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表紙：ポンペ病の世界市場：投与経路別、最終用途別、治療タイプ別、国別、地域別 - 産業分析、市場規模、市場シェア、2023年～2030年予測
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ポンペ病の世界市場：投与経路別、最終用途別、治療タイプ別、国別、地域別 - 産業分析、市場規模、市場シェア、2023年～2030年予測

Pompe Disease Market, By Route of Administration, By End-Use, By Treatment Type, By Country, and By Region - Industry Analysis, Market Size, Market Share & Forecast from 2023-2030

出版日
ページ情報
英文 290 Pages
納期
2～3営業日
カスタマイズ可能
価格
価格表記: USDを日本円(税抜)に換算
本日の銀行送金レート: 1USD=143.57円
ポンペ病の世界市場：投与経路別、最終用途別、治療タイプ別、国別、地域別 - 産業分析、市場規模、市場シェア、2023年～2030年予測
出版日: 2023年08月01日
発行: AnalystView Market Insights
ページ情報: 英文 290 Pages
納期: 2～3営業日
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  • 概要
  • 図表
  • 目次
概要

世界のポンペ病の市場規模は、2022年は13億2,223万米ドルとなり、2023年から2030年にかけてCAGR 4.2％で拡大すると予想されています。

ポンペ病市場 - 市場力学

  • 製薬企業、研究機関、患者支援団体間の協力関係の拡大が市場の需要を促進
  • ポンペ病の研究と治療の進歩は、製薬会社、学術機関、ポンペ病患者支援団体間の協力関係の拡大によって大きく促進されます。この共同研究の相乗効果により、知識、専門知識、リソースの交換が促進され、革新的な治療法の発見が促進されます。規制機関は、希少疾病研究に投資する企業のインセンティブを高めるため、奨励金や希少疾病用医薬品の指定を提供しています。さらに、患者支援団体は、一般の人々の認識を高め、研究や臨床試験のための資金を生み出す募金活動を組織することで、極めて重要な役割を果たしています。このような努力の積み重ねにより、ポンペ病の根本的な原因に対する理解が深まり、個別化された治療法の開発への道が開かれ、最終的にはポンペ病に罹患した人々の予後と生活の質が改善されるのです。

ポンペ病市場 - セグメンテーション分析

  • 世界のポンペ病市場は、投与経路、最終用途、治療タイプ、地域など、さまざまな要因に基づいてセグメンテーションを提示します。
  • 投与経路別のカテゴリーでは、非経口投与が市場をリードしています。これは、まれな遺伝性疾患であるポンペ病を管理する上で、非経口的治療が好まれていることを示しています。静脈注射による酵素補充療法（ERT）は、疾患管理において極めて重要な役割を果たしています。この療法は、欠乏した酵素を直接投与し、細胞内のグリコーゲン蓄積に効果的に対処することで、罹患者の筋機能を改善します。

ポンペ病市場 - 競合情勢

ポンペ病の研究・治療市場は、製薬会社、研究機関、支援団体のダイナミックな相互作用によって特徴付けられています。学術団体との協力関係は科学的進歩を促進し、患者支援団体は認知度の向上、研究活動への資金提供、規制当局の支援の提唱において極めて重要な役割を果たしています。希少疾病用医薬品の指定は、この分野での競争力をさらに高める。この競合環境において、企業は治療の有効性、アクセスのしやすさ、患者支援イニシアチブの実施を強調することで、他社との差別化を図ろうと努力しています。このような競争は、進歩を加速させる触媒として機能し、より幅広い治療選択肢と、ポンペ病患者に提供されるケアの質の全体的な向上につながります。

目次

第1章 ポンペ病市場概要

  • 調査範囲
  • 市場推定年数

第2章 エグゼクティブサマリー

  • 市場内訳
  • 競合考察

第3章 ポンペ病の主要な市場動向

  • 市場促進要因
  • 市場抑制要因
  • 市場機会
  • 今後の市場動向

第4章 ポンペ病産業の調査

  • PEST分析
  • ポーターのファイブフォース分析
  • 成長見通しのマッピング
  • 規制枠組みの分析

第5章 ポンペ病市場：COVID-19の影響分析

  • 新型コロナウイルス感染症以前の影響分析
  • 新型コロナウイルス感染症後の影響分析

第6章 ポンペ病市場情勢

  • ポンペ病市場シェア分析、2022年
  • 主要メーカー別の内訳データ
    • 既存企業の分析
    • 新興企業の分析

第7章 ポンペ病市場 - 投与経路別

  • 概要
    • 投与経路別セグメントシェア分析
    • 経口
    • 非経口

第8章 ポンペ病市場 - 治療タイプ別

  • 概要
    • 治療タイプ別のセグメントシェア分析
    • 基質除去療法（SRT）
    • 酵素補充療法（ERT）
    • その他

第9章 ポンペ病市場 - エンドユーザー別

  • 概要
    • エンドユーザー別のセグメントシェア分析
    • 病院
    • 外来手術センター
    • その他

第10章 ポンペ病市場 - 地域別

  • イントロダクション
  • 北米
    • 概要
    • 北米の主要メーカー
    • 米国
    • カナダ
  • 欧州
    • 概要
    • 欧州の主要メーカー
    • ドイツ
    • イタリア
    • 英国
    • フランス
    • ロシア
    • オランダ
    • スウェーデン
    • ポーランド
    • その他
  • アジア太平洋
    • 概要
    • アジア太平洋の主要メーカー
    • インド
    • 中国
    • 日本
    • 韓国
    • オーストラリア
    • タイ
    • インドネシア
    • フィリピン
    • その他
  • ラテンアメリカ
    • 概要
    • ラテンアメリカの主要メーカー
    • ブラジル
    • メキシコ
    • アルゼンチン
    • コロンビア
    • その他
  • 中東・アフリカ
    • 概要
    • 中東・アフリカの主要メーカー
    • サウジアラビア
    • アラブ首長国連邦
    • イスラエル
    • トルコ
    • アルジェリア
    • エジプト
    • その他

第11章 主要ベンダー分析 - ポンペ病産業

  • 競合ダッシュボード
  • 企業プロファイル
    • Sanofi Genzyme
    • Amicus Therapeutics
    • BioMarin Pharmaceutical
    • Ultragenyx Pharmaceutical
    • Audentes Therapeutics
    • Avrobio
    • Regenxbio
    • EpiVax
    • Selecta Biosciences
    • Cytokinetics
    • Adverum Biotechnologies
    • Audentes Therapeutics
    • JCR Pharmaceuticals
    • Audentes Therapeutics
    • Valerion Therapeutics

第12章 アナリストの全方位展望

図表

List of Tables

  • TABLE List of data sources
  • TABLE Market drivers; Impact Analysis
  • TABLE Market restraints; Impact Analysis
  • TABLE Pompe Disease Market: Route of Administration Snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by Route of Administration
  • TABLE Global Pompe Disease Market, by Route of Administration 2018-2030 (USD Million)
  • TABLE Pompe Disease Market: Treatment Type Snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by Treatment Type
  • TABLE Global Pompe Disease Market, by Treatment Type 2018-2030 (USD Million)
  • TABLE Pompe Disease Market: End-User Snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by End-User
  • TABLE Global Pompe Disease Market, by End-User 2018-2030 (USD Million)
  • TABLE Pompe Disease Market: Regional snapshot (2022)
  • TABLE Segment Dashboard; Definition and Scope, by Region
  • TABLE Global Pompe Disease Market, by Region 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE North America Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Europe Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Asia Pacific Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Latin America Pompe Disease Market, by End-User, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by Country, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by Route of Administration, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by Treatment Type, 2018-2030 (USD Million)
  • TABLE Middle East and Africa Pompe Disease Market, by End-User, 2018-2030 (USD Million)
目次
Product Code: ANV1642

REPORT HIGHLIGHT

Pompe Disease Market size was valued at USD 1,322.23 Million in 2022, expanding at a CAGR of 4.2% from 2023 to 2030.

Pompe disease, a rare genetic disorder, arises from a deficiency of the enzyme acid alpha-glucosidase (GAA). This deficiency leads to the accumulation of glycogen within cells, with the most pronounced impact on muscle tissues, resulting in a gradual loss of function. Symptoms commonly associated with this condition encompass muscle weakness, respiratory challenges, and cardiac complications. The disease's severity varies, with some individuals experiencing early-onset forms that can have life-threatening cardiac and muscular consequences, while others may have a later onset characterized primarily by muscle weakening. Pompe disease underscores the crucial importance of early detection and ongoing medical management to mitigate its impact on an individual's overall quality of life.

Pompe Disease Market - Market Dynamics:

  • Growing collaboration between pharmaceutical companies, research institutions, and patient advocacy groups to propel market demand
  • The advancement of research and treatment for Pompe disease is significantly propelled by the increasing collaboration among pharmaceutical companies, academic institutions, and advocacy organizations dedicated to patients with this condition. This collaborative synergy facilitates the exchange of knowledge, expertise, and resources, thereby expediting the discovery of innovative therapies. Regulatory bodies provide incentives and orphan drug designations to incentivize companies to invest in rare disease research. Additionally, patient advocacy groups play a pivotal role by raising public awareness and organizing fundraising initiatives that generate funds for research and clinical trials. This collective endeavor enhances our understanding of the disease's underlying causes and paves the way for the development of personalized treatments, ultimately improving the prognosis and quality of life for individuals affected by Pompe disease.

Pompe Disease Market - Key Insights:

  • Our research analyst estimates that the global Pompe Disease market is poised for annual growth at a CAGR of approximately 4.2% during the forecast period from 2023 to 2030. This projected growth is attributed to the increasing collaboration among pharmaceutical firms, research institutions, and patient advocacy groups, indicating a positive trend toward advancing Pompe Disease research and treatment.
  • The Global Pompe Disease Market is categorized based on various factors, including Route of Administration, End-Use, and Region.
  • Within the Route of Administration category, Parenteral administration stood out as the dominant segment in the year 2022. This indicates a significant preference for this mode of administration in treating Pompe Disease.
  • In terms of End-Use segmentation, Hospitals took the lead in 2022. This suggests that hospitals play a crucial role in providing medical care and treatment for Pompe Disease patients.
  • Moreover, North America emerged as the primary revenue generator in 2022 among different regions.

Pompe Disease Market- Segmentation Analysis:

  • The Global Pompe Disease Market presents segmentation based on various factors, including Route of Administration, End-Use, Treatment Type, and Region.
  • Among the categories determined by Route of Administration, the Parenteral sector takes the lead in market dominance. This indicates a prevalent preference for parenteral treatments in managing Pompe disease, a rare genetic disorder. The administration of enzyme replacement therapy (ERT) through intravenous injections plays a pivotal role in disease management. This therapy directly delivers the deficient enzyme, effectively addressing glycogen accumulation within cells, and thereby improving muscle function in affected individuals.

Pompe Disease Market- Competitive Landscape:

The landscape of Pompe disease research and treatment is characterized by a dynamic interplay among pharmaceutical companies, research institutions, and advocacy groups. Collaborative efforts with academic organizations foster scientific advancements, while patient advocacy groups play a pivotal role in raising awareness, funding research endeavors, and advocating for regulatory support. The orphan drug designation further incentivizes competitiveness within the field. In this competitive environment, companies strive to set themselves apart by emphasizing treatment efficacy, accessibility, and the implementation of patient support initiatives. This competition acts as a catalyst for accelerated progress, leading to a broader range of therapeutic options and an overall enhancement in the quality of care provided to individuals with Pompe disease.

Recent Developments:

In June 2023, Amicus Therapeutics, a globally oriented biotechnology firm with a patient-centered approach, specializing in the development and commercialization of innovative medications for rare diseases, announced a significant milestone. The European Commission (EC) granted approval for Opfolda (miglustat) 65mg capsules, an enzyme stabilizer for cipaglucosidase alfa, as a long-term enzyme replacement therapy for adults afflicted with late-onset Pompe disease.

SCOPE OF THE REPORT

The scope of this report covers the market by its major segments, which include as follows:

GLOBAL POMPE DISEASE MARKET KEY PLAYERS

  • Sanofi Genzyme
  • Amicus Therapeutics
  • BioMarin Pharmaceutical
  • Ultragenyx Pharmaceutical
  • Audentes Therapeutics
  • Avrobio
  • Regenxbio
  • EpiVax
  • Selecta Biosciences
  • Cytokinetics
  • Adverum Biotechnologies
  • Audentes Therapeutics
  • JCR Pharmaceuticals
  • Audentes Therapeutics
  • Valerion Therapeutics

GLOBAL POMPE DISEASE MARKET, BY ROUTE OF ADMINISTRATION

  • Oral
  • Parenteral

GLOBAL POMPE DISEASE MARKET, BY END-USE

  • Hospitals
  • Ambulatory Surgical Centers
  • Other

GLOBAL POMPE DISEASE MARKET, BY TREATMENT TYPE

  • Substrate Reduction Therapy (SRT)
  • Enzyme Replacement Therapy (ERT)
  • Other

GLOBAL POMPE DISEASE MARKET, BY REGION

  • North America
    • The U.S.
    • Canada
  • Europe
    • Germany
    • France
    • Italy
    • Spain
    • United Kingdom
    • Russia
    • Netherlands
    • Sweden
    • Poland
    • Rest of Europe
  • Asia Pacific
    • India
    • China
    • South Korea
    • Japan
    • Australia
    • Thailand
    • Indonesia
    • Philippines
    • Rest of APAC
  • Latin America
    • Brazil
    • Mexico
    • Argentina
    • Colombia
    • Rest of LATAM
  • The Middle East and Africa
    • Saudi Arabia
    • United Arab Emirates
    • Israel
    • Turkey
    • Algeria
    • Egypt
    • Rest of MEA

Table of Contents

1. Pompe Disease Market Overview

  • 1.1. Study Scope
  • 1.2. Market Estimation Years

2. Executive Summary

  • 2.1. Market Snippet
    • 2.1.1. Pompe Disease Market Snippet by Route of Administration
    • 2.1.2. Pompe Disease Market Snippet by Treatment Type
    • 2.1.3. Pompe Disease Market Snippet by End-User
    • 2.1.4. Pompe Disease Market Snippet by Country
    • 2.1.5. Pompe Disease Market Snippet by Region
  • 2.2. Competitive Insights

3. Pompe Disease Key Market Trends

  • 3.1. Pompe Disease Market Drivers
    • 3.1.1. Impact Analysis of Market Drivers
  • 3.2. Pompe Disease Market Restraints
    • 3.2.1. Impact Analysis of Market Restraints
  • 3.3. Pompe Disease Market Opportunities
  • 3.4. Pompe Disease Market Future Trends

4. Pompe Disease Industry Study

  • 4.1. PEST Analysis
  • 4.2. Porter's Five Forces Analysis
  • 4.3. Growth Prospect Mapping
  • 4.4. Regulatory Framework Analysis

5. Pompe Disease Market: COVID-19 Impact Analysis

  • 5.1. Pre-COVID-19 Impact Analysis
  • 5.2. Post-COVID-19 Impact Analysis
    • 5.2.1. Top Performing Segments
    • 5.2.2. Marginal Growth Segments
    • 5.2.3. Top Looser Segments
    • 5.2.4. Marginal Loss Segments

6. Pompe Disease Market Landscape

  • 6.1. Pompe Disease Market Share Analysis, 2022
  • 6.2. Breakdown Data, by Key Manufacturer
    • 6.2.1. Established Players' Analysis
    • 6.2.2. Emerging Players' Analysis

7. Pompe Disease Market - By Route of Administration

  • 7.1. Overview
    • 7.1.1. Segment Share Analysis, By Route of Administration, 2022 & 2030 (%)
    • 7.1.2. Oral
    • 7.1.3. Parenteral

8. Pompe Disease Market - By Treatment Type

  • 8.1. Overview
    • 8.1.1. Segment Share Analysis, By Treatment Type, 2022 & 2030 (%)
    • 8.1.2. Substrate Reduction Therapy (SRT)
    • 8.1.3. Enzyme Replacement Therapy (ERT)
    • 8.1.4. Other

9. Pompe Disease Market - By End-User

  • 9.1. Overview
    • 9.1.1. Segment Share Analysis, By End-User, 2022 & 2030 (%)
    • 9.1.2. Hospitals
    • 9.1.3. Ambulatory Surgical Centers
    • 9.1.4. Other

10. Pompe Disease Market- By Geography

  • 10.1. Introduction
    • 10.1.1. Segment Share Analysis, By Geography, 2022 & 2030 (%)
  • 10.2. North America
    • 10.2.1. Overview
    • 10.2.2. Pompe Disease Key Manufacturers in North America
    • 10.2.3. North America Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.2.4. North America Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.2.5. North America Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.2.6. North America Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.2.7. U.S.
      • 10.2.7.1. Overview
      • 10.2.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.2.7.3. U.S. Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.2.7.4. U.S. Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.2.7.5. U.S. Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.2.8. Canada
      • 10.2.8.1. Overview
      • 10.2.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.2.8.3. Canada Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.2.8.4. Canada Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.2.8.5. Canada Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.3. Europe
    • 10.3.1. Overview
    • 10.3.2. Pompe Disease Key Manufacturers in Europe
    • 10.3.3. Europe Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.3.4. Europe Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.3.5. Europe Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.3.6. Europe Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.7. Germany
      • 10.3.7.1. Overview
      • 10.3.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.7.3. Germany Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.7.4. Germany Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.7.5. Germany Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.8. Italy
      • 10.3.8.1. Overview
      • 10.3.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.8.3. Italy Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.8.4. Italy Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.8.5. Italy Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.9. United Kingdom
      • 10.3.9.1. Overview
      • 10.3.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.9.3. United Kingdom Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.9.4. United Kingdom Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.9.5. United Kingdom Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.10. France
      • 10.3.10.1. Overview
      • 10.3.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.10.3. France Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.10.4. France Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.10.5. France Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.11. Russia
      • 10.3.11.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.11.2. Russia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.11.3. Russia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.11.4. Russia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.12. Netherlands
      • 10.3.12.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.12.2. Netherlands Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.12.3. Netherlands Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.12.4. Netherlands Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.13. Sweden
      • 10.3.13.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.13.2. Sweden Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.13.3. Sweden Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.13.4. Sweden Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.14. Poland
      • 10.3.14.1. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.14.2. Poland Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.14.3. Poland Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.14.4. Poland Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.3.15. Rest of Europe
      • 10.3.15.1. Overview
      • 10.3.15.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.3.15.3. Rest of the Europe Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.3.15.4. Rest of the Europe Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.3.15.5. Rest of the Europe Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.4. Asia Pacific (APAC)
    • 10.4.1. Overview
    • 10.4.2. Pompe Disease Key Manufacturers in Asia Pacific
    • 10.4.3. Asia Pacific Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.4.4. Asia Pacific Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.4.5. Asia Pacific Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.4.6. Asia Pacific Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.7. India
      • 10.4.7.1. Overview
      • 10.4.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.7.3. India Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.7.4. India Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.7.5. India Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.8. China
      • 10.4.8.1. Overview
      • 10.4.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.8.3. China Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.8.4. China Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.8.5. China Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.9. Japan
      • 10.4.9.1. Overview
      • 10.4.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.9.3. Japan Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.9.4. Japan Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.9.5. Japan Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.10. South Korea
      • 10.4.10.1. Overview
      • 10.4.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.10.3. South Korea Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.10.4. South Korea Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.10.5. South Korea Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.11. Australia
      • 10.4.11.1. Overview
      • 10.4.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.11.3. Australia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.11.4. Australia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.11.5. Australia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.12. Thailand
      • 10.4.12.1. Overview
      • 10.4.12.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.12.3. Thailand Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.12.4. Thailand Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.12.5. Thailand Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.13. Indonesia
      • 10.4.13.1. Overview
      • 10.4.13.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.13.3. Indonesia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.13.4. Indonesia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.13.5. Indonesia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.14. Philippines
      • 10.4.14.1. Overview
      • 10.4.14.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.14.3. Philippines Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.14.4. Philippines Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.14.5. Philippines Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.4.15. Rest of APAC
      • 10.4.15.1. Overview
      • 10.4.15.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.4.15.3. Rest of APAC Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.4.15.4. Rest of APAC Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.4.15.5. Rest of APAC Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.5. Latin America
    • 10.5.1. Overview
    • 10.5.2. Pompe Disease Key Manufacturers in Latin America
    • 10.5.3. Latin America Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.5.4. Latin America Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.5.5. Latin America Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.5.6. Latin America Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.7. Brazil
      • 10.5.7.1. Overview
      • 10.5.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.7.3. Brazil Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.7.4. Brazil Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.7.5. Brazil Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.8. Mexico
      • 10.5.8.1. Overview
      • 10.5.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.8.3. Mexico Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.8.4. Mexico Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.8.5. Mexico Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.9. Argentina
      • 10.5.9.1. Overview
      • 10.5.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.9.3. Argentina Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.9.4. Argentina Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.9.5. Argentina Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.10. Colombia
      • 10.5.10.1. Overview
      • 10.5.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.10.3. Colombia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.10.4. Colombia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.10.5. Colombia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.5.11. Rest of LATAM
      • 10.5.11.1. Overview
      • 10.5.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.5.11.3. Rest of LATAM Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.5.11.4. Rest of LATAM Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.5.11.5. Rest of LATAM Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
  • 10.6. Middle East and Africa
    • 10.6.1. Overview
    • 10.6.2. Pompe Disease Key Manufacturers in Middle East and Africa
    • 10.6.3. Middle East and Africa Market Size and Forecast, By Country, 2018 - 2030 (US$ Million)
    • 10.6.4. Middle East and Africa Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
    • 10.6.5. Middle East and Africa Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
    • 10.6.6. Middle East and Africa Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.7. Saudi Arabia
      • 10.6.7.1. Overview
      • 10.6.7.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.7.3. Saudi Arabia Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.7.4. Saudi Arabia Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.7.5. Saudi Arabia Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.8. United Arab Emirates
      • 10.6.8.1. Overview
      • 10.6.8.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.8.3. United Arab Emirates Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.8.4. United Arab Emirates Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.8.5. United Arab Emirates Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.9. Israel
      • 10.6.9.1. Overview
      • 10.6.9.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.9.3. Israel Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.9.4. Israel Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.9.5. Israel Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.10. Turkey
      • 10.6.10.1. Overview
      • 10.6.10.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.10.3. Turkey Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.10.4. Turkey Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.10.5. Turkey Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.11. Algeria
      • 10.6.11.1. Overview
      • 10.6.11.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.11.3. Algeria Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.11.4. Algeria Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.11.5. Algeria Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.12. Egypt
      • 10.6.12.1. Overview
      • 10.6.12.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.12.3. Egypt Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.12.4. Egypt Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.12.5. Egypt Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)
    • 10.6.13. Rest of MEA
      • 10.6.13.1. Overview
      • 10.6.13.2. Market Analysis, Forecast, and Y-O-Y Growth Rate, 2018 - 2030, (US$ Million)
      • 10.6.13.3. Rest of MEA Market Size and Forecast, By Route of Administration, 2018 - 2030 (US$ Million)
      • 10.6.13.4. Rest of MEA Market Size and Forecast, By Treatment Type, 2018 - 2030 (US$ Million)
      • 10.6.13.5. Rest of MEA Market Size and Forecast, By End-User, 2018 - 2030 (US$ Million)

11. Key Vendor Analysis- Pompe Disease Industry

  • 11.1. Competitive Dashboard
  • 11.2. Company Profiles
    • 11.2.1. Sanofi Genzyme
    • 11.2.2. Amicus Therapeutics
    • 11.2.3. BioMarin Pharmaceutical
    • 11.2.4. Ultragenyx Pharmaceutical
    • 11.2.5. Audentes Therapeutics
    • 11.2.6. Avrobio
    • 11.2.7. Regenxbio
    • 11.2.8. EpiVax
    • 11.2.9. Selecta Biosciences
    • 11.2.10. Cytokinetics
    • 11.2.11. Adverum Biotechnologies
    • 11.2.12. Audentes Therapeutics
    • 11.2.13. JCR Pharmaceuticals
    • 11.2.14. Audentes Therapeutics
    • 11.2.15. Valerion Therapeutics

12. 360 Degree Analyst View

13. Appendix

  • 13.1. Research Methodology
  • 13.2. References
  • 13.3. Abbreviations
  • 13.4. Disclaimer
  • 13.5. Contact Us