ファブリー病治療市場-世界の産業規模、シェア、動向、機会、予測、2018～2028年、薬剤別、治療法別、投与経路別、流通経路別、地域別、競合

世界のファブリー病治療市場は、2022年に18億6,250万米ドルと評価され、2028年までのCAGRは6.30%で、予測期間中に目覚ましい成長を遂げると予測されています。

ファブリー病は、アンダーソン・ファブリー病としても知られ、ライソゾーム貯蔵障害として知られる疾患群に属するまれな遺伝性疾患です。この疾患は、α-ガラクトシダーゼA（α-Gal A）と呼ばれる酵素をコードするGLA遺伝子の変異によって引き起こされます。この酵素が欠損すると、全身の細胞内にグロボトリアオシルセラミド（Gb3またはGL-3）として知られる特定の種類の脂肪物質が蓄積します。このGb3の蓄積は主に血管、腎臓、心臓、神経系の細胞に影響を及ぼし、様々な症状や合併症を引き起こします。ファブリー病の症状は多くの場合、小児期または青年期に現れるが、症状の発現年齢や重症度は罹患者によって大きく異なります。ファブリー病の特徴的な症状の一つは神経障害性疼痛であり、重篤で慢性化することがあります。この痛みは典型的には手や足などの四肢に起こり、しばしば灼熱感や疼きと表現されます。

ファブリー病に対する医療専門家、患者、介護者の意識の高まりは、診断率の向上につながっています。治療開始には早期診断が重要であるため、認知度の向上は市場の重要な促進要因となっています。診断ツールや遺伝子検査の進歩により、ファブリー病を初期段階でも容易に特定できるようになっています。診断能力の向上により、より多くの症例が診断・治療されるようになっています。世界の医療支出は増加しており、ファブリー病のような希少疾患治療への投資も拡大しています。医療予算の増加は研究開発の努力を支え、治療法への患者のアクセスを改善しました。製薬会社はファブリー病の新規治療法を開発するために研究開発に投資しています。これには遺伝子治療、シャペロン治療、その他の革新的な治療法が含まれ、市場を拡大しています。バイオテクノロジーとドラッグデリバリー方法の進歩により、ファブリー病治療の安全性と有効性が向上し、患者や医療提供者にとってより魅力的なものとなっています。

主要市場促進要因

診断の進歩

目次

第1章 概要

第2章 調査手法

第3章 エグゼクティブサマリー

第4章 顧客の声

第5章 ファブリー病治療の世界市場展望

• 市場規模・予測
  • 金額別
• 市場シェアと予測
  • 薬剤別（アガルシダーゼβ、ミガラスタット、その他）
  • 治療法別（酵素補充療法（ERT）、シャペロン療法、基質低減療法（SRT）、その他）
  • 投与経路別（経口、非経口、その他）
  • 流通チャネル別（病院薬局、小売薬局、オンライン薬局）
  • 地域別
  • 企業別（2022年）
• 市場マップ

第6章 アジア太平洋のファブリー病治療市場展望

• 市場規模・予測
  • 金額別
• 市場シェアと予測
  • 薬剤別
  • 治療法別
  • 投与経路別
  • 流通チャネル別
  • 国別
• アジア太平洋：国別分析
  • 中国
  • インド
  • オーストラリア
  • 日本
  • 韓国

第7章 欧州のファブリー病治療市場展望

• 市場規模・予測
  • 金額別
• 市場シェアと予測
  • 薬剤別
  • 治療法別
  • 投与経路別
  • 流通チャネル別
  • 国別
• 欧州：国別分析
  • フランス
  • ドイツ
  • スペイン
  • イタリア
  • 英国

第8章 北米のファブリー病治療市場展望

• 市場規模・予測
  • 金額別
• 市場シェアと予測
  • 薬剤別
  • 治療法別
  • 投与経路別
  • 流通チャネル別
  • 国別
• 北米：国別分析
  • 米国
  • メキシコ
  • カナダ

第9章 南米のファブリー病治療市場展望

• 市場規模・予測
  • 金額別
• 市場シェアと予測
  • 薬剤別
  • 治療法別
  • 投与経路別
  • 流通チャネル別
  • 国別
• 南米：国別分析
  • ブラジル
  • アルゼンチン
  • コロンビア

第10章 中東・アフリカのファブリー病治療市場展望

• 市場規模・予測
  • 金額別
• 市場シェアと予測
  • 薬剤別
  • 治療法別
  • 投与経路別
  • 流通チャネル別
  • 国別
• 中東・アフリカ：国別分析
  • 南アフリカ
  • サウジアラビア
  • アラブ首長国連邦

第11章 市場力学

• 促進要因
• 課題

第12章 市場動向と発展

• 製品上市
• 合併と買収

第13章 ファブリー病治療の世界市場のSWOT分析

第14章 ポーターのファイブフォース分析

• 業界内の競合
• 新規参入の可能性
• サプライヤーの力
• 顧客の力
• 代替品の脅威

第15章 PESTLE分析

第16章 競合情勢

• Sanofi（Genzyme Corporation）
• Takeda Pharmaceutical Company Limited
• Amicus Therapeutics, Inc
• JCR Pharmaceuticals Co., Ltd.
• Protalix BioTherapeutics Inc.
• Chiesi Farmaceutici S.p.A.
• Freeline Therapeutics Holdings PLC
• Yuhan Corporation
• M6P Therapeutics
• ISU Abxis Co Ltd

第17章 戦略的提言

第18章 調査会社・免責事項

Global Fabry Disease Treatment Market has valued at USD 1862.50 million in 2022 and is anticipated to witness an impressive growth in the forecast period with a CAGR of 6.30% through 2028. Fabry disease, also known as Anderson-Fabry disease, is a rare and inherited genetic disorder that belongs to a group of conditions known as lysosomal storage disorders. This disease is caused by mutations in the GLA gene, which encodes an enzyme called alpha-galactosidase A (alpha-Gal A). The deficiency of this enzyme results in the accumulation of a specific type of fatty substance, known as globotriaosylceramide (Gb3 or GL-3), within cells throughout the body. This buildup of Gb3 primarily affects the cells of blood vessels, kidneys, heart, and nervous system, leading to a wide range of symptoms and complications. Symptoms of Fabry disease often appear in childhood or adolescence, although the age of symptom onset and their severity can vary widely among affected individuals. One of the hallmark symptoms of Fabry disease is neuropathic pain, which can be severe and chronic. This pain typically affects the extremities, such as the hands and feet, and is often described as burning or tingling.

Growing awareness among healthcare professionals, patients, and caregivers about Fabry disease has led to improved diagnosis rates. Increased awareness is a significant driver for the market, as early diagnosis is critical for initiating treatment. Advances in diagnostic tools and genetic testing have made it easier to identify Fabry disease, even in its early stages. Improved diagnostic capabilities have led to more cases being diagnosed and treated. Global healthcare expenditure has been increasing, allowing for greater investment in rare disease treatments like Fabry disease. Increased healthcare budgets have supported research and development efforts and improved patient access to treatments. Pharmaceutical companies have been investing in research and development to develop novel therapies for Fabry disease. This includes gene therapy, chaperone therapy, and other innovative treatment options, expanding the market. Advances in biotechnology and drug delivery methods have improved the safety and efficacy of Fabry disease treatments, making them more attractive to patients and healthcare providers.

Key Market Drivers

Advancements in Diagnosis

Genetic testing has become a cornerstone in the diagnosis of Fabry disease. Advances in genetic sequencing technology have made it more accessible and cost-effective to identify specific mutations in the GLA gene, which is responsible for the disease. Genetic testing can confirm the presence of Fabry disease and provide information about the specific genetic mutations involved. In some regions, newborn screening programs have been implemented to identify Fabry disease in infants shortly after birth. This early detection allows for prompt intervention and treatment, potentially preventing or delaying the onset of symptoms and organ damage. Researchers have been investigating biomarkers associated with Fabry disease. Biomarkers are measurable substances in the body that can indicate the presence of a disease or its progression. Biomarker research can aid in early diagnosis and monitoring the effectiveness of treatment. Clinical diagnostic criteria for Fabry disease have been refined and standardized. Healthcare professionals now have clearer guidelines and criteria to assist in diagnosing disease based on clinical symptoms and genetic testing results.

Advanced imaging techniques, such as magnetic resonance imaging (MRI) and echocardiography, can help visualize organ damage caused by Fabry disease. These non-invasive methods allow for the assessment of heart, kidney, and other organ involvement. Enzyme activity assays, which measure the activity of alpha-galactosidase A, the deficient enzyme in Fabry disease, have become more precise and widely available. These assays can confirm the enzyme deficiency in individuals suspected of having the disease. Telemedicine and telehealth technologies have expanded access to Fabry disease specialists, allowing patients to receive consultations and diagnostic evaluations remotely. This is especially important for individuals in underserved or remote areas. Collaboration among healthcare professionals, researchers, and patient advocacy groups on a global scale has facilitated the sharing of diagnostic knowledge and best practices, leading to more accurate and consistent diagnosis. Healthcare providers are increasingly educated about Fabry disease, leading to better recognition and diagnosis of the condition. Continuing medical education programs and resources have contributed to this improvement. Fabry disease patients and their families have become more informed and proactive in seeking a diagnosis. Online resources and patient advocacy groups have empowered individuals to advocate for their healthcare needs. This factor will help in the development of the Global Fabry Disease Treatment Market.

Rising Pharmaceutical Innovation

Pharmaceutical companies invest in research and development to create novel and more effective treatments for Fabry disease. These innovations can lead to therapies that are better at managing the disease, reducing symptoms, and improving the quality of life for patients. Pharmaceutical innovation leads to a broader range of treatment options for Fabry disease. This diversification of therapies allows healthcare providers and patients to choose the most appropriate treatment based on individual needs, preferences, and disease characteristics. Advancements in pharmaceutical research enable the development of targeted therapies. These treatments are designed to address the specific molecular and genetic mechanisms underlying Fabry disease. Targeted therapies can be more effective and have fewer side effects than traditional treatments. Pharmaceutical innovation supports the concept of personalized medicine, where treatments are tailored to an individual's genetic profile and disease characteristics. This approach can lead to more precise and effective treatments, optimizing patient outcomes. Innovations in drug delivery technology can enhance the convenience and effectiveness of Fabry disease treatments. For example, advancements in enzyme replacement therapy (ERT) delivery methods can make it easier for patients to receive treatment. Pharmaceutical research can lead to the development of therapies that require less frequent administration. This can improve patient adherence to treatment regimens and reduce the burden of frequent hospital visits.

Many pharmaceutical companies pursue orphan drug designations for Fabry disease treatments. These designations provide incentives and regulatory support for the development of treatments for rare diseases, increasing investment in this area. Pharmaceutical companies conduct clinical trials to test the safety and efficacy of new Fabry disease treatments. These trials provide valuable data on the benefits and risks of innovative therapies and help bring them to market. Competition among pharmaceutical companies can drive innovation by encouraging the development of new and improved Fabry disease treatments. This competition can lead to better treatment options and potentially lower costs for patients. As pharmaceutical companies expand their presence in global markets, access to Fabry disease treatments improves for patients in different regions, increasing demand for these therapies. Patient advocacy groups and organizations often collaborate with pharmaceutical companies in research and development efforts. This collaboration can accelerate the development and availability of innovative treatments. This factor will pace up the demand of the Global Fabry Disease Treatment Market.

Increasing Disease Awareness

Disease awareness campaigns educate healthcare providers and the public about Fabry disease, its symptoms, and risk factors. This knowledge can lead to earlier diagnosis, enabling patients to access treatment before the disease progresses to more severe stages. Improved awareness can help reduce delays in diagnosis. Fabry disease is often underdiagnosed or misdiagnosed because its symptoms can mimic other conditions. Increased awareness among healthcare professionals can lead to more accurate and timely diagnoses. When people become more aware of Fabry disease, they may seek medical advice and testing if they exhibit symptoms or have a family history of the disease. This can result in more individuals being tested for Fabry disease, potentially leading to earlier identification and treatment. Awareness campaigns are often driven by patient advocacy groups and organizations. These groups work to raise awareness about Fabry disease, support affected individuals, and advocate for better access to treatment and resources. Disease awareness initiatives often include educational programs for healthcare providers. These programs help physicians recognize the signs and symptoms of Fabry disease and consider it as a potential diagnosis when evaluating patients.

Disease awareness efforts provide patients and their families with accurate information about Fabry disease, available treatments, and support services. Informed patients are more likely to seek appropriate care and treatment options. Raising awareness can reduce the stigma associated with rare diseases like Fabry disease. This can encourage individuals to discuss their symptoms openly with healthcare providers and seek help without fear of judgment. Increased awareness can lead to greater interest from pharmaceutical companies and researchers in developing new and improved Fabry disease treatments. As the demand for treatments grows, so does the incentive for innovation in the field. Public awareness campaigns can garner support from policymakers and government agencies. This support can lead to increased funding for research, improved healthcare policies, and better access to treatment. Disease awareness is not limited by geographical boundaries. Global collaboration among healthcare organizations, advocacy groups, and researchers can further drive awareness and foster international efforts to combat Fabry disease. This factor will accelerate the demand of the Global Fabry Disease Treatment Market.

Key Market Challenges

Limited Patient Population

The small patient population with Fabry disease results in a limited market size for pharmaceutical companies. This can make it less economically attractive for these companies to invest in research and development of treatments for disease. Developing and gaining regulatory approval for new treatments, including clinical trials and research, is costly. In the case of rare diseases like Fabry disease, the small number of potential patients can make it challenging to recoup these expenses. Due to the small market size, the revenue potential for treatments for Fabry disease may be limited compared to drugs for more common conditions. This can affect the profitability of drug development efforts. Limited patient populations can result in challenges related to patient access to treatments and affordability. Even if effective treatments exist, they may not be accessible to all patients due to cost or availability. The rarity of Fabry disease can lead to delayed diagnosis or misdiagnosis, as healthcare providers may not be familiar with the condition. This can result in patients not receiving appropriate treatment until the disease has progressed. Limited patient populations can also result in a scarcity of clinical data on the disease and its treatment. This can make it challenging for healthcare providers to make informed treatment decisions. Recognizing the challenges posed by rare diseases, some regulatory agencies provide incentives for orphan drug development. These incentives can include extended market exclusivity and reduced regulatory fees.

Supply Chain Vulnerabilities

The primary treatment for Fabry disease involves enzyme replacement therapy, which can be costly. ERT drugs are typically administered intravenously every two weeks, and the cost of these treatments can accumulate significantly over time. Fabry disease is a chronic condition that requires lifelong treatment. The long-term nature of treatment can result in a substantial financial burden on patients and healthcare systems. Access to ERT and other Fabry disease treatments may be limited in some regions. Even when treatments are available, not all patients may have adequate insurance coverage to offset the costs, leading to disparities in access to care. Patients with Fabry disease often require ongoing medical care, including monitoring for complications in various organs (e.g., heart, kidneys) and managing associated symptoms. These additional healthcare expenses can further contribute to the overall cost of treatment. From a pharmaceutical industry perspective, developing and bringing Fabry disease treatments to market can be expensive due to the need for extensive research, clinical trials, and regulatory approvals. These costs can influence the pricing of therapies. Fabry disease is a rare condition, and the limited patient population can result in higher treatment costs per patient. Pharmaceutical companies may need to recover development costs from a smaller pool of patients, which can lead to higher drug prices. Many Fabry disease treatments receive orphan drug designation, which provides certain incentives to pharmaceutical companies but can also result in higher drug prices.

Key Market Trends

Biomarker Development

Biomarkers can aid in the early diagnosis of Fabry disease, allowing for timely intervention and treatment initiation. Early diagnosis is essential for preventing or delaying the onset of symptoms and organ damage. Biomarkers can be used to monitor disease progression and assess the effectiveness of treatment over time. This enables healthcare providers to tailor treatment plans to individual patients' needs. Certain biomarkers may be associated with the severity of Fabry disease. Identifying these biomarkers can help predict disease outcomes and guide treatment decisions. Biomarkers can help determine how well a patient is responding to treatment. If treatment is effective, biomarkers may show improvements in disease-related indicators. Biomarkers can serve as valuable endpoints in clinical trials of new Fabry disease treatments. They provide objective measures of treatment efficacy and safety. The development of biomarkers supports the concept of personalized medicine, where treatments are tailored to individual patients based on their biomarker profiles. This approach can optimize treatment outcomes. Biomarkers provide insights into the underlying molecular and genetic mechanisms of Fabry disease. This knowledge can inform drug development efforts, leading to more targeted and effective therapies. Biomarkers can be used to stratify Fabry disease patients into different subgroups based on disease characteristics. This stratification can guide treatment decisions and improve patient outcomes. Biomarkers can help reduce diagnostic delays by providing objective evidence of Fabry disease. This is particularly important because Fabry disease is often underdiagnosed or misdiagnosed.

Segmental Insights

Drugs Insights

In 2022, the Global Fabry Disease Treatment Market largest share was held by Agalsidase Beta segment and is predicted to continue expanding over the coming years. Agalsidase Beta has been available for Fabry disease treatment for an extended period. Its long history in the market has contributed to its recognition and use among healthcare providers. Clinical studies have demonstrated the efficacy of Agalsidase Beta in reducing symptoms and slowing the progression of Fabry disease. It works by replacing the deficient enzyme alpha-galactosidase A in patients with the condition. Many Fabry disease patients have received treatment with Agalsidase Beta and have reported positive outcomes, such as a reduction in pain, improved kidney function, and enhanced overall quality of life. Healthcare professionals, including specialists in Fabry disease, are familiar with Agalsidase Beta and its administration. Their experience with this therapy contributes to its continued use.

Treatment Insights

In 2022, the Global Fabry Disease Treatment Market largest share was held by Enzyme Replacement Therapy (ERT) segment and is predicted to continue expanding over the coming years. Enzyme Replacement Therapy (ERT) was one of the earliest and most established treatment options for Fabry disease. It has been used for many years to manage the symptoms and complications of the disease. ERT has demonstrated efficacy in stabilizing and improving the health of individuals with Fabry disease by replacing the deficient enzyme (alpha-galactosidase A). Clinical studies have shown that ERT can reduce pain, improve kidney function, and slow the progression of organ damage. Many Fabry disease patients have had positive experiences with ERT in terms of symptom relief and improved quality of life. This has contributed to its continued use and market dominance. Healthcare providers, particularly specialists in Fabry disease, have extensive experience with ERT. They are familiar with its administration and monitoring, making it a preferred choice for treatment.

Route of Administration Insights

In 2022, the Global Fabry Disease Treatment Market largest share was held by Oral segment and is predicted to continue expanding over the coming years. Oral medications are generally more convenient for patients compared to other routes of administration, such as intravenous (IV) infusions. Fabry disease patients may prefer oral treatments, as they can take these medications at home without the need for frequent hospital visits. Oral medications can enhance patient adherence to treatment regimens. Patients are more likely to consistently take oral medications as prescribed, which is crucial for managing a chronic condition like Fabry disease effectively. Advancements in drug development have led to the creation of oral medications that are effective in managing Fabry disease. These medications can stabilize and improve patients' health by addressing the underlying enzyme deficiency.

Distribution Channel Insights

In 2022, the Global Fabry Disease Treatment Market largest share was held by Hospital Pharmacies segment in the forecast period and is predicted to continue expanding over the coming years. Fabry disease is a rare genetic disorder that requires specialized medications, such as enzyme replacement therapy (ERT), for treatment. These medications are typically administered under the supervision of healthcare professionals in hospital settings. Hospital pharmacies are well-equipped to handle the storage, preparation, and administration of these specialized drugs. Patients with Fabry disease often require close monitoring of their treatment and health status. Hospitals have the resources and expertise to provide comprehensive patient care and monitor treatment efficacy, including managing potential side effects or complications. Fabry disease patients are typically under the care of specialized physicians, such as geneticists or metabolic disease specialists, who work closely with hospital-based healthcare teams. Hospital pharmacies are integrated into the healthcare system, facilitating collaboration among healthcare professionals to ensure optimal patient care.

Regional Insights

The North America region dominates the Global Fabry Disease Treatment Market in 2022. North America, particularly the United States and Canada, has a well-developed and advanced healthcare infrastructure. This infrastructure includes a network of hospitals, clinics, and research institutions with access to cutting-edge medical technology and expertise. North America has a relatively high level of awareness about rare diseases, including Fabry disease. Healthcare providers in the region are more likely to recognize and diagnose rare diseases, which can lead to earlier treatment and better outcomes. North America is a hub for clinical research and pharmaceutical development. Many clinical trials for Fabry disease treatments are conducted in the region, attracting global pharmaceutical companies and researchers. The United States has a well-established regulatory framework for drug approvals through the Food and Drug Administration (FDA). This facilitates the development and approval of Fabry disease treatments, making them available to patients more quickly.

Key Market Players

Sanofi (Genzyme Corporation)

Takeda Pharmaceutical Company Limited

Amicus Therapeutics, Inc

ISU ABXIS Co Ltd.

JCR Pharmaceuticals Co., Ltd.

Protalix BioTherapeutics Inc.

Chiesi Farmaceutici S.p.A.

Freeline Therapeutics Holdings PLC

Yuhan Corporation

M6P Therapeutics

Report Scope:

In this report, the Global Fabry Disease Treatment Market has been segmented into the following categories, in addition to the industry trends which have also been detailed below:

Fabry Disease Treatment Market, By Drugs:

• Agalsidase Beta
• Migalastat
• others

Fabry Disease Treatment Market, By Treatment:

• Enzyme Replacement Therapy (ERT)
• Chaperone Treatment
• Substrate Reduction Therapy (SRT)
• Others

Fabry Disease Treatment Market, By Route of Administration:

• Oral
• Parenteral
• Others

Fabry Disease Treatment Market, By Distribution Channel:

• Hospital pharmacies
• Retail pharmacies
• Online Pharmacies

Global Fabry Disease Treatment Market, By region:

• North America
• United States
• Canada
• Mexico
• Asia-Pacific
• China
• India
• South Korea
• Australia
• Japan
• Europe
• Germany
• France
• United Kingdom
• Spain
• Italy
• South America
• Brazil
• Argentina
• Colombia
• Middle East & Africa
• South Africa
• Saudi Arabia
• UAE

Competitive Landscape

• Company Profiles: Detailed analysis of the major companies present in the Global Fabry Disease Treatment Market.

Available Customizations:

• Global Fabry Disease Treatment Market report with the given market data, Tech Sci Research offers customizations according to a company's specific needs. The following customization options are available for the report:

Company Information

• Detailed analysis and profiling of additional market players (up to five).

Table of Contents

1. Product Overview

• 1.1. Market Definition
• 1.2. Scope of the Market
  • 1.2.1. Markets Covered
  • 1.2.2. Years Considered for Study
  • 1.2.3. Key Market Segmentations

2. Research Methodology

• 2.1. Objective of the Study
• 2.2. Baseline Methodology
• 2.3. Key Industry Partners
• 2.4. Major Association and Secondary Sources
• 2.5. Forecasting Methodology
• 2.6. Data Triangulation & Validation
• 2.7. Assumptions and Limitations

3. Executive Summary

• 3.1. Overview of the Market
• 3.2. Overview of Key Market Segmentations
• 3.3. Overview of Key Market Players
• 3.4. Overview of Key Regions/Countries
• 3.5. Overview of Market Drivers, Challenges, Trends

4. Voice of Customer

5. Global Fabry Disease Treatment Market Outlook

• 5.1. Market Size & Forecast
  • 5.1.1. By Value
• 5.2. Market Share & Forecast
  • 5.2.1. By Drugs (Agalsidase Beta, Migalastat, others)
  • 5.2.2. By Treatment (Enzyme Replacement Therapy (ERT), Chaperone Treatment, Substrate Reduction Therapy (SRT), others)
  • 5.2.3. By Route of Administration (Oral, Parenteral, others)
  • 5.2.4. By Distribution Channel (Hospital pharmacies, Retail pharmacies, Online Pharmacies)
  • 5.2.5. By Region
  • 5.2.6. By Company (2022)
• 5.3. Market Map

6. Asia Pacific Fabry Disease Treatment Market Outlook

• 6.1. Market Size & Forecast
  • 6.1.1. By Value
• 6.2. Market Share & Forecast
  • 6.2.1. By Drugs
  • 6.2.2. By Treatment
  • 6.2.3. By Route of Administration
  • 6.2.4. By Distribution Channel
  • 6.2.5. By Country
• 6.3. Asia Pacific: Country Analysis
  • 6.3.1. China Fabry Disease Treatment Market Outlook
    • 6.3.1.1. Market Size & Forecast
      • 6.3.1.1.1. By Value
    • 6.3.1.2. Market Share & Forecast
      • 6.3.1.2.1. By Drugs
      • 6.3.1.2.2. By Treatment
      • 6.3.1.2.3. By Route of Administration
      • 6.3.1.2.4. By Distribution Channel
  • 6.3.2. India Fabry Disease Treatment Market Outlook
    • 6.3.2.1. Market Size & Forecast
      • 6.3.2.1.1. By Value
    • 6.3.2.2. Market Share & Forecast
      • 6.3.2.2.1. By Drugs
      • 6.3.2.2.2. By Treatment
      • 6.3.2.2.3. By Route of Administration
      • 6.3.2.2.4. By Distribution Channel
  • 6.3.3. Australia Fabry Disease Treatment Market Outlook
    • 6.3.3.1. Market Size & Forecast
      • 6.3.3.1.1. By Value
    • 6.3.3.2. Market Share & Forecast
      • 6.3.3.2.1. By Drugs
      • 6.3.3.2.2. By Treatment
      • 6.3.3.2.3. By Route of Administration
      • 6.3.3.2.4. By Distribution Channel
  • 6.3.4. Japan Fabry Disease Treatment Market Outlook
    • 6.3.4.1. Market Size & Forecast
      • 6.3.4.1.1. By Value
    • 6.3.4.2. Market Share & Forecast
      • 6.3.4.2.1. By Drugs
      • 6.3.4.2.2. By Treatment
      • 6.3.4.2.3. By Route of Administration
      • 6.3.4.2.4. By Distribution Channel
  • 6.3.5. South Korea Fabry Disease Treatment Market Outlook
    • 6.3.5.1. Market Size & Forecast
      • 6.3.5.1.1. By Value
    • 6.3.5.2. Market Share & Forecast
      • 6.3.5.2.1. By Drugs
      • 6.3.5.2.2. By Treatment
      • 6.3.5.2.3. By Route of Administration
      • 6.3.5.2.4. By Distribution Channel

7. Europe Fabry Disease Treatment Market Outlook

• 7.1. Market Size & Forecast
  • 7.1.1. By Value
• 7.2. Market Share & Forecast
  • 7.2.1. By Drugs
  • 7.2.2. By Treatment
  • 7.2.3. By Route of Administration
  • 7.2.4. By Distribution Channel
  • 7.2.5. By Country
• 7.3. Europe: Country Analysis
  • 7.3.1. France Fabry Disease Treatment Market Outlook
    • 7.3.1.1. Market Size & Forecast
      • 7.3.1.1.1. By Value
    • 7.3.1.2. Market Share & Forecast
      • 7.3.1.2.1. By Drugs
      • 7.3.1.2.2. By Treatment
      • 7.3.1.2.3. By Route of Administration
      • 7.3.1.2.4. By Distribution Channel
  • 7.3.2. Germany Fabry Disease Treatment Market Outlook
    • 7.3.2.1. Market Size & Forecast
      • 7.3.2.1.1. By Value
    • 7.3.2.2. Market Share & Forecast
      • 7.3.2.2.1. By Drugs
      • 7.3.2.2.2. By Treatment
      • 7.3.2.2.3. By Route of Administration
      • 7.3.2.2.4. By Distribution Channel
  • 7.3.3. Spain Fabry Disease Treatment Market Outlook
    • 7.3.3.1. Market Size & Forecast
      • 7.3.3.1.1. By Value
    • 7.3.3.2. Market Share & Forecast
      • 7.3.3.2.1. By Drugs
      • 7.3.3.2.2. By Treatment
      • 7.3.3.2.3. By Route of Administration
      • 7.3.3.2.4. By Distribution Channel
  • 7.3.4. Italy Fabry Disease Treatment Market Outlook
    • 7.3.4.1. Market Size & Forecast
      • 7.3.4.1.1. By Value
    • 7.3.4.2. Market Share & Forecast
      • 7.3.4.2.1. By Drugs
      • 7.3.4.2.2. By Treatment
      • 7.3.4.2.3. By Route of Administration
      • 7.3.4.2.4. By Distribution Channel
  • 7.3.5. United Kingdom Fabry Disease Treatment Market Outlook
    • 7.3.5.1. Market Size & Forecast
      • 7.3.5.1.1. By Value
    • 7.3.5.2. Market Share & Forecast
      • 7.3.5.2.1. By Drugs
      • 7.3.5.2.2. By Treatment
      • 7.3.5.2.3. By Route of Administration
      • 7.3.5.2.4. By Distribution Channel

8. North America Fabry Disease Treatment Market Outlook

• 8.1. Market Size & Forecast
  • 8.1.1. By Value
• 8.2. Market Share & Forecast
  • 8.2.1. By Drugs
  • 8.2.2. By Treatment
  • 8.2.3. By Route of Administration
  • 8.2.4. By Distribution Channel
  • 8.2.5. By Country
• 8.3. North America: Country Analysis
  • 8.3.1. United States Fabry Disease Treatment Market Outlook
    • 8.3.1.1. Market Size & Forecast
      • 8.3.1.1.1. By Value
    • 8.3.1.2. Market Share & Forecast
      • 8.3.1.2.1. By Drugs
      • 8.3.1.2.2. By Treatment
      • 8.3.1.2.3. By Route of Administration
      • 8.3.1.2.4. By Distribution Channel
  • 8.3.2. Mexico Fabry Disease Treatment Market Outlook
    • 8.3.2.1. Market Size & Forecast
      • 8.3.2.1.1. By Value
    • 8.3.2.2. Market Share & Forecast
      • 8.3.2.2.1. By Drugs
      • 8.3.2.2.2. By Treatment
      • 8.3.2.2.3. By Route of Administration
      • 8.3.2.2.4. By Distribution Channel
  • 8.3.3. Canada Fabry Disease Treatment Market Outlook
    • 8.3.3.1. Market Size & Forecast
      • 8.3.3.1.1. By Value
    • 8.3.3.2. Market Share & Forecast
      • 8.3.3.2.1. By Drugs
      • 8.3.3.2.2. By Treatment
      • 8.3.3.2.3. By Route of Administration
      • 8.3.3.2.4. By Distribution Channel

9. South America Fabry Disease Treatment Market Outlook

• 9.1. Market Size & Forecast
  • 9.1.1. By Value
• 9.2. Market Share & Forecast
  • 9.2.1. By Drugs
  • 9.2.2. By Treatment
  • 9.2.3. By Route of Administration
  • 9.2.4. By Distribution Channel
  • 9.2.5. By Country
• 9.3. South America: Country Analysis
  • 9.3.1. Brazil Fabry Disease Treatment Market Outlook
    • 9.3.1.1. Market Size & Forecast
      • 9.3.1.1.1. By Value
    • 9.3.1.2. Market Share & Forecast
      • 9.3.1.2.1. By Drugs
      • 9.3.1.2.2. By Treatment
      • 9.3.1.2.3. By Route of Administration
      • 9.3.1.2.4. By Distribution Channel
  • 9.3.2. Argentina Fabry Disease Treatment Market Outlook
    • 9.3.2.1. Market Size & Forecast
      • 9.3.2.1.1. By Value
    • 9.3.2.2. Market Share & Forecast
      • 9.3.2.2.1. By Drugs
      • 9.3.2.2.2. By Treatment
      • 9.3.2.2.3. By Route of Administration
      • 9.3.2.2.4. By Distribution Channel
  • 9.3.3. Colombia Fabry Disease Treatment Market Outlook
    • 9.3.3.1. Market Size & Forecast
      • 9.3.3.1.1. By Value
    • 9.3.3.2. Market Share & Forecast
      • 9.3.3.2.1. By Drugs
      • 9.3.3.2.2. By Treatment
      • 9.3.3.2.3. By Route of Administration
      • 9.3.3.2.4. By Distribution Channel

10. Middle East and Africa Fabry Disease Treatment Market Outlook

• 10.1. Market Size & Forecast
  • 10.1.1. By Value
• 10.2. Market Share & Forecast
  • 10.2.1. By Drugs
  • 10.2.2. By Treatment
  • 10.2.3. By Route of Administration
  • 10.2.4. By Distribution Channel
  • 10.2.5. By Country
• 10.3. MEA: Country Analysis
  • 10.3.1. South Africa Fabry Disease Treatment Market Outlook
    • 10.3.1.1. Market Size & Forecast
      • 10.3.1.1.1. By Value
    • 10.3.1.2. Market Share & Forecast
      • 10.3.1.2.1. By Drugs
      • 10.3.1.2.2. By Treatment
      • 10.3.1.2.3. By Route of Administration
      • 10.3.1.2.4. By Distribution Channel
  • 10.3.2. Saudi Arabia Fabry Disease Treatment Market Outlook
    • 10.3.2.1. Market Size & Forecast
      • 10.3.2.1.1. By Value
    • 10.3.2.2. Market Share & Forecast
      • 10.3.2.2.1. By Drugs
      • 10.3.2.2.2. By Treatment
      • 10.3.2.2.3. By Route of Administration
      • 10.3.2.2.4. By Distribution Channel
  • 10.3.3. UAE Fabry Disease Treatment Market Outlook
    • 10.3.3.1. Market Size & Forecast
      • 10.3.3.1.1. By Value
    • 10.3.3.2. Market Share & Forecast
      • 10.3.3.2.1. By Drugs
      • 10.3.3.2.2. By Treatment
      • 10.3.3.2.3. By Route of Administration
      • 10.3.3.2.4. By Distribution Channel

11. Market Dynamics

• 11.1. Drivers
• 11.2. Challenges

12. Market Trends & Developments

• 12.1. Recent Developments
• 12.2. Product Launches
• 12.3. Mergers & Acquisitions

13. Global Fabry Disease Treatment Market: SWOT Analysis

14. Porter's Five Forces Analysis

• 14.1. Competition in the Industry
• 14.2. Potential of New Entrants
• 14.3. Power of Suppliers
• 14.4. Power of Customers
• 14.5. Threat of Substitute Product

15. PESTLE Analysis

16. Competitive Landscape

• 16.1. Sanofi (Genzyme Corporation)
  • 16.1.1. Business Overview
  • 16.1.2. Company Snapshot
  • 16.1.3. Products & Services
  • 16.1.4. Financials (In case of listed companies)
  • 16.1.5. Recent Developments
  • 16.1.6. SWOT Analysis
• 16.2. Takeda Pharmaceutical Company Limited
  • 16.2.1. Business Overview
  • 16.2.2. Company Snapshot
  • 16.2.3. Products & Services
  • 16.2.4. Financials (In case of listed companies)
  • 16.2.5. Recent Developments
  • 16.2.6. SWOT Analysis
• 16.3. Amicus Therapeutics, Inc
  • 16.3.1. Business Overview
  • 16.3.2. Company Snapshot
  • 16.3.3. Products & Services
  • 16.3.4. Financials (In case of listed companies)
  • 16.3.5. Recent Developments
  • 16.3.6. SWOT Analysis
• 16.4. JCR Pharmaceuticals Co., Ltd.
  • 16.4.1. Business Overview
  • 16.4.2. Company Snapshot
  • 16.4.3. Products & Services
  • 16.4.4. Financials (In case of listed companies)
  • 16.4.5. Recent Developments
  • 16.4.6. SWOT Analysis
• 16.5. Protalix BioTherapeutics Inc.
  • 16.5.1. Business Overview
  • 16.5.2. Company Snapshot
  • 16.5.3. Products & Services
  • 16.5.4. Financials (In case of listed companies)
  • 16.5.5. Recent Developments
  • 16.5.6. SWOT Analysis
• 16.6. Chiesi Farmaceutici S.p.A.
  • 16.6.1. Business Overview
  • 16.6.2. Company Snapshot
  • 16.6.3. Products & Services
  • 16.6.4. Financials (In case of listed companies)
  • 16.6.5. Recent Developments
  • 16.6.6. SWOT Analysis
• 16.7. Freeline Therapeutics Holdings PLC
  • 16.7.1. Business Overview
  • 16.7.2. Company Snapshot
  • 16.7.3. Products & Services
  • 16.7.4. Financials (In case of listed companies)
  • 16.7.5. Recent Developments
  • 16.7.6. SWOT Analysis
• 16.8. Yuhan Corporation
  • 16.8.1. Business Overview
  • 16.8.2. Company Snapshot
  • 16.8.3. Products & Services
  • 16.8.4. Financials (In case of listed companies)
  • 16.8.5. Recent Developments
  • 16.8.6. SWOT Analysis
• 16.9. M6P Therapeutics
  • 16.9.1. Business Overview
  • 16.9.2. Company Snapshot
  • 16.9.3. Products & Services
  • 16.9.4. Financials (In case of listed companies)
  • 16.9.5. Recent Developments
  • 16.9.6. SWOT Analysis
• 16.10. ISU Abxis Co Ltd
  • 16.10.1. Business Overview
  • 16.10.2. Company Snapshot
  • 16.10.3. Products & Services
  • 16.10.4. Financials (In case of listed companies)
  • 16.10.5. Recent Developments
  • 16.10.6. SWOT Analysis

17. Strategic Recommendations

18. About Us & Disclaimer