サラセミア治療市場 - 世界の産業規模、シェア、動向、機会、予測、治療法別、タイプ別、エンドユーザー別、地域別、競合別、2020年～2030年

サラセミア治療の世界市場規模は、2024年に9億105万米ドルとなり、2030年までには14億1,920万米ドルに達し、予測期間中のCAGRは7.84%で成長すると予測されています。

同市場は、診断率の上昇、ヘルスケアアクセスの改善、希少遺伝性疾患の管理に対する官民の取り組みの拡大などを背景に変貌を遂げつつあります。患者やヘルスケアプロバイダーの意識の高まりは、早期スクリーニングとタイムリーな介入を促しています。輸血は依然として中心的な治療手段ですが、キレーション療法の進歩により、長期的な安全性と治療成績が向上しています。製薬会社は、輸血依存を減らしヘモグロビン産生を増加させるために、ルスパテルセプトやミタピバットのような治療薬を積極的に開発しています。同時に、新興市場では規制輸血サービスのインフラが強化されつつあり、包括的ケアモデルの広範な導入に貢献し、世界市場の成長に拍車をかけています。

主要な市場促進要因

世界のサラセミア有病率の上昇

主要な市場課題

先進治療へのアクセス制限

主要市場動向

遺伝子編集療法の出現

目次

第1章 製品概要

第2章 調査手法

第3章 エグゼクティブサマリー

第4章 顧客の声

第5章 世界のサラセミア治療市場展望

• 市場規模・予測
  • 金額別
• 市場シェア・予測
  • 治療法別（鉄キレート薬、輸血、甲状腺成熟化薬、幹細胞療法、その他）
  • タイプ別（アルファサラセミア、ベータサラセミア）
  • エンドユーザー別（病院、研究機関、その他）
  • 企業別（2024年）
  • 地域別
• 市場マップ

第6章 北米のサラセミア治療市場展望

• 市場規模・予測
• 市場シェア・予測
• 北米：国別分析
  • 米国
  • メキシコ
  • カナダ

第7章 欧州のサラセミア治療市場展望

• 市場規模・予測
• 市場シェア・予測
• 欧州：国別分析
  • フランス
  • ドイツ
  • 英国
  • イタリア
  • スペイン

第8章 アジア太平洋のサラセミア治療市場展望

• 市場規模・予測
• 市場シェア・予測
• アジア太平洋：国別分析
  • 中国
  • インド
  • 韓国
  • 日本
  • オーストラリア

第9章 南米のサラセミア治療市場展望

• 市場規模・予測
• 市場シェア・予測
• 南米：国別分析
  • ブラジル
  • アルゼンチン
  • コロンビア

第10章 中東・アフリカのサラセミア治療市場展望

• 市場規模・予測
• 市場シェア・予測
• 中東・アフリカ：国別分析
  • 南アフリカ
  • サウジアラビア
  • アラブ首長国連邦

第11章 市場力学

• 促進要因
• 課題

第12章 市場動向と発展

• 合併と買収
• 製品上市
• 最近の動向

第13章 ポーターのファイブフォース分析

• 業界内の競合
• 新規参入の可能性
• サプライヤーの力
• 顧客の力
• 代替品の脅威

第14章 競合情勢

• Bluebird Bio, Inc.
• Merck & Co., Inc.
• Novartis AG
• ApoPharma Inc.
• Pfizer, Inc.
• Celgene Corporation
• Takeda Pharmaceuticals Company Limited
• Incyte Corporation
• Bellicum Pharmaceuticals
• GSK plc

第15章 戦略的提言

第16章 調査会社について・免責事項

The Global Thalassemia Treatment Market was valued at USD 901.05 Million in 2024 and is projected to reach USD 1,419.20 Million by 2030, growing at a CAGR of 7.84% during the forecast period. The market is undergoing a transformation driven by increasing diagnosis rates, improved healthcare access, and expanding public and private efforts to manage rare genetic disorders. Enhanced awareness among patients and healthcare providers is encouraging early screening and timely intervention. While blood transfusions remain a core treatment modality, advancements in chelation therapies have improved long-term safety and outcomes. Pharmaceutical companies are actively developing therapies like luspatercept and mitapivat to reduce transfusion dependency and increase hemoglobin production. Simultaneously, emerging markets are enhancing infrastructure for regulated transfusion services, contributing to a broader adoption of comprehensive care models and fueling global market growth.

Key Market Drivers

Rising Global Prevalence of Thalassemia

The growing global prevalence of thalassemia is a major driver of market expansion. Thalassemia, a genetic blood disorder, is most prevalent in regions such as Southeast Asia, the Mediterranean, the Middle East, and North Africa. According to the World Health Organization (WHO), approximately 5% of the global population carries the thalassemia gene, contributing to increasing case numbers, especially in areas lacking genetic counseling or prenatal screening. As diagnosis rates improve, demand for lifelong care-including regular transfusions and iron chelation therapy-is rising. In parallel, innovative treatments such as stem cell transplantation and gene therapy are gaining attention as potential curative options. Governments and health organizations are investing in early detection programs, public health campaigns, and treatment facilities, all of which are fueling sustained market growth by ensuring better access to thalassemia care.

Key Market Challenges

Limited Access to Advanced Therapies

A significant challenge facing the thalassemia treatment market is the limited access to advanced therapies, particularly in low- and middle-income regions. While gene therapies and stem cell transplants offer promising long-term outcomes or potential cures, their availability is often restricted due to high costs, complex infrastructure requirements, and the need for specialized medical expertise. These therapies are financially inaccessible for many patients, with prices often reaching hundreds of thousands of dollars. Moreover, resource-poor regions lack the necessary facilities and personnel to support advanced treatments, leaving patients dependent on traditional methods like blood transfusions and iron chelation, which are less effective over the long term. This disparity in care contributes to uneven patient outcomes and underscores the need for global strategies to improve accessibility, affordability, and infrastructure for advanced thalassemia therapies.

Key Market Trends

Emergence of Gene Editing Therapies

Gene editing therapies, particularly CRISPR-Cas9, are emerging as transformative innovations in the treatment of thalassemia. These techniques allow precise modification of defective genes responsible for the disease, offering the potential for a one-time curative approach. Traditional therapies manage symptoms without addressing the genetic root cause, whereas gene editing targets and corrects the underlying mutation. In 2023, clinical trials showed positive outcomes using CRISPR-Cas9 to treat beta-thalassemia, significantly reducing or eliminating transfusion needs. Companies like CRISPR Therapeutics and Vertex Pharmaceuticals are advancing therapies such as CTX001, which modifies patient stem cells to promote functional hemoglobin production. These advancements mark a shift toward personalized, curative treatments that could redefine long-term disease management. As regulatory pathways for orphan drugs and genetic therapies evolve, these approaches are expected to play a larger role in the future of thalassemia care.

Key Market Players

• Bluebird Bio, Inc.
• Merck & Co., Inc.
• Novartis AG
• ApoPharma Inc.
• Pfizer, Inc.
• Celgene Corporation
• Takeda Pharmaceuticals Company Limited
• Incyte Corporation
• Bellicum Pharmaceuticals
• GSK plc

Report Scope

In this report, the Global Thalassemia Treatment Market has been segmented into the following categories, in addition to the industry trends which have also been detailed below:

Thalassemia Treatment Market, By Treatment:

• Iron Chelating Drugs
• Blood Transfusions
• Erythyroid Maturation Agents
• Stem Cell Therapy
• Others

Thalassemia Treatment Market, By Type:

• Alpha Thalassemia
• Beta Thalassemia

Thalassemia Treatment Market, By End User:

• Hospitals
• Research Institutes
• Others

Thalassemia Treatment Market, By Region:

• North America
  • United States
  • Canada
  • Mexico
• Europe
  • France
  • United Kingdom
  • Italy
  • Germany
  • Spain
• Asia-Pacific
  • China
  • India
  • Japan
  • Australia
  • South Korea
• South America
  • Brazil
  • Argentina
  • Colombia
• Middle East & Africa
  • South Africa
  • Saudi Arabia
  • UAE

Competitive Landscape

Company Profiles: Detailed analysis of the major companies present in the Global Thalassemia Treatment Market.

Available Customizations

Global Thalassemia Treatment Market report with the given market data, TechSci Research offers customizations according to a company's specific needs. The following customization options are available for the report:

Company Information

• Detailed analysis and profiling of additional market players (up to five).

Table of Contents

1. Product Overview

• 1.1. Market Definition
• 1.2. Scope of the Market
  • 1.2.1. Markets Covered
  • 1.2.2. Years Considered for Study
  • 1.2.3. Key Market Segmentations

2. Research Methodology

• 2.1. Objective of the Study
• 2.2. Baseline Methodology
• 2.3. Key Industry Partners
• 2.4. Major Association and Secondary Sources
• 2.5. Forecasting Methodology
• 2.6. Data Triangulation & Validation
• 2.7. Assumptions and Limitations

3. Executive Summary

• 3.1. Overview of the Market
• 3.2. Overview of Key Market Segmentations
• 3.3. Overview of Key Market Players
• 3.4. Overview of Key Regions/Countries
• 3.5. Overview of Market Drivers, Challenges, and Trends

4. Voice of Customer

5. Global Thalassemia Treatment Market Outlook

• 5.1. Market Size & Forecast
  • 5.1.1. By Value
• 5.2. Market Share & Forecast
  • 5.2.1. By Treatment (Iron Chelating Drugs, Blood Transfusions, Erythyroid Maturation Agents, Stem Cell Therapy, Others)
  • 5.2.2. By Type (Alpha Thalassemia, Beta Thalassemia)
  • 5.2.3. By End User (Hospitals, Research Institutes, Others)
  • 5.2.4. By Company (2024)
  • 5.2.5. By Region
• 5.3. Market Map

6. North America Thalassemia Treatment Market Outlook

• 6.1. Market Size & Forecast
  • 6.1.1. By Value
• 6.2. Market Share & Forecast
  • 6.2.1. By Treatment
  • 6.2.2. By Type
  • 6.2.3. By End User
  • 6.2.4. By Country
• 6.3. North America: Country Analysis
  • 6.3.1. United States Thalassemia Treatment Market Outlook
    • 6.3.1.1. Market Size & Forecast
      • 6.3.1.1.1. By Value
    • 6.3.1.2. Market Share & Forecast
      • 6.3.1.2.1. By Treatment
      • 6.3.1.2.2. By Type
      • 6.3.1.2.3. By End User
  • 6.3.2. Mexico Thalassemia Treatment Market Outlook
    • 6.3.2.1. Market Size & Forecast
      • 6.3.2.1.1. By Value
    • 6.3.2.2. Market Share & Forecast
      • 6.3.2.2.1. By Treatment
      • 6.3.2.2.2. By Type
      • 6.3.2.2.3. By End User
  • 6.3.3. Canada Thalassemia Treatment Market Outlook
    • 6.3.3.1. Market Size & Forecast
      • 6.3.3.1.1. By Value
    • 6.3.3.2. Market Share & Forecast
      • 6.3.3.2.1. By Treatment
      • 6.3.3.2.2. By Type
      • 6.3.3.2.3. By End User

7. Europe Thalassemia Treatment Market Outlook

• 7.1. Market Size & Forecast
  • 7.1.1. By Value
• 7.2. Market Share & Forecast
  • 7.2.1. By Treatment
  • 7.2.2. By Type
  • 7.2.3. By End User
  • 7.2.4. By Country
• 7.3. Europe: Country Analysis
  • 7.3.1. France Thalassemia Treatment Market Outlook
    • 7.3.1.1. Market Size & Forecast
      • 7.3.1.1.1. By Value
    • 7.3.1.2. Market Share & Forecast
      • 7.3.1.2.1. By Treatment
      • 7.3.1.2.2. By Type
      • 7.3.1.2.3. By End User
  • 7.3.2. Germany Thalassemia Treatment Market Outlook
    • 7.3.2.1. Market Size & Forecast
      • 7.3.2.1.1. By Value
    • 7.3.2.2. Market Share & Forecast
      • 7.3.2.2.1. By Treatment
      • 7.3.2.2.2. By Type
      • 7.3.2.2.3. By End User
  • 7.3.3. United Kingdom Thalassemia Treatment Market Outlook
    • 7.3.3.1. Market Size & Forecast
      • 7.3.3.1.1. By Value
    • 7.3.3.2. Market Share & Forecast
      • 7.3.3.2.1. By Treatment
      • 7.3.3.2.2. By Type
      • 7.3.3.2.3. By End User
  • 7.3.4. Italy Thalassemia Treatment Market Outlook
    • 7.3.4.1. Market Size & Forecast
      • 7.3.4.1.1. By Value
    • 7.3.4.2. Market Share & Forecast
      • 7.3.4.2.1. By Treatment
      • 7.3.4.2.2. By Type
      • 7.3.4.2.3. By End User
  • 7.3.5. Spain Thalassemia Treatment Market Outlook
    • 7.3.5.1. Market Size & Forecast
      • 7.3.5.1.1. By Value
    • 7.3.5.2. Market Share & Forecast
      • 7.3.5.2.1. By Treatment
      • 7.3.5.2.2. By Type
      • 7.3.5.2.3. By End User

8. Asia-Pacific Thalassemia Treatment Market Outlook

• 8.1. Market Size & Forecast
  • 8.1.1. By Value
• 8.2. Market Share & Forecast
  • 8.2.1. By Treatment
  • 8.2.2. By Type
  • 8.2.3. By End User
  • 8.2.4. By Country
• 8.3. Asia-Pacific: Country Analysis
  • 8.3.1. China Thalassemia Treatment Market Outlook
    • 8.3.1.1. Market Size & Forecast
      • 8.3.1.1.1. By Value
    • 8.3.1.2. Market Share & Forecast
      • 8.3.1.2.1. By Treatment
      • 8.3.1.2.2. By Type
      • 8.3.1.2.3. By End User
  • 8.3.2. India Thalassemia Treatment Market Outlook
    • 8.3.2.1. Market Size & Forecast
      • 8.3.2.1.1. By Value
    • 8.3.2.2. Market Share & Forecast
      • 8.3.2.2.1. By Treatment
      • 8.3.2.2.2. By Type
      • 8.3.2.2.3. By End User
  • 8.3.3. South Korea Thalassemia Treatment Market Outlook
    • 8.3.3.1. Market Size & Forecast
      • 8.3.3.1.1. By Value
    • 8.3.3.2. Market Share & Forecast
      • 8.3.3.2.1. By Treatment
      • 8.3.3.2.2. By Type
      • 8.3.3.2.3. By End User
  • 8.3.4. Japan Thalassemia Treatment Market Outlook
    • 8.3.4.1. Market Size & Forecast
      • 8.3.4.1.1. By Value
    • 8.3.4.2. Market Share & Forecast
      • 8.3.4.2.1. By Treatment
      • 8.3.4.2.2. By Type
      • 8.3.4.2.3. By End User
  • 8.3.5. Australia Thalassemia Treatment Market Outlook
    • 8.3.5.1. Market Size & Forecast
      • 8.3.5.1.1. By Value
    • 8.3.5.2. Market Share & Forecast
      • 8.3.5.2.1. By Treatment
      • 8.3.5.2.2. By Type
      • 8.3.5.2.3. By End User

9. South America Thalassemia Treatment Market Outlook

• 9.1. Market Size & Forecast
  • 9.1.1. By Value
• 9.2. Market Share & Forecast
  • 9.2.1. By Treatment
  • 9.2.2. By Type
  • 9.2.3. By End User
  • 9.2.4. By Country
• 9.3. South America: Country Analysis
  • 9.3.1. Brazil Thalassemia Treatment Market Outlook
    • 9.3.1.1. Market Size & Forecast
      • 9.3.1.1.1. By Value
    • 9.3.1.2. Market Share & Forecast
      • 9.3.1.2.1. By Treatment
      • 9.3.1.2.2. By Type
      • 9.3.1.2.3. By End User
  • 9.3.2. Argentina Thalassemia Treatment Market Outlook
    • 9.3.2.1. Market Size & Forecast
      • 9.3.2.1.1. By Value
    • 9.3.2.2. Market Share & Forecast
      • 9.3.2.2.1. By Treatment
      • 9.3.2.2.2. By Type
      • 9.3.2.2.3. By End User
  • 9.3.3. Colombia Thalassemia Treatment Market Outlook
    • 9.3.3.1. Market Size & Forecast
      • 9.3.3.1.1. By Value
    • 9.3.3.2. Market Share & Forecast
      • 9.3.3.2.1. By Treatment
      • 9.3.3.2.2. By Type
      • 9.3.3.2.3. By End User

10. Middle East and Africa Thalassemia Treatment Market Outlook

• 10.1. Market Size & Forecast
  • 10.1.1. By Value
• 10.2. Market Share & Forecast
  • 10.2.1. By Treatment
  • 10.2.2. By Type
  • 10.2.3. By End User
  • 10.2.4. By Country
• 10.3. MEA: Country Analysis
  • 10.3.1. South Africa Thalassemia Treatment Market Outlook
    • 10.3.1.1. Market Size & Forecast
      • 10.3.1.1.1. By Value
    • 10.3.1.2. Market Share & Forecast
      • 10.3.1.2.1. By Treatment
      • 10.3.1.2.2. By Type
      • 10.3.1.2.3. By End User
  • 10.3.2. Saudi Arabia Thalassemia Treatment Market Outlook
    • 10.3.2.1. Market Size & Forecast
      • 10.3.2.1.1. By Value
    • 10.3.2.2. Market Share & Forecast
      • 10.3.2.2.1. By Treatment
      • 10.3.2.2.2. By Type
      • 10.3.2.2.3. By End User
  • 10.3.3. UAE Thalassemia Treatment Market Outlook
    • 10.3.3.1. Market Size & Forecast
      • 10.3.3.1.1. By Value
    • 10.3.3.2. Market Share & Forecast
      • 10.3.3.2.1. By Treatment
      • 10.3.3.2.2. By Type
      • 10.3.3.2.3. By End User

11. Market Dynamics

• 11.1. Drivers
• 11.2. Challenges

12. Market Trends & Developments

• 12.1. Merger & Acquisition (If Any)
• 12.2. Product Launches (If Any)
• 12.3. Recent Developments

13. Porters Five Forces Analysis

• 13.1. Competition in the Industry
• 13.2. Potential of New Entrants
• 13.3. Power of Suppliers
• 13.4. Power of Customers
• 13.5. Threat of Substitute Products

14. Competitive Landscape

• 14.1. Bluebird Bio, Inc.
  • 14.1.1. Business Overview
  • 14.1.2. Company Snapshot
  • 14.1.3. Products & Services
  • 14.1.4. Financials (As Reported)
  • 14.1.5. Recent Developments
  • 14.1.6. Key Personnel Details
  • 14.1.7. SWOT Analysis
• 14.2. Merck & Co., Inc.
• 14.3. Novartis AG
• 14.4. ApoPharma Inc.
• 14.5. Pfizer, Inc.
• 14.6. Celgene Corporation
• 14.7. Takeda Pharmaceuticals Company Limited
• 14.8. Incyte Corporation
• 14.9. Bellicum Pharmaceuticals
• 14.10. GSK plc

15. Strategic Recommendations

16. About Us & Disclaimer