。この市場の性質は患者中心で専門性が高いため、研究機関、製薬会社、患者支援団体間の強固な連携が必要となります。このような力学をうまく利用し、強固な利害関係者の協力と患者中心のソリューションに投資することで、市場の成長を促進することができるため、企業はこのようなニッチ分野で戦略的に地位を確立することが不可欠となります。

主な市場の統計
基準年[2023] 68億1,000万米ドル
予測年[2024] 74億9,000万米ドル
予測年[2030] 139億8,000万米ドル
CAGR(%) 10.82%

市場力学:急速に進化するアルファ型マンノシドーシス市場の主要市場インサイトを公開

アルファ型マンノシドーシス市場は、需要と供給のダイナミックな相互作用によって変貌を遂げています。このような市場力学の進化を理解することで、企業は十分な情報に基づいた投資決定、戦略的決定の精緻化、そして新たなビジネスチャンスの獲得に備えることができます。こうした動向を包括的に把握することで、企業は政治的、地理的、技術的、社会的、経済的な領域にわたる様々なリスクを軽減することができるとともに、消費者行動とそれが製造コストや購買動向に与える影響をより明確に理解することができます。

  • 市場促進要因
    • 国民のアルファ型マンノシドーシスに対する意識の高まり
    • 近代的なヘルスケアインフラ整備のための投資の増加
  • 市場抑制要因
    • アルファ型マンノシドーシス治療に伴う高コスト
  • 市場機会
    • 希少遺伝性疾患を治療するための酵素補充療法の台頭
    • アルファ型マンノシドーシス治療薬の承認取得の増加
  • 市場の課題
    • 熟練したヘルスケア専門家の不足に伴う問題

ポーターの5つの力:アルファ型マンノシドーシス市場をナビゲートする戦略ツール

ポーターの5つの力フレームワークは、市場情勢の競合情勢を理解するための重要なツールです。ポーターのファイブフォース・フレームワークは、企業の競争力を評価し、戦略的機会を探るための明確な手法を提供します。このフレームワークは、企業が市場内の勢力図を評価し、新規事業の収益性を判断するのに役立ちます。これらの洞察により、企業は自社の強みを活かし、弱みに対処し、潜在的な課題を回避することができ、より強靭な市場でのポジショニングを確保することができます。

PESTLE分析:アルファ型マンノシドーシス市場における外部からの影響の把握

外部マクロ環境要因は、アルファ型マンノシドーシス市場の業績ダイナミクスを形成する上で極めて重要な役割を果たします。政治的、経済的、社会的、技術的、法的、環境的要因の分析は、これらの影響をナビゲートするために必要な情報を提供します。PESTLE要因を調査することで、企業は潜在的なリスクと機会をよりよく理解することができます。この分析により、企業は規制、消費者の嗜好、経済動向の変化を予測し、先を見越した積極的な意思決定を行う準備ができます。

市場シェア分析アルファ型マンノシドーシス市場における競合情勢の把握

アルファ型マンノシドーシス市場の詳細な市場シェア分析により、ベンダーの業績を包括的に評価することができます。企業は、収益、顧客ベース、成長率などの主要指標を比較することで、競争上のポジショニングを明らかにすることができます。この分析により、市場の集中、断片化、統合の動向が明らかになり、ベンダーは競争が激化する中で自社の地位を高める戦略的な意思決定を行うために必要な知見を得ることができます。

FPNVポジショニング・マトリックスアルファ型マンノシドーシス市場におけるベンダーのパフォーマンス評価

FPNVポジショニングマトリックスは、アルファ型マンノシドーシス市場においてベンダーを評価するための重要なツールです。このマトリックスにより、ビジネス組織はベンダーのビジネス戦略と製品満足度に基づき評価することで、目標に沿った十分な情報に基づいた意思決定を行うことができます。4つの象限によってベンダーを明確かつ正確にセグメント化し、戦略目標に最適なパートナーやソリューションを特定することができます。

戦略分析と推奨アルファ型マンノシドーシス市場における成功への道筋を描く

アルファ型マンノシドーシス市場の戦略分析は、世界市場でのプレゼンス強化を目指す企業にとって不可欠です。主要なリソース、能力、業績指標を見直すことで、企業は成長機会を特定し、改善に取り組むことができます。このアプローチにより、競合情勢における課題を克服し、新たなビジネスチャンスを活かして長期的な成功を収めるための体制を整えることができます。

本レポートでは、主要な注目分野を網羅した市場の包括的な分析を提供しています:

1.市場の浸透度:現在の市場環境の詳細なレビュー、主要企業による広範なデータ、市場でのリーチと全体的な影響力の評価。

2.市場の開拓度:新興市場における成長機会を特定し、既存分野における拡大可能性を評価し、将来の成長に向けた戦略的ロードマップを提供します。

3.市場の多様化:最近の製品発売、未開拓の地域、業界の主要な進歩、市場を形成する戦略的投資を分析します。

4.競合の評価と情報:競合情勢を徹底的に分析し、市場シェア、事業戦略、製品ポートフォリオ、認証、規制当局の承認、特許動向、主要企業の技術進歩などを検証します。

5.製品開発およびイノベーション:将来の市場成長を促進すると期待される最先端技術、研究開発活動、製品イノベーションをハイライトしています。

また、利害関係者が十分な情報を得た上で意思決定できるよう、重要な質問にも答えています:

1.現在の市場規模と今後の成長予測は?

2.最高の投資機会を提供する製品、セグメント、地域はどこか?

3.市場を形成する主な技術動向と規制の影響とは?

4.主要ベンダーの市場シェアと競合ポジションは?

5.ベンダーの市場参入・撤退戦略の原動力となる収益源と戦略的機会は何か?

目次

第1章 序文

第2章 調査手法

第3章 エグゼクティブサマリー

第4章 市場の概要

第5章 市場洞察

  • 市場力学
    • 促進要因
      • 国民の間でアルファ型マンノシドーシスの認知度が高まっている
      • 近代的なヘルスケアインフラの開発への投資増加
    • 抑制要因
      • アルファ型マンノシドーシス治療に伴う高コスト
    • 機会
      • 希少遺伝性疾患の治療に新たな酵素補充療法が登場
      • アルファ型マンノシドーシス医薬品の製品承認数の増加
    • 課題
      • 熟練したヘルスケア専門家の不足に関連する問題
  • 市場セグメンテーション分析
  • ポーターのファイブフォース分析
  • PESTEL分析
    • 政治的
    • 経済
    • 社交
    • 技術的
    • 法律上
    • 環境

第6章 アルファ型マンノシドーシスの市場治療の種類別

  • 骨髄移植
  • 酵素補充療法

第7章 アルファ型マンノシドーシスの市場適応症別

  • タイプI
  • タイプ II
  • タイプIII

第8章 アルファ型マンノシドーシスの市場:エンドユーザー別

  • 病院
  • 専門クリニック

第9章 南北アメリカのアルファ型マンノシドーシスの市場

  • アルゼンチン
  • ブラジル
  • カナダ
  • メキシコ
  • 米国

第10章 アジア太平洋地域のアルファ型マンノシドーシスの市場

  • オーストラリア
  • 中国
  • インド
  • インドネシア
  • 日本
  • マレーシア
  • フィリピン
  • シンガポール
  • 韓国
  • 台湾
  • タイ
  • ベトナム

第11章 欧州・中東・アフリカのアルファ型マンノシドーシスの市場

  • デンマーク
  • エジプト
  • フィンランド
  • フランス
  • ドイツ
  • イスラエル
  • イタリア
  • オランダ
  • ナイジェリア
  • ノルウェー
  • ポーランド
  • カタール
  • ロシア
  • サウジアラビア
  • 南アフリカ
  • スペイン
  • スウェーデン
  • スイス
  • トルコ
  • アラブ首長国連邦
  • 英国

第12章 競合情勢

  • 市場シェア分析2023
  • FPNVポジショニングマトリックス, 2023
  • 競合シナリオ分析
  • 戦略分析と提言

企業一覧

  • Chiesi Farmaceutici S.p.A.
  • Cigna Corporation
  • CVS Caremark
  • Kamada Ltd.
  • Orient Europharma(M)Sdn Bhd
  • Talaris Therapeutics Inc.
図表

LIST OF FIGURES

  • FIGURE 1. ALPHA MANNOSIDOSIS MARKET RESEARCH PROCESS
  • FIGURE 2. ALPHA MANNOSIDOSIS MARKET SIZE, 2023 VS 2030
  • FIGURE 3. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, 2018-2030 (USD MILLION)
  • FIGURE 4. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY REGION, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 5. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 6. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2023 VS 2030 (%)
  • FIGURE 7. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 8. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2023 VS 2030 (%)
  • FIGURE 9. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 10. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2023 VS 2030 (%)
  • FIGURE 11. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 12. AMERICAS ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
  • FIGURE 13. AMERICAS ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 14. UNITED STATES ALPHA MANNOSIDOSIS MARKET SIZE, BY STATE, 2023 VS 2030 (%)
  • FIGURE 15. UNITED STATES ALPHA MANNOSIDOSIS MARKET SIZE, BY STATE, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 16. ASIA-PACIFIC ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
  • FIGURE 17. ASIA-PACIFIC ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 18. EUROPE, MIDDLE EAST & AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
  • FIGURE 19. EUROPE, MIDDLE EAST & AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 20. ALPHA MANNOSIDOSIS MARKET SHARE, BY KEY PLAYER, 2023
  • FIGURE 21. ALPHA MANNOSIDOSIS MARKET, FPNV POSITIONING MATRIX, 2023

LIST OF TABLES

  • TABLE 1. ALPHA MANNOSIDOSIS MARKET SEGMENTATION & COVERAGE
  • TABLE 2. UNITED STATES DOLLAR EXCHANGE RATE, 2018-2023
  • TABLE 3. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, 2018-2030 (USD MILLION)
  • TABLE 4. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 5. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 6. ALPHA MANNOSIDOSIS MARKET DYNAMICS
  • TABLE 7. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 8. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY BONE MARROW TRANSPLANT, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 9. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 10. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 11. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY TYPE I, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 12. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY TYPE II, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 13. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY TYPE III, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 14. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 15. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY HOSPITALS, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 16. GLOBAL ALPHA MANNOSIDOSIS MARKET SIZE, BY SPECIALTY CLINICS, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 17. AMERICAS ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 18. AMERICAS ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 19. AMERICAS ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 20. AMERICAS ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 21. ARGENTINA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 22. ARGENTINA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 23. ARGENTINA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 24. BRAZIL ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 25. BRAZIL ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 26. BRAZIL ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 27. CANADA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 28. CANADA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 29. CANADA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 30. MEXICO ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 31. MEXICO ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 32. MEXICO ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 33. UNITED STATES ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 34. UNITED STATES ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 35. UNITED STATES ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 36. UNITED STATES ALPHA MANNOSIDOSIS MARKET SIZE, BY STATE, 2018-2030 (USD MILLION)
  • TABLE 37. ASIA-PACIFIC ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 38. ASIA-PACIFIC ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 39. ASIA-PACIFIC ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 40. ASIA-PACIFIC ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 41. AUSTRALIA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 42. AUSTRALIA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 43. AUSTRALIA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 44. CHINA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 45. CHINA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 46. CHINA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 47. INDIA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 48. INDIA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 49. INDIA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 50. INDONESIA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 51. INDONESIA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 52. INDONESIA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 53. JAPAN ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 54. JAPAN ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 55. JAPAN ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 56. MALAYSIA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 57. MALAYSIA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 58. MALAYSIA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 59. PHILIPPINES ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 60. PHILIPPINES ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 61. PHILIPPINES ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 62. SINGAPORE ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 63. SINGAPORE ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 64. SINGAPORE ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 65. SOUTH KOREA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 66. SOUTH KOREA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 67. SOUTH KOREA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 68. TAIWAN ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 69. TAIWAN ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 70. TAIWAN ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 71. THAILAND ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 72. THAILAND ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 73. THAILAND ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 74. VIETNAM ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 75. VIETNAM ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 76. VIETNAM ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 77. EUROPE, MIDDLE EAST & AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 78. EUROPE, MIDDLE EAST & AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 79. EUROPE, MIDDLE EAST & AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 80. EUROPE, MIDDLE EAST & AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 81. DENMARK ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 82. DENMARK ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 83. DENMARK ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 84. EGYPT ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 85. EGYPT ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 86. EGYPT ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 87. FINLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 88. FINLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 89. FINLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 90. FRANCE ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 91. FRANCE ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 92. FRANCE ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 93. GERMANY ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 94. GERMANY ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 95. GERMANY ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 96. ISRAEL ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 97. ISRAEL ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 98. ISRAEL ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 99. ITALY ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 100. ITALY ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 101. ITALY ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 102. NETHERLANDS ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 103. NETHERLANDS ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 104. NETHERLANDS ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 105. NIGERIA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 106. NIGERIA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 107. NIGERIA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 108. NORWAY ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 109. NORWAY ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 110. NORWAY ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 111. POLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 112. POLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 113. POLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 114. QATAR ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 115. QATAR ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 116. QATAR ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 117. RUSSIA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 118. RUSSIA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 119. RUSSIA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 120. SAUDI ARABIA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 121. SAUDI ARABIA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 122. SAUDI ARABIA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 123. SOUTH AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 124. SOUTH AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 125. SOUTH AFRICA ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 126. SPAIN ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 127. SPAIN ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 128. SPAIN ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 129. SWEDEN ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 130. SWEDEN ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 131. SWEDEN ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 132. SWITZERLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 133. SWITZERLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 134. SWITZERLAND ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 135. TURKEY ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 136. TURKEY ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 137. TURKEY ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 138. UNITED ARAB EMIRATES ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 139. UNITED ARAB EMIRATES ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 140. UNITED ARAB EMIRATES ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 141. UNITED KINGDOM ALPHA MANNOSIDOSIS MARKET SIZE, BY TREATMENT TYPE, 2018-2030 (USD MILLION)
  • TABLE 142. UNITED KINGDOM ALPHA MANNOSIDOSIS MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
  • TABLE 143. UNITED KINGDOM ALPHA MANNOSIDOSIS MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
  • TABLE 144. ALPHA MANNOSIDOSIS MARKET SHARE, BY KEY PLAYER, 2023
  • TABLE 145. ALPHA MANNOSIDOSIS MARKET, FPNV POSITIONING MATRIX, 2023
目次
Product Code: MRR-C002B1C99848

The Alpha Mannosidosis Market was valued at USD 6.81 billion in 2023, expected to reach USD 7.49 billion in 2024, and is projected to grow at a CAGR of 10.82%, to USD 13.98 billion by 2030.

Alpha Mannosidosis is a rare genetic disorder caused by mutations in the MAN2B1 gene, leading to lysosomal storage issues. This condition results in a spectrum of symptoms from intellectual disabilities to skeletal abnormalities. The market scope involves therapeutic drugs, enzyme replacement therapies, and supportive care addressing these symptoms. Necessity for market growth is driven by the demand for novel treatments and advances in early diagnosis. Applications primarily focus on improving patient quality of life and extending lifespan, with end-use primarily seen in specialized healthcare facilities and research institutions. Market growth is influenced by increased awareness, funding for rare diseases, and advancements in genomics and molecular medicine. Opportunities are ripe given the increase in regulatory incentives like orphan drug designations and grants. Moreover, partnerships between biotech firms and healthcare providers are essential to expedite therapy development and accessibility. However, market expansion faces limitations like high treatment costs, limited patient populations, and stringent regulatory pathways that can elongate the time-to-market for new treatments. A significant challenge is the current lack of comprehensive global registries that hinders understanding of patient demographics. Innovation is best directed towards developing cost-effective and patient-friendly therapies with the focus on gene therapies and precision medicine. Moreover, leveraging big data and AI in clinical trials could potentially reduce development times. Businesses could also innovate in patient engagement platforms, enhancing adherence and outcomes. The nature of this market is patient-centric and highly specialized, calling for robust collaborations between research institutions, pharmaceutical companies, and patient advocacy groups. Navigating these dynamics and investing in robust stakeholder collaborations and patient-centric solutions can propel market growth, making it imperative for firms to strategically position themselves in these niche areas.

KEY MARKET STATISTICS
Base Year [2023] USD 6.81 billion
Estimated Year [2024] USD 7.49 billion
Forecast Year [2030] USD 13.98 billion
CAGR (%) 10.82%

Market Dynamics: Unveiling Key Market Insights in the Rapidly Evolving Alpha Mannosidosis Market

The Alpha Mannosidosis Market is undergoing transformative changes driven by a dynamic interplay of supply and demand factors. Understanding these evolving market dynamics prepares business organizations to make informed investment decisions, refine strategic decisions, and seize new opportunities. By gaining a comprehensive view of these trends, business organizations can mitigate various risks across political, geographic, technical, social, and economic domains while also gaining a clearer understanding of consumer behavior and its impact on manufacturing costs and purchasing trends.

  • Market Drivers
    • Increasing awareness of alpha mannosidosis among population
    • Increasing investment to develop modern healthcare infrastructure
  • Market Restraints
    • High cost associated with alpha mannosidosis treatments
  • Market Opportunities
    • Emerging enzyme replacement therapy to treat rare genetic disorders
    • Rising product approvals for alpha mannosidosis medications
  • Market Challenges
    • Issues associated with dearth of skilled healthcare professionals

Porter's Five Forces: A Strategic Tool for Navigating the Alpha Mannosidosis Market

Porter's five forces framework is a critical tool for understanding the competitive landscape of the Alpha Mannosidosis Market. It offers business organizations with a clear methodology for evaluating their competitive positioning and exploring strategic opportunities. This framework helps businesses assess the power dynamics within the market and determine the profitability of new ventures. With these insights, business organizations can leverage their strengths, address weaknesses, and avoid potential challenges, ensuring a more resilient market positioning.

PESTLE Analysis: Navigating External Influences in the Alpha Mannosidosis Market

External macro-environmental factors play a pivotal role in shaping the performance dynamics of the Alpha Mannosidosis Market. Political, Economic, Social, Technological, Legal, and Environmental factors analysis provides the necessary information to navigate these influences. By examining PESTLE factors, businesses can better understand potential risks and opportunities. This analysis enables business organizations to anticipate changes in regulations, consumer preferences, and economic trends, ensuring they are prepared to make proactive, forward-thinking decisions.

Market Share Analysis: Understanding the Competitive Landscape in the Alpha Mannosidosis Market

A detailed market share analysis in the Alpha Mannosidosis Market provides a comprehensive assessment of vendors' performance. Companies can identify their competitive positioning by comparing key metrics, including revenue, customer base, and growth rates. This analysis highlights market concentration, fragmentation, and trends in consolidation, offering vendors the insights required to make strategic decisions that enhance their position in an increasingly competitive landscape.

FPNV Positioning Matrix: Evaluating Vendors' Performance in the Alpha Mannosidosis Market

The Forefront, Pathfinder, Niche, Vital (FPNV) Positioning Matrix is a critical tool for evaluating vendors within the Alpha Mannosidosis Market. This matrix enables business organizations to make well-informed decisions that align with their goals by assessing vendors based on their business strategy and product satisfaction. The four quadrants provide a clear and precise segmentation of vendors, helping users identify the right partners and solutions that best fit their strategic objectives.

Strategy Analysis & Recommendation: Charting a Path to Success in the Alpha Mannosidosis Market

A strategic analysis of the Alpha Mannosidosis Market is essential for businesses looking to strengthen their global market presence. By reviewing key resources, capabilities, and performance indicators, business organizations can identify growth opportunities and work toward improvement. This approach helps businesses navigate challenges in the competitive landscape and ensures they are well-positioned to capitalize on newer opportunities and drive long-term success.

Key Company Profiles

The report delves into recent significant developments in the Alpha Mannosidosis Market, highlighting leading vendors and their innovative profiles. These include Chiesi Farmaceutici S.p.A., Cigna Corporation, CVS Caremark, Kamada Ltd., Orient Europharma (M) Sdn Bhd, and Talaris Therapeutics Inc..

Market Segmentation & Coverage

This research report categorizes the Alpha Mannosidosis Market to forecast the revenues and analyze trends in each of the following sub-markets:

  • Based on Treatment Type, market is studied across Bone Marrow Transplant and Enzyme Replacement Therapy.
  • Based on Indication, market is studied across Type I, Type II, and Type III.
  • Based on End-User, market is studied across Hospitals and Specialty Clinics.
  • Based on Region, market is studied across Americas, Asia-Pacific, and Europe, Middle East & Africa. The Americas is further studied across Argentina, Brazil, Canada, Mexico, and United States. The United States is further studied across California, Florida, Illinois, New York, Ohio, Pennsylvania, and Texas. The Asia-Pacific is further studied across Australia, China, India, Indonesia, Japan, Malaysia, Philippines, Singapore, South Korea, Taiwan, Thailand, and Vietnam. The Europe, Middle East & Africa is further studied across Denmark, Egypt, Finland, France, Germany, Israel, Italy, Netherlands, Nigeria, Norway, Poland, Qatar, Russia, Saudi Arabia, South Africa, Spain, Sweden, Switzerland, Turkey, United Arab Emirates, and United Kingdom.

The report offers a comprehensive analysis of the market, covering key focus areas:

1. Market Penetration: A detailed review of the current market environment, including extensive data from top industry players, evaluating their market reach and overall influence.

2. Market Development: Identifies growth opportunities in emerging markets and assesses expansion potential in established sectors, providing a strategic roadmap for future growth.

3. Market Diversification: Analyzes recent product launches, untapped geographic regions, major industry advancements, and strategic investments reshaping the market.

4. Competitive Assessment & Intelligence: Provides a thorough analysis of the competitive landscape, examining market share, business strategies, product portfolios, certifications, regulatory approvals, patent trends, and technological advancements of key players.

5. Product Development & Innovation: Highlights cutting-edge technologies, R&D activities, and product innovations expected to drive future market growth.

The report also answers critical questions to aid stakeholders in making informed decisions:

1. What is the current market size, and what is the forecasted growth?

2. Which products, segments, and regions offer the best investment opportunities?

3. What are the key technology trends and regulatory influences shaping the market?

4. How do leading vendors rank in terms of market share and competitive positioning?

5. What revenue sources and strategic opportunities drive vendors' market entry or exit strategies?

Table of Contents

1. Preface

  • 1.1. Objectives of the Study
  • 1.2. Market Segmentation & Coverage
  • 1.3. Years Considered for the Study
  • 1.4. Currency & Pricing
  • 1.5. Language
  • 1.6. Stakeholders

2. Research Methodology

  • 2.1. Define: Research Objective
  • 2.2. Determine: Research Design
  • 2.3. Prepare: Research Instrument
  • 2.4. Collect: Data Source
  • 2.5. Analyze: Data Interpretation
  • 2.6. Formulate: Data Verification
  • 2.7. Publish: Research Report
  • 2.8. Repeat: Report Update

3. Executive Summary

4. Market Overview

5. Market Insights

  • 5.1. Market Dynamics
    • 5.1.1. Drivers
      • 5.1.1.1. Increasing awareness of alpha mannosidosis among population
      • 5.1.1.2. Increasing investment to develop modern healthcare infrastructure
    • 5.1.2. Restraints
      • 5.1.2.1. High cost associated with alpha mannosidosis treatments
    • 5.1.3. Opportunities
      • 5.1.3.1. Emerging enzyme replacement therapy to treat rare genetic disorders
      • 5.1.3.2. Rising product approvals for alpha mannosidosis medications
    • 5.1.4. Challenges
      • 5.1.4.1. Issues associated with dearth of skilled healthcare professionals
  • 5.2. Market Segmentation Analysis
  • 5.3. Porter's Five Forces Analysis
    • 5.3.1. Threat of New Entrants
    • 5.3.2. Threat of Substitutes
    • 5.3.3. Bargaining Power of Customers
    • 5.3.4. Bargaining Power of Suppliers
    • 5.3.5. Industry Rivalry
  • 5.4. PESTLE Analysis
    • 5.4.1. Political
    • 5.4.2. Economic
    • 5.4.3. Social
    • 5.4.4. Technological
    • 5.4.5. Legal
    • 5.4.6. Environmental

6. Alpha Mannosidosis Market, by Treatment Type

  • 6.1. Introduction
  • 6.2. Bone Marrow Transplant
  • 6.3. Enzyme Replacement Therapy

7. Alpha Mannosidosis Market, by Indication

  • 7.1. Introduction
  • 7.2. Type I
  • 7.3. Type II
  • 7.4. Type III

8. Alpha Mannosidosis Market, by End-User

  • 8.1. Introduction
  • 8.2. Hospitals
  • 8.3. Specialty Clinics

9. Americas Alpha Mannosidosis Market

  • 9.1. Introduction
  • 9.2. Argentina
  • 9.3. Brazil
  • 9.4. Canada
  • 9.5. Mexico
  • 9.6. United States

10. Asia-Pacific Alpha Mannosidosis Market

  • 10.1. Introduction
  • 10.2. Australia
  • 10.3. China
  • 10.4. India
  • 10.5. Indonesia
  • 10.6. Japan
  • 10.7. Malaysia
  • 10.8. Philippines
  • 10.9. Singapore
  • 10.10. South Korea
  • 10.11. Taiwan
  • 10.12. Thailand
  • 10.13. Vietnam

11. Europe, Middle East & Africa Alpha Mannosidosis Market

  • 11.1. Introduction
  • 11.2. Denmark
  • 11.3. Egypt
  • 11.4. Finland
  • 11.5. France
  • 11.6. Germany
  • 11.7. Israel
  • 11.8. Italy
  • 11.9. Netherlands
  • 11.10. Nigeria
  • 11.11. Norway
  • 11.12. Poland
  • 11.13. Qatar
  • 11.14. Russia
  • 11.15. Saudi Arabia
  • 11.16. South Africa
  • 11.17. Spain
  • 11.18. Sweden
  • 11.19. Switzerland
  • 11.20. Turkey
  • 11.21. United Arab Emirates
  • 11.22. United Kingdom

12. Competitive Landscape

  • 12.1. Market Share Analysis, 2023
  • 12.2. FPNV Positioning Matrix, 2023
  • 12.3. Competitive Scenario Analysis
  • 12.4. Strategy Analysis & Recommendation

Companies Mentioned

  • 1. Chiesi Farmaceutici S.p.A.
  • 2. Cigna Corporation
  • 3. CVS Caremark
  • 4. Kamada Ltd.
  • 5. Orient Europharma (M) Sdn Bhd
  • 6. Talaris Therapeutics Inc.