デフォルト表紙
市場調査レポート
商品コード
1598384

サラセミア治療市場:タイプ別、適応症別、エンドユーザー別-2025-2030年の世界予測

Thalassemia Treatment Market by Type (Blood Transfusion, Bone Marrow & Stem Cell Transplant, Iron Chelation), Indication Type (Alpha Thalassemia, Beta Thalassemia), End-Users - Global Forecast 2025-2030


出版日
発行
360iResearch
ページ情報
英文 199 Pages
納期
即日から翌営業日
カスタマイズ可能
適宜更新あり
価格
価格表記: USDを日本円(税抜)に換算
本日の銀行送金レート: 1USD=143.57円
サラセミア治療市場:タイプ別、適応症別、エンドユーザー別-2025-2030年の世界予測
出版日: 2024年10月31日
発行: 360iResearch
ページ情報: 英文 199 Pages
納期: 即日から翌営業日
GIIご利用のメリット
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  • 概要
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概要

サラセミア治療市場は、2023年に63億8,000万米ドルと評価され、2024年には70億6,000万米ドルに達すると予測され、CAGR 12.31%で成長し、2030年には143億8,000万米ドルに達すると予測されています。

サラセミア治療は、ヘモグロビン産生障害を特徴とし、貧血やその他の合併症を引き起こすこの遺伝性血液疾患の管理を目的とした医療戦略を包含しています。効果的なサラセミア治療の必要性は、患者の生活の質を改善し、定期的な輸血への依存を減らし、鉄過剰症のような合併症を予防する必要性によって推進されています。治療用途には、定期的な輸血、鉄キレート療法、新興の遺伝子治療が含まれ、最終用途は主に病院、専門クリニック、在宅医療の現場です。市場の洞察によると、遺伝子治療の進歩とアジア太平洋地域などにおけるサラセミア有病率の増加が主な成長要因です。さらに、パーソナライズされた治療計画を策定し、デジタルヘルス技術を統合して患者データと治療レジメンのアドヒアランスを管理することには大きな可能性があります。しかし、治療費の高騰、低所得国での認知度の低さ、新規治療に対する厳しい規制承認の必要性といった要因が市場成長の課題となっています。技術革新の主な分野としては、費用対効果の高い遺伝子編集技術の開発、より広範なサラセミア変異を標的とした治療法の考案、治療結果評価における予測分析のためのAIの活用などが挙げられます。企業は、研究開発努力を強化し、臨床試験を加速するための戦略的協力関係の構築に注力すべきです。新たな機会を捉えるためには、最新の技術的進歩と規制の変更に常に対応することが重要です。一方、教育プログラムを推進し、一般市民の認知度を高めることは、市場の抑制要因を緩和する一助となります。市場力学の性質はダイナミックであり、治療の合理化に向けた継続的な取り組みが、患者ケアの変革を目指すイノベーションの肥沃な土壌となっています。

主な市場の統計
基準年[2023] 63億8,000万米ドル
予測年[2024] 70億6,000万米ドル
予測年[2030] 143億8,000万米ドル
CAGR(%) 12.31%

市場力学:急速に進化するサラセミア治療市場の主要市場インサイトを公開

サラセミア治療市場は、需要と供給のダイナミックな相互作用によって変貌を遂げています。このような市場力学の進化を理解することで、企業は十分な情報に基づいた投資決定、戦略的決定の精緻化、そして新たなビジネスチャンスの獲得に備えることができます。こうした動向を包括的に把握することで、企業は政治的、地理的、技術的、社会的、経済的な領域にわたる様々なリスクを軽減することができるとともに、消費者行動とそれが製造コストや購買動向に与える影響についてより明確に理解することができます。

  • 市場促進要因
    • サラセミア疾患の人口増加
    • サラセミアの早期診断と治療に関する認識
    • ゲノム研究の重視の高まり
  • 市場抑制要因
    • サラセミア治療に伴う高コスト
  • 市場機会
    • 新規のサラセミア治療に対する承認数の増加
    • 各国におけるヘルスケアインフラ支出の増加
  • 市場の課題
    • サラセミア治療に伴う合併症の可能性

ポーターの5つの力:サラセミア治療市場をナビゲートする戦略ツール

ポーターの5つの力フレームワークは、市場情勢の競合情勢を理解するための重要なツールです。ポーターのファイブフォース・フレームワークは、企業の競争力を評価し、戦略的機会を探るための明確な手法を提供します。このフレームワークは、企業が市場内の勢力図を評価し、新規事業の収益性を判断するのに役立ちます。これらの洞察により、企業は自社の強みを活かし、弱みに対処し、潜在的な課題を回避することができ、より強靭な市場でのポジショニングを確保することができます。

PESTLE分析:サラセミア治療市場における外部からの影響の把握

外部マクロ環境要因は、サラセミア治療市場の業績ダイナミクスを形成する上で極めて重要な役割を果たします。政治的、経済的、社会的、技術的、法的、環境的要因の分析は、これらの影響をナビゲートするために必要な情報を提供します。PESTLE要因を調査することで、企業は潜在的なリスクと機会をよりよく理解することができます。この分析により、企業は規制、消費者の嗜好、経済動向の変化を予測し、先を見越した積極的な意思決定を行う準備ができます。

市場シェア分析サラセミア治療市場における競合情勢の把握

サラセミア治療市場の詳細な市場シェア分析により、ベンダーの業績を包括的に評価することができます。企業は、収益、顧客ベース、成長率などの主要指標を比較することで、競争上のポジショニングを明らかにすることができます。この分析により、市場の集中、断片化、統合の動向が明らかになり、ベンダーは競争が激化する中で自社の地位を高める戦略的意思決定を行うために必要な知見を得ることができます。

FPNVポジショニング・マトリックスサラセミア治療市場におけるベンダーのパフォーマンス評価

FPNVポジショニングマトリックスは、サラセミア治療市場においてベンダーを評価するための重要なツールです。このマトリックスにより、ビジネス組織はベンダーのビジネス戦略と製品満足度に基づき評価することで、目標に沿った十分な情報に基づいた意思決定を行うことができます。4つの象限によってベンダーを明確かつ正確にセグメント化し、戦略目標に最適なパートナーやソリューションを特定することができます。

戦略分析と推奨サラセミア治療市場における成功への道筋を描く

サラセミア治療市場の戦略分析は、世界市場でのプレゼンス強化を目指す企業にとって不可欠です。主要なリソース、能力、業績指標を見直すことで、企業は成長機会を特定し、改善に取り組むことができます。このアプローチにより、競合情勢における課題を克服し、新たなビジネスチャンスを活かして長期的な成功を収めるための体制を整えることができます。

本レポートでは、主要な注目分野を網羅した市場の包括的な分析を提供しています:

1.市場の浸透度:現在の市場環境の詳細なレビュー、主要企業による広範なデータ、市場でのリーチと全体的な影響力の評価。

2.市場の開拓度:新興市場における成長機会を特定し、既存分野における拡大可能性を評価し、将来の成長に向けた戦略的ロードマップを提供します。

3.市場の多様化:最近の製品発売、未開拓の地域、業界の主要な進歩、市場を形成する戦略的投資を分析します。

4.競合の評価と情報:競合情勢を徹底的に分析し、市場シェア、事業戦略、製品ポートフォリオ、認証、規制当局の承認、特許動向、主要企業の技術進歩などを検証します。

5.製品開発およびイノベーション:将来の市場成長を促進すると期待される最先端技術、研究開発活動、製品イノベーションをハイライトしています。

また、利害関係者が十分な情報を得た上で意思決定できるよう、重要な質問にも答えています:

1.現在の市場規模と今後の成長予測は?

2.最高の投資機会を提供する製品、セグメント、地域はどこか?

3.市場を形成する主な技術動向と規制の影響とは?

4.主要ベンダーの市場シェアと競合ポジションは?

5.ベンダーの市場参入・撤退戦略の原動力となる収益源と戦略的機会は何か?

目次

第1章 序文

第2章 調査手法

第3章 エグゼクティブサマリー

第4章 市場の概要

第5章 市場洞察

  • 市場力学
    • 促進要因
      • 人口におけるサラセミア疾患の発生率の上昇
      • サラセミアの早期診断と治療に関する意識
      • ゲノム調査の重要性の高まり
    • 抑制要因
      • サラセミア治療に伴う高額な費用
    • 機会
      • 新たなサラセミア治療薬の承認数が増加
      • 各国のヘルスケアインフラ支出の増加
    • 課題
      • サラセミア治療に伴う可能性のある合併症
  • 市場セグメンテーション分析
  • ポーターのファイブフォース分析
  • PESTEL分析
    • 政治的
    • 経済
    • 社交
    • 技術的
    • 法律上
    • 環境

第6章 サラセミア治療市場:タイプ別

  • 輸血
  • 骨髄および幹細胞移植
  • 鉄キレート化
  • ルスパテルセプト

第7章 サラセミア治療市場適応症の種類別

  • アルファサラセミア
  • ベータサラセミア

第8章 サラセミア治療市場:エンドユーザー別

  • 外来手術センター
  • 病院
  • 専門クリニック

第9章 南北アメリカのサラセミア治療市場

  • アルゼンチン
  • ブラジル
  • カナダ
  • メキシコ
  • 米国

第10章 アジア太平洋地域のサラセミア治療市場

  • オーストラリア
  • 中国
  • インド
  • インドネシア
  • 日本
  • マレーシア
  • フィリピン
  • シンガポール
  • 韓国
  • 台湾
  • タイ
  • ベトナム

第11章 欧州・中東・アフリカのサラセミア治療市場

  • デンマーク
  • エジプト
  • フィンランド
  • フランス
  • ドイツ
  • イスラエル
  • イタリア
  • オランダ
  • ナイジェリア
  • ノルウェー
  • ポーランド
  • カタール
  • ロシア
  • サウジアラビア
  • 南アフリカ
  • スペイン
  • スウェーデン
  • スイス
  • トルコ
  • アラブ首長国連邦
  • 英国

第12章 競合情勢

  • 市場シェア分析2023
  • FPNVポジショニングマトリックス, 2023
  • 競合シナリオ分析
  • 戦略分析と提言

企業一覧

  • ApoPharma Inc.
  • Bellicum Pharmaceuticals, Inc.
  • bluebird bio, Inc.
  • Bristol-Myers Squibb Company
  • CRISPR Therapeutics AG
  • Editas Medicine Inc.
  • Errant Gene Therapeutics LLC
  • Gamida Cell Ltd.
  • GL Pharma
  • Grifols International SA
  • Ionis Pharmaceuticals, Inc.
  • La Jolla Pharmaceutical Company
  • Lonza Group AG
  • Macsen Laboratories
  • Merck & Co., Inc.
  • Novartis AG
  • Novo Nordisk A/S
  • Pfizer, Inc.
  • Pharmascience Inc.
  • Rajasthan Antibiotics Ltd
  • Sangamo Therapeutics, Inc.
  • Sanofi S.A.
  • Taj Pharmaceuticals Limited
  • Teva Pharmaceutical Industries Ltd.
  • Vertex Pharmaceuticals Incorporated
図表

LIST OF FIGURES

  • FIGURE 1. THALASSEMIA TREATMENT MARKET RESEARCH PROCESS
  • FIGURE 2. THALASSEMIA TREATMENT MARKET SIZE, 2023 VS 2030
  • FIGURE 3. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, 2018-2030 (USD MILLION)
  • FIGURE 4. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY REGION, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 5. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 6. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2023 VS 2030 (%)
  • FIGURE 7. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 8. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2023 VS 2030 (%)
  • FIGURE 9. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 10. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2023 VS 2030 (%)
  • FIGURE 11. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 12. AMERICAS THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
  • FIGURE 13. AMERICAS THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 14. UNITED STATES THALASSEMIA TREATMENT MARKET SIZE, BY STATE, 2023 VS 2030 (%)
  • FIGURE 15. UNITED STATES THALASSEMIA TREATMENT MARKET SIZE, BY STATE, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 16. ASIA-PACIFIC THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
  • FIGURE 17. ASIA-PACIFIC THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 18. EUROPE, MIDDLE EAST & AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
  • FIGURE 19. EUROPE, MIDDLE EAST & AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
  • FIGURE 20. THALASSEMIA TREATMENT MARKET SHARE, BY KEY PLAYER, 2023
  • FIGURE 21. THALASSEMIA TREATMENT MARKET, FPNV POSITIONING MATRIX, 2023

LIST OF TABLES

  • TABLE 1. THALASSEMIA TREATMENT MARKET SEGMENTATION & COVERAGE
  • TABLE 2. UNITED STATES DOLLAR EXCHANGE RATE, 2018-2023
  • TABLE 3. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, 2018-2030 (USD MILLION)
  • TABLE 4. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 5. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 6. THALASSEMIA TREATMENT MARKET DYNAMICS
  • TABLE 7. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 8. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY BLOOD TRANSFUSION, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 9. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY BONE MARROW & STEM CELL TRANSPLANT, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 10. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY IRON CHELATION, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 11. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY LUSPATERCEPT, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 12. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 13. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY ALPHA THALASSEMIA, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 14. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY BETA THALASSEMIA, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 15. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 16. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY AMBULATORY SURGICAL CENTERS, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 17. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY HOSPITALS, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 18. GLOBAL THALASSEMIA TREATMENT MARKET SIZE, BY SPECIALTY CLINICS, BY REGION, 2018-2030 (USD MILLION)
  • TABLE 19. AMERICAS THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 20. AMERICAS THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 21. AMERICAS THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 22. AMERICAS THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 23. ARGENTINA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 24. ARGENTINA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 25. ARGENTINA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 26. BRAZIL THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 27. BRAZIL THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 28. BRAZIL THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 29. CANADA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 30. CANADA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 31. CANADA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 32. MEXICO THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 33. MEXICO THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 34. MEXICO THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 35. UNITED STATES THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 36. UNITED STATES THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 37. UNITED STATES THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 38. UNITED STATES THALASSEMIA TREATMENT MARKET SIZE, BY STATE, 2018-2030 (USD MILLION)
  • TABLE 39. ASIA-PACIFIC THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 40. ASIA-PACIFIC THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 41. ASIA-PACIFIC THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 42. ASIA-PACIFIC THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 43. AUSTRALIA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 44. AUSTRALIA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 45. AUSTRALIA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 46. CHINA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 47. CHINA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 48. CHINA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 49. INDIA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 50. INDIA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 51. INDIA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 52. INDONESIA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 53. INDONESIA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 54. INDONESIA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 55. JAPAN THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 56. JAPAN THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 57. JAPAN THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 58. MALAYSIA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 59. MALAYSIA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 60. MALAYSIA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 61. PHILIPPINES THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 62. PHILIPPINES THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 63. PHILIPPINES THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 64. SINGAPORE THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 65. SINGAPORE THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 66. SINGAPORE THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 67. SOUTH KOREA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 68. SOUTH KOREA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 69. SOUTH KOREA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 70. TAIWAN THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 71. TAIWAN THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 72. TAIWAN THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 73. THAILAND THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 74. THAILAND THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 75. THAILAND THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 76. VIETNAM THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 77. VIETNAM THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 78. VIETNAM THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 79. EUROPE, MIDDLE EAST & AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 80. EUROPE, MIDDLE EAST & AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 81. EUROPE, MIDDLE EAST & AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 82. EUROPE, MIDDLE EAST & AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
  • TABLE 83. DENMARK THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 84. DENMARK THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 85. DENMARK THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 86. EGYPT THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 87. EGYPT THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 88. EGYPT THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 89. FINLAND THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 90. FINLAND THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 91. FINLAND THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 92. FRANCE THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 93. FRANCE THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 94. FRANCE THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 95. GERMANY THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 96. GERMANY THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 97. GERMANY THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 98. ISRAEL THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 99. ISRAEL THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 100. ISRAEL THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 101. ITALY THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 102. ITALY THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 103. ITALY THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 104. NETHERLANDS THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 105. NETHERLANDS THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 106. NETHERLANDS THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 107. NIGERIA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 108. NIGERIA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 109. NIGERIA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 110. NORWAY THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 111. NORWAY THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 112. NORWAY THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 113. POLAND THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 114. POLAND THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 115. POLAND THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 116. QATAR THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 117. QATAR THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 118. QATAR THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 119. RUSSIA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 120. RUSSIA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 121. RUSSIA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 122. SAUDI ARABIA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 123. SAUDI ARABIA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 124. SAUDI ARABIA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 125. SOUTH AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 126. SOUTH AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 127. SOUTH AFRICA THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 128. SPAIN THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 129. SPAIN THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 130. SPAIN THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 131. SWEDEN THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 132. SWEDEN THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 133. SWEDEN THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 134. SWITZERLAND THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 135. SWITZERLAND THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 136. SWITZERLAND THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 137. TURKEY THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 138. TURKEY THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 139. TURKEY THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 140. UNITED ARAB EMIRATES THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 141. UNITED ARAB EMIRATES THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 142. UNITED ARAB EMIRATES THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 143. UNITED KINGDOM THALASSEMIA TREATMENT MARKET SIZE, BY TYPE, 2018-2030 (USD MILLION)
  • TABLE 144. UNITED KINGDOM THALASSEMIA TREATMENT MARKET SIZE, BY INDICATION TYPE, 2018-2030 (USD MILLION)
  • TABLE 145. UNITED KINGDOM THALASSEMIA TREATMENT MARKET SIZE, BY END-USERS, 2018-2030 (USD MILLION)
  • TABLE 146. THALASSEMIA TREATMENT MARKET SHARE, BY KEY PLAYER, 2023
  • TABLE 147. THALASSEMIA TREATMENT MARKET, FPNV POSITIONING MATRIX, 2023
目次
Product Code: MRR-C002B1C996FB

The Thalassemia Treatment Market was valued at USD 6.38 billion in 2023, expected to reach USD 7.06 billion in 2024, and is projected to grow at a CAGR of 12.31%, to USD 14.38 billion by 2030.

Thalassemia treatment encompasses medical strategies aimed at managing this inherited blood disorder characterized by faulty hemoglobin production, leading to anemia and other complications. The necessity of effective thalassemia treatments is driven by the need to improve patients' quality of life, reduce dependence on regular blood transfusions, and prevent complications like iron overload. Treatment applications include regular blood transfusions, iron chelation therapy, and emerging gene therapies, with end-use primarily among hospitals, specialty clinics, and homecare settings. Market insights reveal that advances in gene therapy and the increasing prevalence of thalassemia in regions such as Asia-Pacific are major growth factors. Furthermore, there is considerable potential in developing personalized treatment plans and integrating digital health technologies to manage patient data and adherence to treatment regimens. However, market growth is challenged by factors like the high cost of treatments, a lack of awareness in low-income countries, and the need for stringent regulatory approvals for new therapies. Key areas for innovation include developing cost-effective gene-editing technologies, crafting therapies that target a broader spectrum of thalassemia mutations, and leveraging AI for predictive analytics in treatment outcome assessments. Companies should focus on building strategic collaborations to enhance R&D efforts and accelerate clinical trials. Staying updated with the latest technological advancements and regulatory changes is crucial to capture emerging opportunities. Meanwhile, promoting educational programs and raising public awareness can aid in mitigating market limitations. The nature of the thalassemia treatment market is dynamic, with ongoing efforts to streamline therapies making it a fertile ground for innovations aimed at transformative patient care.

KEY MARKET STATISTICS
Base Year [2023] USD 6.38 billion
Estimated Year [2024] USD 7.06 billion
Forecast Year [2030] USD 14.38 billion
CAGR (%) 12.31%

Market Dynamics: Unveiling Key Market Insights in the Rapidly Evolving Thalassemia Treatment Market

The Thalassemia Treatment Market is undergoing transformative changes driven by a dynamic interplay of supply and demand factors. Understanding these evolving market dynamics prepares business organizations to make informed investment decisions, refine strategic decisions, and seize new opportunities. By gaining a comprehensive view of these trends, business organizations can mitigate various risks across political, geographic, technical, social, and economic domains while also gaining a clearer understanding of consumer behavior and its impact on manufacturing costs and purchasing trends.

  • Market Drivers
    • Rising incidences of thalassemia disorders among population
    • Awareness related to early diagnosis and treating thalassemia
    • Growing emphasis on genomic research
  • Market Restraints
    • High cost associated with thalassemia treatments
  • Market Opportunities
    • Rising number of approvals for novel thalassemia treatments
    • Increasing healthcare infrastructure spendings across economies
  • Market Challenges
    • Possible complications associated with thalassemia therapies

Porter's Five Forces: A Strategic Tool for Navigating the Thalassemia Treatment Market

Porter's five forces framework is a critical tool for understanding the competitive landscape of the Thalassemia Treatment Market. It offers business organizations with a clear methodology for evaluating their competitive positioning and exploring strategic opportunities. This framework helps businesses assess the power dynamics within the market and determine the profitability of new ventures. With these insights, business organizations can leverage their strengths, address weaknesses, and avoid potential challenges, ensuring a more resilient market positioning.

PESTLE Analysis: Navigating External Influences in the Thalassemia Treatment Market

External macro-environmental factors play a pivotal role in shaping the performance dynamics of the Thalassemia Treatment Market. Political, Economic, Social, Technological, Legal, and Environmental factors analysis provides the necessary information to navigate these influences. By examining PESTLE factors, businesses can better understand potential risks and opportunities. This analysis enables business organizations to anticipate changes in regulations, consumer preferences, and economic trends, ensuring they are prepared to make proactive, forward-thinking decisions.

Market Share Analysis: Understanding the Competitive Landscape in the Thalassemia Treatment Market

A detailed market share analysis in the Thalassemia Treatment Market provides a comprehensive assessment of vendors' performance. Companies can identify their competitive positioning by comparing key metrics, including revenue, customer base, and growth rates. This analysis highlights market concentration, fragmentation, and trends in consolidation, offering vendors the insights required to make strategic decisions that enhance their position in an increasingly competitive landscape.

FPNV Positioning Matrix: Evaluating Vendors' Performance in the Thalassemia Treatment Market

The Forefront, Pathfinder, Niche, Vital (FPNV) Positioning Matrix is a critical tool for evaluating vendors within the Thalassemia Treatment Market. This matrix enables business organizations to make well-informed decisions that align with their goals by assessing vendors based on their business strategy and product satisfaction. The four quadrants provide a clear and precise segmentation of vendors, helping users identify the right partners and solutions that best fit their strategic objectives.

Strategy Analysis & Recommendation: Charting a Path to Success in the Thalassemia Treatment Market

A strategic analysis of the Thalassemia Treatment Market is essential for businesses looking to strengthen their global market presence. By reviewing key resources, capabilities, and performance indicators, business organizations can identify growth opportunities and work toward improvement. This approach helps businesses navigate challenges in the competitive landscape and ensures they are well-positioned to capitalize on newer opportunities and drive long-term success.

Key Company Profiles

The report delves into recent significant developments in the Thalassemia Treatment Market, highlighting leading vendors and their innovative profiles. These include ApoPharma Inc., Bellicum Pharmaceuticals, Inc., bluebird bio, Inc., Bristol-Myers Squibb Company, CRISPR Therapeutics AG, Editas Medicine Inc., Errant Gene Therapeutics LLC, Gamida Cell Ltd., GL Pharma, Grifols International SA, Ionis Pharmaceuticals, Inc., La Jolla Pharmaceutical Company, Lonza Group AG, Macsen Laboratories, Merck & Co., Inc., Novartis AG, Novo Nordisk A/S, Pfizer, Inc., Pharmascience Inc., Rajasthan Antibiotics Ltd, Sangamo Therapeutics, Inc., Sanofi S.A., Taj Pharmaceuticals Limited, Teva Pharmaceutical Industries Ltd., and Vertex Pharmaceuticals Incorporated.

Market Segmentation & Coverage

This research report categorizes the Thalassemia Treatment Market to forecast the revenues and analyze trends in each of the following sub-markets:

  • Based on Type, market is studied across Blood Transfusion, Bone Marrow & Stem Cell Transplant, Iron Chelation, and Luspatercept.
  • Based on Indication Type, market is studied across Alpha Thalassemia and Beta Thalassemia.
  • Based on End-Users, market is studied across Ambulatory Surgical Centers, Hospitals, and Specialty Clinics.
  • Based on Region, market is studied across Americas, Asia-Pacific, and Europe, Middle East & Africa. The Americas is further studied across Argentina, Brazil, Canada, Mexico, and United States. The United States is further studied across California, Florida, Illinois, New York, Ohio, Pennsylvania, and Texas. The Asia-Pacific is further studied across Australia, China, India, Indonesia, Japan, Malaysia, Philippines, Singapore, South Korea, Taiwan, Thailand, and Vietnam. The Europe, Middle East & Africa is further studied across Denmark, Egypt, Finland, France, Germany, Israel, Italy, Netherlands, Nigeria, Norway, Poland, Qatar, Russia, Saudi Arabia, South Africa, Spain, Sweden, Switzerland, Turkey, United Arab Emirates, and United Kingdom.

The report offers a comprehensive analysis of the market, covering key focus areas:

1. Market Penetration: A detailed review of the current market environment, including extensive data from top industry players, evaluating their market reach and overall influence.

2. Market Development: Identifies growth opportunities in emerging markets and assesses expansion potential in established sectors, providing a strategic roadmap for future growth.

3. Market Diversification: Analyzes recent product launches, untapped geographic regions, major industry advancements, and strategic investments reshaping the market.

4. Competitive Assessment & Intelligence: Provides a thorough analysis of the competitive landscape, examining market share, business strategies, product portfolios, certifications, regulatory approvals, patent trends, and technological advancements of key players.

5. Product Development & Innovation: Highlights cutting-edge technologies, R&D activities, and product innovations expected to drive future market growth.

The report also answers critical questions to aid stakeholders in making informed decisions:

1. What is the current market size, and what is the forecasted growth?

2. Which products, segments, and regions offer the best investment opportunities?

3. What are the key technology trends and regulatory influences shaping the market?

4. How do leading vendors rank in terms of market share and competitive positioning?

5. What revenue sources and strategic opportunities drive vendors' market entry or exit strategies?

Table of Contents

1. Preface

  • 1.1. Objectives of the Study
  • 1.2. Market Segmentation & Coverage
  • 1.3. Years Considered for the Study
  • 1.4. Currency & Pricing
  • 1.5. Language
  • 1.6. Stakeholders

2. Research Methodology

  • 2.1. Define: Research Objective
  • 2.2. Determine: Research Design
  • 2.3. Prepare: Research Instrument
  • 2.4. Collect: Data Source
  • 2.5. Analyze: Data Interpretation
  • 2.6. Formulate: Data Verification
  • 2.7. Publish: Research Report
  • 2.8. Repeat: Report Update

3. Executive Summary

4. Market Overview

5. Market Insights

  • 5.1. Market Dynamics
    • 5.1.1. Drivers
      • 5.1.1.1. Rising incidences of thalassemia disorders among population
      • 5.1.1.2. Awareness related to early diagnosis and treating thalassemia
      • 5.1.1.3. Growing emphasis on genomic research
    • 5.1.2. Restraints
      • 5.1.2.1. High cost associated with thalassemia treatments
    • 5.1.3. Opportunities
      • 5.1.3.1. Rising number of approvals for novel thalassemia treatments
      • 5.1.3.2. Increasing healthcare infrastructure spendings across economies
    • 5.1.4. Challenges
      • 5.1.4.1. Possible complications associated with thalassemia therapies
  • 5.2. Market Segmentation Analysis
  • 5.3. Porter's Five Forces Analysis
    • 5.3.1. Threat of New Entrants
    • 5.3.2. Threat of Substitutes
    • 5.3.3. Bargaining Power of Customers
    • 5.3.4. Bargaining Power of Suppliers
    • 5.3.5. Industry Rivalry
  • 5.4. PESTLE Analysis
    • 5.4.1. Political
    • 5.4.2. Economic
    • 5.4.3. Social
    • 5.4.4. Technological
    • 5.4.5. Legal
    • 5.4.6. Environmental

6. Thalassemia Treatment Market, by Type

  • 6.1. Introduction
  • 6.2. Blood Transfusion
  • 6.3. Bone Marrow & Stem Cell Transplant
  • 6.4. Iron Chelation
  • 6.5. Luspatercept

7. Thalassemia Treatment Market, by Indication Type

  • 7.1. Introduction
  • 7.2. Alpha Thalassemia
  • 7.3. Beta Thalassemia

8. Thalassemia Treatment Market, by End-Users

  • 8.1. Introduction
  • 8.2. Ambulatory Surgical Centers
  • 8.3. Hospitals
  • 8.4. Specialty Clinics

9. Americas Thalassemia Treatment Market

  • 9.1. Introduction
  • 9.2. Argentina
  • 9.3. Brazil
  • 9.4. Canada
  • 9.5. Mexico
  • 9.6. United States

10. Asia-Pacific Thalassemia Treatment Market

  • 10.1. Introduction
  • 10.2. Australia
  • 10.3. China
  • 10.4. India
  • 10.5. Indonesia
  • 10.6. Japan
  • 10.7. Malaysia
  • 10.8. Philippines
  • 10.9. Singapore
  • 10.10. South Korea
  • 10.11. Taiwan
  • 10.12. Thailand
  • 10.13. Vietnam

11. Europe, Middle East & Africa Thalassemia Treatment Market

  • 11.1. Introduction
  • 11.2. Denmark
  • 11.3. Egypt
  • 11.4. Finland
  • 11.5. France
  • 11.6. Germany
  • 11.7. Israel
  • 11.8. Italy
  • 11.9. Netherlands
  • 11.10. Nigeria
  • 11.11. Norway
  • 11.12. Poland
  • 11.13. Qatar
  • 11.14. Russia
  • 11.15. Saudi Arabia
  • 11.16. South Africa
  • 11.17. Spain
  • 11.18. Sweden
  • 11.19. Switzerland
  • 11.20. Turkey
  • 11.21. United Arab Emirates
  • 11.22. United Kingdom

12. Competitive Landscape

  • 12.1. Market Share Analysis, 2023
  • 12.2. FPNV Positioning Matrix, 2023
  • 12.3. Competitive Scenario Analysis
  • 12.4. Strategy Analysis & Recommendation

Companies Mentioned

  • 1. ApoPharma Inc.
  • 2. Bellicum Pharmaceuticals, Inc.
  • 3. bluebird bio, Inc.
  • 4. Bristol-Myers Squibb Company
  • 5. CRISPR Therapeutics AG
  • 6. Editas Medicine Inc.
  • 7. Errant Gene Therapeutics LLC
  • 8. Gamida Cell Ltd.
  • 9. GL Pharma
  • 10. Grifols International SA
  • 11. Ionis Pharmaceuticals, Inc.
  • 12. La Jolla Pharmaceutical Company
  • 13. Lonza Group AG
  • 14. Macsen Laboratories
  • 15. Merck & Co., Inc.
  • 16. Novartis AG
  • 17. Novo Nordisk A/S
  • 18. Pfizer, Inc.
  • 19. Pharmascience Inc.
  • 20. Rajasthan Antibiotics Ltd
  • 21. Sangamo Therapeutics, Inc.
  • 22. Sanofi S.A.
  • 23. Taj Pharmaceuticals Limited
  • 24. Teva Pharmaceutical Industries Ltd.
  • 25. Vertex Pharmaceuticals Incorporated