希少血友病因子市場- 世界の産業規模、シェア、動向、機会、予測、治療別、タイプ別、地域別、競合別セグメント、2020-2030F

希少血友病因子の世界市場規模は2024年に3億2,425万米ドルで、予測期間中のCAGRは6.58%で2030年には4億7,514万米ドルに達すると予測されています。

希少血友病因子の世界市場は、広範なヘルスケア産業の中でもダイナミックで重要なセクターであり、希少型の血友病に苦しむ人々のユニークなニーズへの対応に焦点を当てています。血友病は、主に血液凝固第VIII因子（血友病A）と血液凝固第IX因子（血友病B）という特定の血液凝固因子の欠乏または欠損を特徴とする稀な遺伝性疾患です。しかし、第I、V、VII、X、XIおよびXIII因子を含む他の血液凝固因子の欠乏に起因する血友病はさらにまれです。これらの稀な血友病型は、診断、治療、患者ケアの面で明確な課題を提示しています。

希少血友病因子の市場には、これらの稀な凝固因子障害に関連する特定の欠乏症に対処するために調整された様々な製品および治療法が含まれます。これらの治療は、欠損した凝固因子を補充するか、患者の既存の凝固因子の機能を強化するように設計されています。最近の動向では、遺伝子治療を含む革新的な治療法の開発が大きく進展しており、希少血友病因子を持つ患者の長期的な救済が期待されています。

市場の成長は、診断や認知度の向上による希少血友病因子疾患の有病率の増加、新興国におけるヘルスケアインフラの拡充、治療選択肢の改善を目指した研究開発の進行など、いくつかの要因によって牽引されています。さらに、製薬会社、研究機関、患者支援団体間の協力や提携が、この分野の進歩を加速させています。

主な市場促進要因

有病率の上昇と診断の改善

主な市場課題

高い治療費

主要市場動向

遺伝子治療のブレークスルー

目次

第1章 概要

第2章 調査手法

第3章 エグゼクティブサマリー

第4章 世界の希少血友病因子市場展望

• 市場規模・予測
  • 金額別
• 市場シェア・予測
  • 治療別（凝固因子製剤、新鮮凍結血漿、クリオプレシピテート、その他）
  • タイプ別（第I因子、第II因子、第V因子、第VII因子、第X因子、第XI因子、第XIII因子）
  • 地域別
  • 企業別（2024）
• 市場マップ
  • 治療別
  • タイプ別
  • 地域別

第5章 アジア太平洋地域の希少血友病因子市場展望

• 市場規模・予測
  • 金額別
• 市場シェア・予測
  • 治療別
  • タイプ別
  • 国別
• アジア太平洋地域：国別分析
  • 中国
  • インド
  • オーストラリア
  • 日本
  • 韓国

第6章 欧州の希少血友病因子市場展望

• 市場規模・予測
• 市場シェア・予測
• 欧州：国別分析
  • フランス
  • ドイツ
  • スペイン
  • イタリア
  • 英国

第7章 北米の希少血友病因子市場展望

• 市場規模・予測
• 市場シェア・予測
• 北米：国別分析
  • 米国
  • メキシコ
  • カナダ

第8章 南米の希少血友病因子市場展望

• 市場規模・予測
• 市場シェア・予測
• 南米：国別分析
  • ブラジル
  • アルゼンチン
  • コロンビア

第9章 中東・アフリカの希少血友病因子市場展望

• 市場規模・予測
• 市場シェア・予測
• 中東・アフリカ：国別分析
  • 南アフリカ
  • サウジアラビア
  • アラブ首長国連邦
  • エジプト

第10章 市場力学

• 促進要因
• 課題

第11章 市場動向と発展

• 最近の動向
• 治療開始
• 合併と買収

第12章 世界の希少血友病因子市場：SWOT分析

第13章 ポーターのファイブフォース分析

• 業界内の競合
• 新規参入の可能性
• サプライヤーの力
• 顧客の力
• 代替品の脅威

第14章 競合情勢

• Novo Nordisk A/S
• Biogen
• Bayer AG
• Pfizer, Inc.
• Shire Pharmaceuticals
• Baxalta（Baxter Healthcare）
• CSL Behring
• Bio Products Laboratory Ltd.
• Takeda Pharmaceutical Co. Ltd.
• Alexion Pharmaceuticals, Inc.

第15章 戦略的提言

第16章 調査会社について・免責事項

Global Rare Hemophilia Factors Market was valued at USD 324.25 million in 2024 and is expected to reach USD 475.14 million by 2030 with a CAGR of 6.58% during the forecast period. The Global Rare Hemophilia Factors Market is a dynamic and vital sector within the broader healthcare industry, focused on addressing the unique needs of individuals suffering from rare forms of hemophilia. Hemophilia is a rare genetic disorder characterized by the absence or deficiency of specific blood clotting factors, primarily Factor VIII (hemophilia A) and Factor IX (hemophilia B). However, there are even rarer forms of hemophilia that result from deficiencies in other clotting factors, including Factors I, V, VII, X, XI, and XIII. These rare hemophilia variants present distinct challenges in terms of diagnosis, treatment, and patient care.

The market for rare hemophilia factors encompasses a range of products and therapies tailored to address the specific deficiencies associated with these rare clotting factor disorders. These treatments are designed to either replace the missing clotting factors or enhance the function of the patient's existing clotting factors. In recent years, there have been significant advancements in the development of innovative therapies, including gene therapy, which holds promise for long-term relief for individuals with rare hemophilia factors.

The market's growth is driven by several factors, including the increasing prevalence of rare hemophilia factor disorders due to improved diagnosis and awareness, the expansion of healthcare infrastructure in developing countries, and ongoing research and development efforts aimed at improving treatment options. Additionally, collaborations and partnerships between pharmaceutical companies, research institutions, and patient advocacy groups have accelerated progress in the field.

Key Market Drivers

Rising Prevalence and Improved Diagnosis

Rising prevalence and improved diagnosis are among the foremost factors propelling the growth of the Global Rare Hemophilia Factors Market. Historically, patients with rare hemophilia factor deficiencies often faced delayed or misdiagnoses due to the complexities and the rarity of these disorders. However, in recent years, there has been a significant shift in the healthcare landscape with enhanced awareness, better diagnostic tools, and more comprehensive genetic testing.

The increasing prevalence of rare hemophilia factor deficiencies can be attributed, in part, to improved diagnosis. As healthcare professionals become more knowledgeable about these fewer common forms of hemophilia, more patients are correctly identified and diagnosed. This growing awareness, often fostered by patient advocacy groups, has led to a surge in demand for specialized therapies and treatments tailored to these unique clotting factor disorders. This, in turn, fuels the market by creating a larger patient pool seeking appropriate care.

Advancements in diagnostic technologies, particularly genetic testing, have been pivotal in this context. These tests enable healthcare providers to pinpoint the exact clotting factor deficiency and its genetic basis, allowing for precise and early diagnoses. Such early diagnosis is crucial because it enables timely intervention and personalized treatment strategies, significantly improving patient outcomes. Patients who were once left undiagnosed or misdiagnosed can now receive tailored care, leading to a better quality of life.

Furthermore, as the prevalence of rare hemophilia factor disorders becomes more apparent, healthcare systems worldwide are recognizing the importance of addressing these conditions and allocating resources to support affected individuals. This commitment is fostering a more patient-centric approach in healthcare, driving the development of novel therapies and treatment options.

Key Market Challenges

High Treatment Costs

The Global Rare Hemophilia Factors Market has made significant strides in addressing the unique needs of individuals with rare clotting factor deficiencies. While advancements in therapies have offered new hope to these patients, a pervasive challenge looms large - the high cost of treatment. The exorbitant price of specialized therapies designed for rare hemophilia factors is a key obstacle in achieving equitable access and comprehensive care for affected individuals.

Rare hemophilia factor deficiencies encompass various disorders that result from the deficiency of clotting factors other than the commonly known Factors VIII (hemophilia A) and IX (hemophilia B). These conditions, which include deficiencies in Factors I, V, VII, X, XI, and XIII, present unique challenges in diagnosis and management. As a result, specialized treatments are required, which are often considerably more expensive than traditional clotting factor replacement therapies.

The high treatment costs can be a significant financial burden for both patients and healthcare systems. For patients, it can lead to personal financial strain, jeopardizing their access to the critical care they need. In many cases, individuals with rare hemophilia factor deficiencies find themselves grappling with out-of-pocket expenses that are simply unaffordable. This financial burden can result in treatment non-compliance, reduced quality of life, and overall health complications.

Key Market Trends

Gene Therapy Breakthroughs

Gene therapy breakthroughs have emerged as a powerful driving force in the Global Rare Hemophilia Factors Market. Rare hemophilia factor deficiencies, resulting from the absence or dysfunction of specific clotting factors, have long presented significant challenges in terms of treatment. However, recent breakthroughs in gene therapy are fundamentally transforming the landscape of care for individuals with these conditions, offering newfound hope, improved outcomes, and a promising shift away from lifelong clotting factor replacement therapy.

Gene therapy for rare hemophilia factors involves the introduction of a functional copy of the deficient clotting factor gene into the patient's cells, addressing the root genetic cause of the deficiency. This innovative approach has yielded remarkable results, offering potential cures rather than just symptom management. Clinical trials have demonstrated the safety and efficacy of gene therapy in treating rare hemophilia, showing that it can lead to sustained production of the deficient clotting factor, reducing or eliminating the need for regular infusions of clotting factor concentrates.

Key Market Players

• Novo Nordisk A/S
• Biogen
• Bayer AG
• Pfizer, Inc.
• Shire Pharmaceuticals
• Baxalta (Baxter Healthcare)
• CSL Behring
• Bio Products Laboratory Ltd.
• Takeda Pharmaceutical Co. Ltd.
• Alexion Pharmaceuticals, Inc.

Report Scope:

In this report, the Global Rare Hemophilia Factors Market has been segmented into the following categories, in addition to the industry trends which have also been detailed below:

Rare Hemophilia Factors Market, By Treatment:

• Factor Concentrates
• Fresh Frozen Plasma
• Cryoprecipitate
• Others

Rare Hemophilia Factors Market, By Type:

• Factor I
• Factor II
• Factor V
• Factor VII
• Factor X
• Factor XI
• Factor XIII

Rare Hemophilia Factors Market, By Region:

• North America
  • United States
  • Canada
  • Mexico
• Europe
  • France
  • United Kingdom
  • Italy
  • Germany
  • Spain
• Asia-Pacific
  • China
  • India
  • Japan
  • Australia
  • South Korea
• South America
  • Brazil
  • Argentina
  • Colombia
• Middle East & Africa
  • South Africa
  • Saudi Arabia
  • UAE
  • Egypt

Competitive Landscape

Company Profiles: Detailed analysis of the major companies present in the Global Rare Hemophilia Factors Market.

Available Customizations:

Global Rare Hemophilia Factors Market report with the given market data, TechSci Research offers customizations according to a company's specific needs. The following customization options are available for the report:

Company Information

• Detailed analysis and profiling of additional market players (up to five).

Table of Contents

1. Product Overview

• 1.1. Market Definition
• 1.2. Scope of the Market
  • 1.2.1. Markets Covered
  • 1.2.2. Years Considered for Study
  • 1.2.3. Key Market Segmentations

2. Research Methodology

• 2.1. Objective of the Study
• 2.2. Baseline Methodology
• 2.3. Key Industry Partners
• 2.4. Major Association and Secondary Sources
• 2.5. Forecasting Methodology
• 2.6. Data Triangulation & Validation
• 2.7. Assumptions and Limitations

3. Executive Summary

• 3.1. Overview of the Market
• 3.2. Overview of Key Market Segmentations
• 3.3. Overview of Key Market Players
• 3.4. Overview of Key Regions/Countries
• 3.5. Overview of Market Drivers, Challenges, Trends

4. Global Rare Hemophilia Factors Market Outlook

• 4.1. Market Size & Forecast
  • 4.1.1. By Value
• 4.2. Market Share & Forecast
  • 4.2.1. By Treatment (Factor Concentrates, Fresh Frozen Plasma, Cryoprecipitate, Others)
  • 4.2.2. By Type (Factor I, Factor II, Factor V, Factor VII, Factor X, Factor XI, Factor XIII)
  • 4.2.3. By Region
  • 4.2.4. By Company (2024)
• 4.3. Market Map
  • 4.3.1. By Treatment
  • 4.3.2. By Type
  • 4.3.3. By Region

5. Asia Pacific Rare Hemophilia Factors Market Outlook

• 5.1. Market Size & Forecast
  • 5.1.1. By Value
• 5.2. Market Share & Forecast
  • 5.2.1. By Treatment
  • 5.2.2. By Type
  • 5.2.3. By Country
• 5.3. Asia Pacific: Country Analysis
  • 5.3.1. China Rare Hemophilia Factors Market Outlook
    • 5.3.1.1. Market Size & Forecast
      • 5.3.1.1.1. By Value
    • 5.3.1.2. Market Share & Forecast
      • 5.3.1.2.1. By Treatment
      • 5.3.1.2.2. By Type
  • 5.3.2. India Rare Hemophilia Factors Market Outlook
    • 5.3.2.1. Market Size & Forecast
      • 5.3.2.1.1. By Value
    • 5.3.2.2. Market Share & Forecast
      • 5.3.2.2.1. By Treatment
      • 5.3.2.2.2. By Type
  • 5.3.3. Australia Rare Hemophilia Factors Market Outlook
    • 5.3.3.1. Market Size & Forecast
      • 5.3.3.1.1. By Value
    • 5.3.3.2. Market Share & Forecast
      • 5.3.3.2.1. By Treatment
      • 5.3.3.2.2. By Type
  • 5.3.4. Japan Rare Hemophilia Factors Market Outlook
    • 5.3.4.1. Market Size & Forecast
      • 5.3.4.1.1. By Value
    • 5.3.4.2. Market Share & Forecast
      • 5.3.4.2.1. By Treatment
      • 5.3.4.2.2. By Type
  • 5.3.5. South Korea Rare Hemophilia Factors Market Outlook
    • 5.3.5.1. Market Size & Forecast
      • 5.3.5.1.1. By Value
    • 5.3.5.2. Market Share & Forecast
      • 5.3.5.2.1. By Treatment
      • 5.3.5.2.2. By Type

6. Europe Rare Hemophilia Factors Market Outlook

• 6.1. Market Size & Forecast
  • 6.1.1. By Value
• 6.2. Market Share & Forecast
  • 6.2.1. By Treatment
  • 6.2.2. By Type
  • 6.2.3. By Country
• 6.3. Europe: Country Analysis
  • 6.3.1. France Rare Hemophilia Factors Market Outlook
    • 6.3.1.1. Market Size & Forecast
      • 6.3.1.1.1. By Value
    • 6.3.1.2. Market Share & Forecast
      • 6.3.1.2.1. By Treatment
      • 6.3.1.2.2. By Type
  • 6.3.2. Germany Rare Hemophilia Factors Market Outlook
    • 6.3.2.1. Market Size & Forecast
      • 6.3.2.1.1. By Value
    • 6.3.2.2. Market Share & Forecast
      • 6.3.2.2.1. By Treatment
      • 6.3.2.2.2. By Type
  • 6.3.3. Spain Rare Hemophilia Factors Market Outlook
    • 6.3.3.1. Market Size & Forecast
      • 6.3.3.1.1. By Value
    • 6.3.3.2. Market Share & Forecast
      • 6.3.3.2.1. By Treatment
      • 6.3.3.2.2. By Type
  • 6.3.4. Italy Rare Hemophilia Factors Market Outlook
    • 6.3.4.1. Market Size & Forecast
      • 6.3.4.1.1. By Value
    • 6.3.4.2. Market Share & Forecast
      • 6.3.4.2.1. By Treatment
      • 6.3.4.2.2. By Type
  • 6.3.5. United Kingdom Rare Hemophilia Factors Market Outlook
    • 6.3.5.1. Market Size & Forecast
      • 6.3.5.1.1. By Value
    • 6.3.5.2. Market Share & Forecast
      • 6.3.5.2.1. By Treatment
      • 6.3.5.2.2. By Type

7. North America Rare Hemophilia Factors Market Outlook

• 7.1. Market Size & Forecast
  • 7.1.1. By Value
• 7.2. Market Share & Forecast
  • 7.2.1. By Treatment
  • 7.2.2. By Type
  • 7.2.3. By Country
• 7.3. North America: Country Analysis
  • 7.3.1. United States Rare Hemophilia Factors Market Outlook
    • 7.3.1.1. Market Size & Forecast
      • 7.3.1.1.1. By Value
    • 7.3.1.2. Market Share & Forecast
      • 7.3.1.2.1. By Treatment
      • 7.3.1.2.2. By Type
  • 7.3.2. Mexico Rare Hemophilia Factors Market Outlook
    • 7.3.2.1. Market Size & Forecast
      • 7.3.2.1.1. By Value
    • 7.3.2.2. Market Share & Forecast
      • 7.3.2.2.1. By Treatment
      • 7.3.2.2.2. By Type
  • 7.3.3. Canada Rare Hemophilia Factors Market Outlook
    • 7.3.3.1. Market Size & Forecast
      • 7.3.3.1.1. By Value
    • 7.3.3.2. Market Share & Forecast
      • 7.3.3.2.1. By Treatment
      • 7.3.3.2.2. By Type

8. South America Rare Hemophilia Factors Market Outlook

• 8.1. Market Size & Forecast
  • 8.1.1. By Value
• 8.2. Market Share & Forecast
  • 8.2.1. By Treatment
  • 8.2.2. By Type
  • 8.2.3. By Country
• 8.3. South America: Country Analysis
  • 8.3.1. Brazil Rare Hemophilia Factors Market Outlook
    • 8.3.1.1. Market Size & Forecast
      • 8.3.1.1.1. By Value
    • 8.3.1.2. Market Share & Forecast
      • 8.3.1.2.1. By Treatment
      • 8.3.1.2.2. By Type
  • 8.3.2. Argentina Rare Hemophilia Factors Market Outlook
    • 8.3.2.1. Market Size & Forecast
      • 8.3.2.1.1. By Value
    • 8.3.2.2. Market Share & Forecast
      • 8.3.2.2.1. By Treatment
      • 8.3.2.2.2. By Type
  • 8.3.3. Colombia Rare Hemophilia Factors Market Outlook
    • 8.3.3.1. Market Size & Forecast
      • 8.3.3.1.1. By Value
    • 8.3.3.2. Market Share & Forecast
      • 8.3.3.2.1. By Treatment
      • 8.3.3.2.2. By Type

9. Middle East and Africa Rare Hemophilia Factors Market Outlook

• 9.1. Market Size & Forecast
  • 9.1.1. By Value
• 9.2. Market Share & Forecast
  • 9.2.1. By Treatment
  • 9.2.2. By Type
  • 9.2.3. By Country
• 9.3. MEA: Country Analysis
  • 9.3.1. South Africa Rare Hemophilia Factors Market Outlook
    • 9.3.1.1. Market Size & Forecast
      • 9.3.1.1.1. By Value
    • 9.3.1.2. Market Share & Forecast
      • 9.3.1.2.1. By Treatment
      • 9.3.1.2.2. By Type
  • 9.3.2. Saudi Arabia Rare Hemophilia Factors Market Outlook
    • 9.3.2.1. Market Size & Forecast
      • 9.3.2.1.1. By Value
    • 9.3.2.2. Market Share & Forecast
      • 9.3.2.2.1. By Treatment
      • 9.3.2.2.2. By Type
  • 9.3.3. UAE Rare Hemophilia Factors Market Outlook
    • 9.3.3.1. Market Size & Forecast
      • 9.3.3.1.1. By Value
    • 9.3.3.2. Market Share & Forecast
      • 9.3.3.2.1. By Treatment
      • 9.3.3.2.2. By Type
  • 9.3.4. Egypt Rare Hemophilia Factors Market Outlook
    • 9.3.4.1. Market Size & Forecast
      • 9.3.4.1.1. By Value
    • 9.3.4.2. Market Share & Forecast
      • 9.3.4.2.1. By Treatment
      • 9.3.4.2.2. By Type

10. Market Dynamics

• 10.1. Drivers
• 10.2. Challenges

11. Market Trends & Developments

• 11.1. Recent Developments
• 11.2. Treatment Launches
• 11.3. Mergers & Acquisitions

12. Global Rare Hemophilia Factors Market: SWOT Analysis

13. Porter's Five Forces Analysis

• 13.1. Competition in the Industry
• 13.2. Potential of New Entrants
• 13.3. Power of Suppliers
• 13.4. Power of Customers
• 13.5. Threat of Substitute Product

14. Competitive Landscape

• 14.1. Novo Nordisk A/S
  • 14.1.1. Business Overview
  • 14.1.2. Company Snapshot
  • 14.1.3. Products & Services
  • 14.1.4. Financials (In case of listed)
  • 14.1.5. Recent Developments
  • 14.1.6. Key Personnel Details
  • 14.1.7. SWOT Analysis
• 14.2. Biogen
• 14.3. Bayer AG
• 14.4. Pfizer, Inc.
• 14.5. Shire Pharmaceuticals
• 14.6. Baxalta (Baxter Healthcare)
• 14.7. CSL Behring
• 14.8. Bio Products Laboratory Ltd.
• 14.9. Takeda Pharmaceutical Co. Ltd.
• 14.10. Alexion Pharmaceuticals, Inc.

15. Strategic Recommendations

16. About Us & Disclaimer