アミノ酸代謝障害治療市場：治療、適応症、エンドユーザー別-2025～2030年の世界予測

アミノ酸代謝障害治療市場は、2023年に7億9,690万米ドルと評価され、2024年には8億5,117万米ドルに達すると予測され、CAGR 7.31％で成長し、2030年には13億641万米ドルに達すると予測されています。

アミノ酸代謝障害は、タンパク質の必須コンポーネントであるアミノ酸を分解または処理する体内の能力に影響を及ぼす遺伝的疾患です。この市場の治療範囲には、栄養補助食品、酵素補充療法、機能不全に陥った代謝経路の調節や補填を目的とした特殊な薬剤が含まれます。このような治療の必要性は、これらの障害に典型的に関連する神経障害、発達遅延、臓器機能不全などの深刻な健康問題を予防する可能性があることによる。用途は小児と成人の両方の患者集団に及び、早期診断と長期管理戦略を重視しています。最終用途の範囲には、罹患者に包括的なケアとサポートを提供する病院、専門クリニック、在宅ケアの現場が含まれます。

この市場に影響を与える主要成長要因としては、代謝異常の有病率の増加、遺伝子・分子診断の進歩、認知度向上と治療アクセス向上のための官民イニシアチブの拡大などが挙げられます。最近の潜在的なビジネス機会は、新規治療法の開発、特に遺伝子編集技術や、疾患の遺伝的根源を対象とする個別化医療戦略が中心となっています。また、治療用アミノ酸や酵素を合成する合成生物学の調査や技術革新も、ビジネス成長の道を開く可能性があります。企業は共同研究パートナーシップに投資し、特にこうした治療に対する需要が高まっている未開拓地域での市場拡大を模索することが推奨されます。

しかし、市場は、治療開発コストの高さ、規制上の課題、これらの疾患に関する認知度の低さといった限界に直面しており、市場への参入と成長を阻害する可能性があります。また、遺伝的疾患が複雑であることも、普遍的に有効な治療法を生み出す上での課題となっています。こうした制約に対処するためには、公的教育プログラムへの戦略的投資と、医療施策を支援するためのロビー活動が不可欠です。市場の競争はイノベーションを重視する傾向が強く、希少疾病に特化したニッチなビジネスモデルが生まれやすい環境にあります。企業は、最先端の研究開発、医療プロバイダーとの提携、サプライチェーンの効率を最適化する技術の活用に注力すべきです。

市場力学：急速に進化するアミノ酸代謝障害治療市場における主要市場洞察の解明

アミノ酸代謝障害治療市場は、需要と供給のダイナミックな相互作用によって変貌を遂げています。このような市場力学の進化を理解することで、企業は十分な情報に基づいた投資決定、戦略的決定の精緻化、そして新たなビジネス機会の獲得に備えることができます。これらの動向を包括的に把握することで、企業は政治的、地理的、技術的、社会的、経済的な領域にわたる様々なリスクを軽減することができるとともに、消費者行動とそれが製造コストや購買動向に与える影響をより明確に理解することができます。

• 市場促進要因
  • アミノ酸代謝異常の診断例の増加、
  • 希少代謝疾患に対する規制施策の強化
• 市場抑制要因
  • 治療費の高騰による患者へのアクセスの制限
• 市場機会
  • 強化された診断ツールと遺伝子検査技術の開発
  • アミノ酸代謝異常の新たな治療法の発見を目指した継続的な研究
• 市場課題
  • アミノ酸代謝障害治療の製品開発における複雑さ

ポーターのファイブフォース：アミノ酸代謝障害治療市場をナビゲートする戦略ツール

ポーターのファイブフォースフレームワークは、アミノ酸代謝障害治療市場の競合情勢を理解するための重要なツールです。ポーターのファイブフォースフレームワークは、企業の競合を評価し、戦略的機会を探るための明確な手法を記載しています。このフレームワークは、企業が市場内の勢力図を評価し、新規事業の収益性を判断するのに役立ちます。これら洞察により、企業は自社の強みを活かし、弱みに対処し、潜在的な課題を回避することができ、より強靭な市場でのポジショニングを確保することができます。

PESTLE分析：アミノ酸代謝障害治療市場における外部からの影響の把握

外部マクロ環境要因は、アミノ酸代謝障害治療市場の業績力学を形成する上で極めて重要な役割を果たします。政治的、経済的、社会的、技術的、法的、環境的要因の分析は、これらの影響をナビゲートするために必要な情報を記載しています。PESTLE要因を調査することで、企業は潜在的なリスクと機会をよりよく理解することができます。この分析により、企業は規制、消費者の嗜好、経済動向の変化を予測し、先を見越した積極的な意思決定を行う準備ができます。

市場シェア分析：アミノ酸代謝障害治療市場における競合情勢の把握

アミノ酸代謝障害治療市場の詳細な市場シェア分析により、ベンダーの業績を包括的に評価することができます。企業は、収益、顧客ベース、成長率などの主要指標を比較することで、競争上のポジショニングを明らかにすることができます。この分析により、市場の集中、セグメント化、統合の動向が明らかになり、ベンダーは競争が激化する中で自社の地位を高める戦略的意思決定を行うために必要な知見を得ることができます。

FPNVポジショニングマトリックス：アミノ酸代謝障害治療市場におけるベンダーのパフォーマンス評価

FPNVポジショニングマトリックスは、アミノ酸代謝障害治療市場においてベンダーを評価するための重要なツールです。このマトリックスにより、ビジネス組織はベンダーのビジネス戦略と製品満足度に基づき評価することで、目標に沿った十分な情報に基づいた意思決定を行うことができます。4つの象限によってベンダーを明確かつ正確にセグメント化し、戦略目標に最適なパートナーやソリューションを特定することができます。

戦略分析と推奨：アミノ酸代謝障害治療市場における成功への道筋を描く

アミノ酸代謝障害治療市場の戦略分析は、世界市場でのプレゼンス強化を目指す企業にとって不可欠です。主要なリソース、能力、業績指標を見直すことで、企業は成長機会を特定し、改善に取り組むことができます。このアプローチにより、競合情勢における課題を克服し、新たなビジネス機会を活かして長期的な成功を収めるための体制を整えることができます。

本レポートでは、主要な注目セグメントを網羅した市場の包括的な分析を提供しています。

1.市場の浸透度：現在の市場環境の詳細なレビュー、主要企業による広範なデータ、市場でのリーチと全体的な影響力を評価します。

2.市場の開拓度：新興市場における成長機会を特定し、既存セグメントにおける拡大可能性を評価し、将来の成長に向けた戦略的ロードマップを記載しています。

3.市場の多様化：最近の製品発売、未開拓の地域、産業の主要な進歩、市場を形成する戦略的投資を分析します。

4.競合の評価と情報：競合情勢を徹底的に分析し、市場シェア、事業戦略、製品ポートフォリオ、認証、規制当局の承認、特許動向、主要企業の技術進歩などを検証します。

5.製品開発とイノベーション：将来の市場成長を促進すると期待される最先端技術、研究開発活動、製品イノベーションをハイライトしています。

また、利害関係者が十分な情報を得た上で意思決定できるよう、重要な質問にも答えています。

1.現在の市場規模と今後の成長予測は？

2.最高の投資機会を提供する製品、地域はどこか？

3.市場を形成する主要技術動向と規制の影響とは？

4.主要ベンダーの市場シェアと競合ポジションは？

5.ベンダーの市場参入・撤退戦略の原動力となる収益源と戦略的機会は何か？

目次

第1章 序文

第2章 調査手法

第3章 エグゼクティブサマリー

第4章 市場概要

第5章 市場洞察

• 市場力学
  • 促進要因
    • アミノ酸代謝障害の診断例が増加
    • 希少代謝疾患に対処するための強化された支援規制施策
  • 抑制要因
    • 治療費が高額で患者のアクセスが制限される
  • 機会
    • 強化された診断ツールと遺伝子検査技術の開発
    • アミノ酸代謝障害の新たな治療法の発見を目指した継続的な研究
  • 課題
    • アミノ酸代謝障害治療の製品開発の複雑さ
• 市場セグメンテーション分析
  • 治療：体内の余分なアミノ酸を除去するための薬剤の使用が増加
  • エンドユーザー：アミノ酸代謝障害の診断と治療のための病院やクリニックを通じて、アミノ酸代謝障害治療へのアクセスが拡大
• ポーターのファイブフォース分析
• PESTEL分析
  • 政治
  • 経済
  • 社会
  • 技術
  • 法律
  • 環境

第6章 アミノ酸代謝障害治療市場：治療別

• イントロダクション
• 遺伝子治療
• 肝臓移植
• 薬剤治療
• 補給

第7章 アミノ酸代謝障害治療市場：適応症別

• イントロダクション
• メープルシロップ尿症
• フェニルケトン尿症

第8章 アミノ酸代謝障害治療市場：エンドユーザー別

• イントロダクション
• 外来手術センター
• 病院・クリニック

第9章 南北アメリカのアミノ酸代謝障害治療市場

• イントロダクション
• アルゼンチン
• ブラジル
• カナダ
• メキシコ
• 米国

第10章 アジア太平洋のアミノ酸代謝障害治療市場

• イントロダクション
• オーストラリア
• 中国
• インド
• インドネシア
• 日本
• マレーシア
• フィリピン
• シンガポール
• 韓国
• 台湾
• タイ
• ベトナム

第11章 欧州・中東・アフリカのアミノ酸代謝障害治療市場

• イントロダクション
• デンマーク
• エジプト
• フィンランド
• フランス
• ドイツ
• イスラエル
• イタリア
• オランダ
• ナイジェリア
• ノルウェー
• ポーランド
• カタール
• ロシア
• サウジアラビア
• 南アフリカ
• スペイン
• スウェーデン
• スイス
• トルコ
• アラブ首長国連邦
• 英国

第12章 競合情勢

• 市場シェア分析、2023年
• FPNVポジショニングマトリックス、2023年
• 競合シナリオ分析
  • PTC TherapeuticsがSSIEM 2023でフェニルケトン尿症治療の新たな進歩を展示
• 戦略分析と提言

企業一覧

• Abeona Therapeutics Inc.
• Alnylam Pharmaceuticals, Inc.
• American Gene Technologies Inc.
• Amgen Inc.
• AnGes, Inc.
• Astellas Gene Therapies
• Beacon Therapeutics Limited
• Biogen Inc.
• Cellectis SA
• Editas Medicine, Inc.
• F. Hoffmann-La Roche Ltd
• Ionis Pharmaceuticals, Inc.
• Merck KGaA
• Mustang Bio, Inc.
• Novartis AG
• Pfizer Inc.

LIST OF FIGURES

• FIGURE 1. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET RESEARCH PROCESS
• FIGURE 2. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, 2023 VS 2030
• FIGURE 3. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, 2018-2030 (USD MILLION)
• FIGURE 4. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY REGION, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 5. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 6. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2023 VS 2030 (%)
• FIGURE 7. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 8. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2023 VS 2030 (%)
• FIGURE 9. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 10. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2023 VS 2030 (%)
• FIGURE 11. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 12. AMERICAS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
• FIGURE 13. AMERICAS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 14. UNITED STATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY STATE, 2023 VS 2030 (%)
• FIGURE 15. UNITED STATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY STATE, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 16. ASIA-PACIFIC AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
• FIGURE 17. ASIA-PACIFIC AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 18. EUROPE, MIDDLE EAST & AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
• FIGURE 19. EUROPE, MIDDLE EAST & AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
• FIGURE 20. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SHARE, BY KEY PLAYER, 2023
• FIGURE 21. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET, FPNV POSITIONING MATRIX, 2023

LIST OF TABLES

• TABLE 1. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SEGMENTATION & COVERAGE
• TABLE 2. UNITED STATES DOLLAR EXCHANGE RATE, 2018-2023
• TABLE 3. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, 2018-2030 (USD MILLION)
• TABLE 4. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY REGION, 2018-2030 (USD MILLION)
• TABLE 5. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
• TABLE 6. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET DYNAMICS
• TABLE 7. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 8. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY GENE THERAPY, BY REGION, 2018-2030 (USD MILLION)
• TABLE 9. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY LIVER TRANSPLANT, BY REGION, 2018-2030 (USD MILLION)
• TABLE 10. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY MEDICATION, BY REGION, 2018-2030 (USD MILLION)
• TABLE 11. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY SUPPLEMENTATION, BY REGION, 2018-2030 (USD MILLION)
• TABLE 12. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 13. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY MAPLE SYRUP URINE DISEASE, BY REGION, 2018-2030 (USD MILLION)
• TABLE 14. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY PHENYLKETONURIA, BY REGION, 2018-2030 (USD MILLION)
• TABLE 15. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 16. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY AMBULATORY SURGERY CENTERS, BY REGION, 2018-2030 (USD MILLION)
• TABLE 17. GLOBAL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY HOSPITALS & CLINICS, BY REGION, 2018-2030 (USD MILLION)
• TABLE 18. AMERICAS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 19. AMERICAS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 20. AMERICAS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 21. AMERICAS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
• TABLE 22. ARGENTINA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 23. ARGENTINA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 24. ARGENTINA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 25. BRAZIL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 26. BRAZIL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 27. BRAZIL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 28. CANADA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 29. CANADA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 30. CANADA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 31. MEXICO AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 32. MEXICO AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 33. MEXICO AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 34. UNITED STATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 35. UNITED STATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 36. UNITED STATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 37. UNITED STATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY STATE, 2018-2030 (USD MILLION)
• TABLE 38. ASIA-PACIFIC AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 39. ASIA-PACIFIC AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 40. ASIA-PACIFIC AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 41. ASIA-PACIFIC AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
• TABLE 42. AUSTRALIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 43. AUSTRALIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 44. AUSTRALIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 45. CHINA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 46. CHINA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 47. CHINA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 48. INDIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 49. INDIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 50. INDIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 51. INDONESIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 52. INDONESIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 53. INDONESIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 54. JAPAN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 55. JAPAN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 56. JAPAN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 57. MALAYSIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 58. MALAYSIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 59. MALAYSIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 60. PHILIPPINES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 61. PHILIPPINES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 62. PHILIPPINES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 63. SINGAPORE AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 64. SINGAPORE AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 65. SINGAPORE AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 66. SOUTH KOREA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 67. SOUTH KOREA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 68. SOUTH KOREA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 69. TAIWAN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 70. TAIWAN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 71. TAIWAN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 72. THAILAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 73. THAILAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 74. THAILAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 75. VIETNAM AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 76. VIETNAM AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 77. VIETNAM AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 78. EUROPE, MIDDLE EAST & AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 79. EUROPE, MIDDLE EAST & AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 80. EUROPE, MIDDLE EAST & AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 81. EUROPE, MIDDLE EAST & AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
• TABLE 82. DENMARK AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 83. DENMARK AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 84. DENMARK AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 85. EGYPT AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 86. EGYPT AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 87. EGYPT AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 88. FINLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 89. FINLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 90. FINLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 91. FRANCE AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 92. FRANCE AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 93. FRANCE AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 94. GERMANY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 95. GERMANY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 96. GERMANY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 97. ISRAEL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 98. ISRAEL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 99. ISRAEL AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 100. ITALY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 101. ITALY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 102. ITALY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 103. NETHERLANDS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 104. NETHERLANDS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 105. NETHERLANDS AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 106. NIGERIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 107. NIGERIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 108. NIGERIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 109. NORWAY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 110. NORWAY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 111. NORWAY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 112. POLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 113. POLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 114. POLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 115. QATAR AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 116. QATAR AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 117. QATAR AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 118. RUSSIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 119. RUSSIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 120. RUSSIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 121. SAUDI ARABIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 122. SAUDI ARABIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 123. SAUDI ARABIA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 124. SOUTH AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 125. SOUTH AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 126. SOUTH AFRICA AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 127. SPAIN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 128. SPAIN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 129. SPAIN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 130. SWEDEN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 131. SWEDEN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 132. SWEDEN AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 133. SWITZERLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 134. SWITZERLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 135. SWITZERLAND AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 136. TURKEY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 137. TURKEY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 138. TURKEY AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 139. UNITED ARAB EMIRATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 140. UNITED ARAB EMIRATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 141. UNITED ARAB EMIRATES AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 142. UNITED KINGDOM AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY TREATMENT, 2018-2030 (USD MILLION)
• TABLE 143. UNITED KINGDOM AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY INDICATION, 2018-2030 (USD MILLION)
• TABLE 144. UNITED KINGDOM AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
• TABLE 145. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET SHARE, BY KEY PLAYER, 2023
• TABLE 146. AMINO ACID METABOLISM DISORDERS TREATMENT MARKET, FPNV POSITIONING MATRIX, 2023

The Amino Acid Metabolism Disorders Treatment Market was valued at USD 796.90 million in 2023, expected to reach USD 851.17 million in 2024, and is projected to grow at a CAGR of 7.31%, to USD 1,306.41 million by 2030.

Amino acid metabolism disorders are genetic conditions that affect the body's ability to break down or process amino acids, which are essential building blocks of proteins. The scope of treatments in this market includes dietary supplements, enzyme replacement therapies, and specialized medications aimed at regulating or compensating for the dysfunctional metabolic pathways. The necessity for such treatments is driven by their potential to prevent serious health issues such as neurological impairment, developmental delays, and organ dysfunction typically associated with these disorders. Applications extend to both pediatric and adult patient populations, emphasizing early diagnosis and long-term management strategies. The end-use scope includes hospitals, specialty clinics, and homecare settings that provide comprehensive care and support for affected individuals.

Key influencing growth factors in this market include the increasing prevalence of metabolic disorders, advances in genetic and molecular diagnostics, and growing public and private initiatives to improve awareness and treatment access. The latest potential opportunities are centered on the development of novel therapies, especially gene editing technologies and personalized medicine strategies that target the disorder at its genetic root. Research and innovation into synthetic biology to engineer therapeutic amino acids or enzymes can also provide business growth avenues. Companies are recommended to invest in collaborative research partnerships and explore regional market expansions, particularly in underserved areas with rising demand for such treatments.

However, the market faces limitations such as high costs of treatment development, regulatory challenges, and a lack of widespread awareness about these disorders, which can impede market entry and growth. The complexity of genetic conditions also presents challenges in creating universally effective therapies. To address these limitations, strategic investment in public education programs and lobbying for supportive healthcare policies is essential. The nature of the market is competitive with a strong emphasis on innovation, creating fertile ground for niche business models focused on rare diseases. Companies should focus on cutting-edge R&D, partnerships with healthcare providers, and leveraging technology to optimize supply chain efficiencies.

Market Dynamics: Unveiling Key Market Insights in the Rapidly Evolving Amino Acid Metabolism Disorders Treatment Market

The Amino Acid Metabolism Disorders Treatment Market is undergoing transformative changes driven by a dynamic interplay of supply and demand factors. Understanding these evolving market dynamics prepares business organizations to make informed investment decisions, refine strategic decisions, and seize new opportunities. By gaining a comprehensive view of these trends, business organizations can mitigate various risks across political, geographic, technical, social, and economic domains while also gaining a clearer understanding of consumer behavior and its impact on manufacturing costs and purchasing trends.

• Market Drivers
  • Growing number of diagnosed cases of amino acid metabolism disorders,
  • Enhanced supportive regulatory policies addressing rare metabolic disorders
• Market Restraints
  • High cost of treatment limiting patient accessibility
• Market Opportunities
  • Development of enhanced diagnostic tools and genetic testing technologies
  • Ongoing research aimed at discovering new treatments for amino acid metabolism disorders
• Market Challenges
  • Complexities in product development for amino acid metabolism disorders treatment

Porter's Five Forces: A Strategic Tool for Navigating the Amino Acid Metabolism Disorders Treatment Market

Porter's five forces framework is a critical tool for understanding the competitive landscape of the Amino Acid Metabolism Disorders Treatment Market. It offers business organizations with a clear methodology for evaluating their competitive positioning and exploring strategic opportunities. This framework helps businesses assess the power dynamics within the market and determine the profitability of new ventures. With these insights, business organizations can leverage their strengths, address weaknesses, and avoid potential challenges, ensuring a more resilient market positioning.

PESTLE Analysis: Navigating External Influences in the Amino Acid Metabolism Disorders Treatment Market

External macro-environmental factors play a pivotal role in shaping the performance dynamics of the Amino Acid Metabolism Disorders Treatment Market. Political, Economic, Social, Technological, Legal, and Environmental factors analysis provides the necessary information to navigate these influences. By examining PESTLE factors, businesses can better understand potential risks and opportunities. This analysis enables business organizations to anticipate changes in regulations, consumer preferences, and economic trends, ensuring they are prepared to make proactive, forward-thinking decisions.

Market Share Analysis: Understanding the Competitive Landscape in the Amino Acid Metabolism Disorders Treatment Market

A detailed market share analysis in the Amino Acid Metabolism Disorders Treatment Market provides a comprehensive assessment of vendors' performance. Companies can identify their competitive positioning by comparing key metrics, including revenue, customer base, and growth rates. This analysis highlights market concentration, fragmentation, and trends in consolidation, offering vendors the insights required to make strategic decisions that enhance their position in an increasingly competitive landscape.

FPNV Positioning Matrix: Evaluating Vendors' Performance in the Amino Acid Metabolism Disorders Treatment Market

The Forefront, Pathfinder, Niche, Vital (FPNV) Positioning Matrix is a critical tool for evaluating vendors within the Amino Acid Metabolism Disorders Treatment Market. This matrix enables business organizations to make well-informed decisions that align with their goals by assessing vendors based on their business strategy and product satisfaction. The four quadrants provide a clear and precise segmentation of vendors, helping users identify the right partners and solutions that best fit their strategic objectives.

Strategy Analysis & Recommendation: Charting a Path to Success in the Amino Acid Metabolism Disorders Treatment Market

A strategic analysis of the Amino Acid Metabolism Disorders Treatment Market is essential for businesses looking to strengthen their global market presence. By reviewing key resources, capabilities, and performance indicators, business organizations can identify growth opportunities and work toward improvement. This approach helps businesses navigate challenges in the competitive landscape and ensures they are well-positioned to capitalize on newer opportunities and drive long-term success.

Key Company Profiles

The report delves into recent significant developments in the Amino Acid Metabolism Disorders Treatment Market, highlighting leading vendors and their innovative profiles. These include Abeona Therapeutics Inc., Alnylam Pharmaceuticals, Inc., American Gene Technologies Inc., Amgen Inc., AnGes, Inc., Astellas Gene Therapies, Beacon Therapeutics Limited, Biogen Inc., Cellectis SA, Editas Medicine, Inc., F. Hoffmann-La Roche Ltd, Ionis Pharmaceuticals, Inc., Merck KGaA, Mustang Bio, Inc., Novartis AG, and Pfizer Inc..

Market Segmentation & Coverage

This research report categorizes the Amino Acid Metabolism Disorders Treatment Market to forecast the revenues and analyze trends in each of the following sub-markets:

• Based on Treatment, market is studied across Gene Therapy, Liver Transplant, Medication, and Supplementation.
• Based on Indication, market is studied across Maple Syrup Urine Disease and Phenylketonuria.
• Based on End-User, market is studied across Ambulatory Surgery Centers and Hospitals & Clinics.
• Based on Region, market is studied across Americas, Asia-Pacific, and Europe, Middle East & Africa. The Americas is further studied across Argentina, Brazil, Canada, Mexico, and United States. The United States is further studied across California, Florida, Illinois, New York, Ohio, Pennsylvania, and Texas. The Asia-Pacific is further studied across Australia, China, India, Indonesia, Japan, Malaysia, Philippines, Singapore, South Korea, Taiwan, Thailand, and Vietnam. The Europe, Middle East & Africa is further studied across Denmark, Egypt, Finland, France, Germany, Israel, Italy, Netherlands, Nigeria, Norway, Poland, Qatar, Russia, Saudi Arabia, South Africa, Spain, Sweden, Switzerland, Turkey, United Arab Emirates, and United Kingdom.

The report offers a comprehensive analysis of the market, covering key focus areas:

1. Market Penetration: A detailed review of the current market environment, including extensive data from top industry players, evaluating their market reach and overall influence.

2. Market Development: Identifies growth opportunities in emerging markets and assesses expansion potential in established sectors, providing a strategic roadmap for future growth.

3. Market Diversification: Analyzes recent product launches, untapped geographic regions, major industry advancements, and strategic investments reshaping the market.

4. Competitive Assessment & Intelligence: Provides a thorough analysis of the competitive landscape, examining market share, business strategies, product portfolios, certifications, regulatory approvals, patent trends, and technological advancements of key players.

5. Product Development & Innovation: Highlights cutting-edge technologies, R&D activities, and product innovations expected to drive future market growth.

The report also answers critical questions to aid stakeholders in making informed decisions:

1. What is the current market size, and what is the forecasted growth?

2. Which products, segments, and regions offer the best investment opportunities?

3. What are the key technology trends and regulatory influences shaping the market?

4. How do leading vendors rank in terms of market share and competitive positioning?

5. What revenue sources and strategic opportunities drive vendors' market entry or exit strategies?

Table of Contents

1. Preface

• 1.1. Objectives of the Study
• 1.2. Market Segmentation & Coverage
• 1.3. Years Considered for the Study
• 1.4. Currency & Pricing
• 1.5. Language
• 1.6. Stakeholders

2. Research Methodology

• 2.1. Define: Research Objective
• 2.2. Determine: Research Design
• 2.3. Prepare: Research Instrument
• 2.4. Collect: Data Source
• 2.5. Analyze: Data Interpretation
• 2.6. Formulate: Data Verification
• 2.7. Publish: Research Report
• 2.8. Repeat: Report Update

3. Executive Summary

4. Market Overview

5. Market Insights

• 5.1. Market Dynamics
  • 5.1.1. Drivers
    • 5.1.1.1. Growing number of diagnosed cases of amino acid metabolism disorders,
    • 5.1.1.2. Enhanced supportive regulatory policies addressing rare metabolic disorders
  • 5.1.2. Restraints
    • 5.1.2.1. High cost of treatment limiting patient accessibility
  • 5.1.3. Opportunities
    • 5.1.3.1. Development of enhanced diagnostic tools and genetic testing technologies
    • 5.1.3.2. Ongoing research aimed at discovering new treatments for amino acid metabolism disorders
  • 5.1.4. Challenges
    • 5.1.4.1. Complexities in product development for amino acid metabolism disorders treatment
• 5.2. Market Segmentation Analysis
  • 5.2.1. Treatment: Growing usage of medications to eliminate excess amino acids from the body
  • 5.2.2. End-User: Growing accessibility of amino acid metabolism disorders treatment through hospitals & clinics for diagnosing and treating cases of amino acid metabolism disorders
• 5.3. Porter's Five Forces Analysis
  • 5.3.1. Threat of New Entrants
  • 5.3.2. Threat of Substitutes
  • 5.3.3. Bargaining Power of Customers
  • 5.3.4. Bargaining Power of Suppliers
  • 5.3.5. Industry Rivalry
• 5.4. PESTLE Analysis
  • 5.4.1. Political
  • 5.4.2. Economic
  • 5.4.3. Social
  • 5.4.4. Technological
  • 5.4.5. Legal
  • 5.4.6. Environmental

6. Amino Acid Metabolism Disorders Treatment Market, by Treatment

• 6.1. Introduction
• 6.2. Gene Therapy
• 6.3. Liver Transplant
• 6.4. Medication
• 6.5. Supplementation

7. Amino Acid Metabolism Disorders Treatment Market, by Indication

• 7.1. Introduction
• 7.2. Maple Syrup Urine Disease
• 7.3. Phenylketonuria

8. Amino Acid Metabolism Disorders Treatment Market, by End-User

• 8.1. Introduction
• 8.2. Ambulatory Surgery Centers
• 8.3. Hospitals & Clinics

9. Americas Amino Acid Metabolism Disorders Treatment Market

• 9.1. Introduction
• 9.2. Argentina
• 9.3. Brazil
• 9.4. Canada
• 9.5. Mexico
• 9.6. United States

10. Asia-Pacific Amino Acid Metabolism Disorders Treatment Market

• 10.1. Introduction
• 10.2. Australia
• 10.3. China
• 10.4. India
• 10.5. Indonesia
• 10.6. Japan
• 10.7. Malaysia
• 10.8. Philippines
• 10.9. Singapore
• 10.10. South Korea
• 10.11. Taiwan
• 10.12. Thailand
• 10.13. Vietnam

11. Europe, Middle East & Africa Amino Acid Metabolism Disorders Treatment Market

• 11.1. Introduction
• 11.2. Denmark
• 11.3. Egypt
• 11.4. Finland
• 11.5. France
• 11.6. Germany
• 11.7. Israel
• 11.8. Italy
• 11.9. Netherlands
• 11.10. Nigeria
• 11.11. Norway
• 11.12. Poland
• 11.13. Qatar
• 11.14. Russia
• 11.15. Saudi Arabia
• 11.16. South Africa
• 11.17. Spain
• 11.18. Sweden
• 11.19. Switzerland
• 11.20. Turkey
• 11.21. United Arab Emirates
• 11.22. United Kingdom

12. Competitive Landscape

• 12.1. Market Share Analysis, 2023
• 12.2. FPNV Positioning Matrix, 2023
• 12.3. Competitive Scenario Analysis
  • 12.3.1. PTC Therapeutics to Showcase New Advances in Phenylketonuria Treatment at SSIEM 2023
• 12.4. Strategy Analysis & Recommendation

Companies Mentioned

• 1. Abeona Therapeutics Inc.
• 2. Alnylam Pharmaceuticals, Inc.
• 3. American Gene Technologies Inc.
• 4. Amgen Inc.
• 5. AnGes, Inc.
• 6. Astellas Gene Therapies
• 7. Beacon Therapeutics Limited
• 8. Biogen Inc.
• 9. Cellectis SA
• 10. Editas Medicine, Inc.
• 11. F. Hoffmann-La Roche Ltd
• 12. Ionis Pharmaceuticals, Inc.
• 13. Merck KGaA
• 14. Mustang Bio, Inc.
• 15. Novartis AG
• 16. Pfizer Inc.